Amlexanox: Readthrough Induction and Nonsense-Mediated mRNA Decay Inhibition in a Charcot-Marie-Tooth Model of hiPSCs-Derived Neuronal Cells Harboring a Nonsense Mutation in GDAP1 Gene.
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| Title: | Amlexanox: Readthrough Induction and Nonsense-Mediated mRNA Decay Inhibition in a Charcot-Marie-Tooth Model of hiPSCs-Derived Neuronal Cells Harboring a Nonsense Mutation in GDAP1 Gene. |
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| Authors: | Benslimane N; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France., Miressi F; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France., Loret C; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France., Richard L; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.; CHU Limoges, Service de Neurologie, F-87000 Limoges, France., Nizou A; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France., Pyromali I; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France., Faye PA; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.; Centre Hospitalier Universitaire (CHU) Limoges, Service de Biochimie et de Génétique Moléculaire, F-87000 Limoges, France., Favreau F; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.; Centre Hospitalier Universitaire (CHU) Limoges, Service de Biochimie et de Génétique Moléculaire, F-87000 Limoges, France., Lejeune F; CNRS, Inserm, CHU Lille, UMR9020-U1277-CANTHER-Cancer Heterogeneity Plasticity and Resistance to Therapies, University of Lille, F-59000 Lille, France., Lia AS; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.; Centre Hospitalier Universitaire (CHU) Limoges, Service de Biochimie et de Génétique Moléculaire, F-87000 Limoges, France.; Centre Hospitalo-Universitaire (CHU) Limoges, UF de Bioinformatique, F-87000 Limoges, France. |
| Source: | Pharmaceuticals (Basel, Switzerland) [Pharmaceuticals (Basel)] 2023 Jul 21; Vol. 16 (7). Date of Electronic Publication: 2023 Jul 21. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: MDPI Country of Publication: Switzerland NLM ID: 101238453 Publication Model: Electronic Cited Medium: Print ISSN: 1424-8247 (Print) Linking ISSN: 14248247 NLM ISO Abbreviation: Pharmaceuticals (Basel) Subsets: PubMed not MEDLINE |
| Database: | MEDLINE Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 37513945 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Amlexanox: Readthrough Induction and Nonsense-Mediated mRNA Decay Inhibition in a Charcot-Marie-Tooth Model of hiPSCs-Derived Neuronal Cells Harboring a Nonsense Mutation in GDAP1 Gene. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Benslimane+N%22">Benslimane N</searchLink>; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.<br /><searchLink fieldCode="AU" term="%22Miressi+F%22">Miressi F</searchLink>; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.<br /><searchLink fieldCode="AU" term="%22Loret+C%22">Loret C</searchLink>; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.<br /><searchLink fieldCode="AU" term="%22Richard+L%22">Richard L</searchLink>; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.; CHU Limoges, Service de Neurologie, F-87000 Limoges, France.<br /><searchLink fieldCode="AU" term="%22Nizou+A%22">Nizou A</searchLink>; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.<br /><searchLink fieldCode="AU" term="%22Pyromali+I%22">Pyromali I</searchLink>; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.<br /><searchLink fieldCode="AU" term="%22Faye+PA%22">Faye PA</searchLink>; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.; Centre Hospitalier Universitaire (CHU) Limoges, Service de Biochimie et de Génétique Moléculaire, F-87000 Limoges, France.<br /><searchLink fieldCode="AU" term="%22Favreau+F%22">Favreau F</searchLink>; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.; Centre Hospitalier Universitaire (CHU) Limoges, Service de Biochimie et de Génétique Moléculaire, F-87000 Limoges, France.<br /><searchLink fieldCode="AU" term="%22Lejeune+F%22">Lejeune F</searchLink>; CNRS, Inserm, CHU Lille, UMR9020-U1277-CANTHER-Cancer Heterogeneity Plasticity and Resistance to Therapies, University of Lille, F-59000 Lille, France.<br /><searchLink fieldCode="AU" term="%22Lia+AS%22">Lia AS</searchLink>; NeurIT UR 20218, GEIST Institute, Faculté de Médecine de Limoges, University of Limoges, F-87000 Limoges, France.; Centre Hospitalier Universitaire (CHU) Limoges, Service de Biochimie et de Génétique Moléculaire, F-87000 Limoges, France.; Centre Hospitalo-Universitaire (CHU) Limoges, UF de Bioinformatique, F-87000 Limoges, France. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101238453%22">Pharmaceuticals (Basel, Switzerland)</searchLink> [Pharmaceuticals (Basel)] 2023 Jul 21; Vol. 16 (7). <i>Date of Electronic Publication: </i>2023 Jul 21. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22MDPI%22">MDPI </searchLink><i>Country of Publication: </i>Switzerland <i>NLM ID: </i>101238453 <i>Publication Model: </i>Electronic <i>Cited Medium: </i>Print <i>ISSN: </i>1424-8247 (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2214248247%22">14248247 </searchLink><i>NLM ISO Abbreviation: </i>Pharmaceuticals (Basel) <i>Subsets: </i>PubMed not MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=37513945 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.3390/ph16071034 Languages: – Code: eng Text: English Titles: – TitleFull: Amlexanox: Readthrough Induction and Nonsense-Mediated mRNA Decay Inhibition in a Charcot-Marie-Tooth Model of hiPSCs-Derived Neuronal Cells Harboring a Nonsense Mutation in GDAP1 Gene. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Benslimane N – PersonEntity: Name: NameFull: Miressi F – PersonEntity: Name: NameFull: Loret C – PersonEntity: Name: NameFull: Richard L – PersonEntity: Name: NameFull: Nizou A – PersonEntity: Name: NameFull: Pyromali I – PersonEntity: Name: NameFull: Faye PA – PersonEntity: Name: NameFull: Favreau F – PersonEntity: Name: NameFull: Lejeune F – PersonEntity: Name: NameFull: Lia AS IsPartOfRelationships: – BibEntity: Dates: – D: 21 M: 07 Text: 2023 Jul 21 Type: published Y: 2023 Identifiers: – Type: issn-print Value: 1424-8247 Numbering: – Type: volume Value: 16 – Type: issue Value: 7 Titles: – TitleFull: Pharmaceuticals (Basel, Switzerland) Type: main |
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