Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria.

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Title: Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria.
Authors: Kulasekararaj AG; King's College Hospital-NHS Foundation Trust, NIHR/Wellcome King's Clinical Research Facility, London, UK and King's College London, London., Lehtinen AE; Helsinki University Hospital Comprehensive Cancer Center and University of Helsinki, Helsinki., Forsyth C; Gosford Hospital, Gosford, NSW., Gandhi S; King's College Hospital-NHS Foundation Trust, NIHR/Wellcome King's Clinical Research Facility, London, UK and King's College London, London., Griffin M; St. James's University Hospital, Leeds., Körper S; University of Ulm, Institute of Transfusion Medicine, and Institute of Transfusion Medicine and Immunogenetics Ulm, Red Cross Blood Transfusion Service Baden-Württemberg-Hessen and University Hospital Ulm, Ulm., Mikala G; Central Hospital of Southern Pest National Institute of Hematology and Infectious Diseases, Budapest., Muus P; King's College Hospital-NHS Foundation Trust, NIHR/Wellcome King's Clinical Research Facility, London, UK and King's College London, London, UK; St. James's University Hospital, Leeds., Overgaard U; University Hospital Copenhagen, Copenhagen, Denmark., Patriquin CJ; University Health Network, Toronto, ON., Pullon H; Waikato Hospital, Hamilton., Shen YM; UT Southwestern Medical Center, Dallas, TX., Spearing R; Christchurch Hospital, Christchurch., Szer J; Peter MacCallum Cancer Centre and The Royal Melbourne Hospital, Melbourne, VIC., De la Borderie G; Peter MacCallum Cancer Centre and The Royal Melbourne Hospital, Melbourne, VIC., Duda PW; UCB Pharma, Cambridge, MA., Farzaneh-Far R; UCB Pharma, Cambridge, MA., Ragunathan S; UCB Pharma, Cambridge, MA., Sayegh CE; UCB Pharma, Cambridge, MA., Vadysirisack DD; UCB Pharma, Cambridge, MA., Schrezenmeier H; University of Ulm, Institute of Transfusion Medicine, and Institute of Transfusion Medicine and Immunogenetics Ulm, Red Cross Blood Transfusion Service Baden-Württemberg-Hessen and University Hospital Ulm, Ulm. h.schrezenmeier@blutspende.de.
Source: Haematologica [Haematologica] 2024 Mar 01; Vol. 109 (3), pp. 929-935. Date of Electronic Publication: 2024 Mar 01.
Publication Type: Clinical Trial, Phase II; Letter; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Ferrata Storti Foundation Country of Publication: Italy NLM ID: 0417435 Publication Model: Electronic Cited Medium: Internet ISSN: 1592-8721 (Electronic) Linking ISSN: 03906078 NLM ISO Abbreviation: Haematologica Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria.
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  Data: <searchLink fieldCode="AU" term="%22Kulasekararaj+AG%22">Kulasekararaj AG</searchLink>; King's College Hospital-NHS Foundation Trust, NIHR/Wellcome King's Clinical Research Facility, London, UK and King's College London, London.<br /><searchLink fieldCode="AU" term="%22Lehtinen+AE%22">Lehtinen AE</searchLink>; Helsinki University Hospital Comprehensive Cancer Center and University of Helsinki, Helsinki.<br /><searchLink fieldCode="AU" term="%22Forsyth+C%22">Forsyth C</searchLink>; Gosford Hospital, Gosford, NSW.<br /><searchLink fieldCode="AU" term="%22Gandhi+S%22">Gandhi S</searchLink>; King's College Hospital-NHS Foundation Trust, NIHR/Wellcome King's Clinical Research Facility, London, UK and King's College London, London.<br /><searchLink fieldCode="AU" term="%22Griffin+M%22">Griffin M</searchLink>; St. James's University Hospital, Leeds.<br /><searchLink fieldCode="AU" term="%22Körper+S%22">Körper S</searchLink>; University of Ulm, Institute of Transfusion Medicine, and Institute of Transfusion Medicine and Immunogenetics Ulm, Red Cross Blood Transfusion Service Baden-Württemberg-Hessen and University Hospital Ulm, Ulm.<br /><searchLink fieldCode="AU" term="%22Mikala+G%22">Mikala G</searchLink>; Central Hospital of Southern Pest National Institute of Hematology and Infectious Diseases, Budapest.<br /><searchLink fieldCode="AU" term="%22Muus+P%22">Muus P</searchLink>; King's College Hospital-NHS Foundation Trust, NIHR/Wellcome King's Clinical Research Facility, London, UK and King's College London, London, UK; St. James's University Hospital, Leeds.<br /><searchLink fieldCode="AU" term="%22Overgaard+U%22">Overgaard U</searchLink>; University Hospital Copenhagen, Copenhagen, Denmark.<br /><searchLink fieldCode="AU" term="%22Patriquin+CJ%22">Patriquin CJ</searchLink>; University Health Network, Toronto, ON.<br /><searchLink fieldCode="AU" term="%22Pullon+H%22">Pullon H</searchLink>; Waikato Hospital, Hamilton.<br /><searchLink fieldCode="AU" term="%22Shen+YM%22">Shen YM</searchLink>; UT Southwestern Medical Center, Dallas, TX.<br /><searchLink fieldCode="AU" term="%22Spearing+R%22">Spearing R</searchLink>; Christchurch Hospital, Christchurch.<br /><searchLink fieldCode="AU" term="%22Szer+J%22">Szer J</searchLink>; Peter MacCallum Cancer Centre and The Royal Melbourne Hospital, Melbourne, VIC.<br /><searchLink fieldCode="AU" term="%22De+la+Borderie+G%22">De la Borderie G</searchLink>; Peter MacCallum Cancer Centre and The Royal Melbourne Hospital, Melbourne, VIC.<br /><searchLink fieldCode="AU" term="%22Duda+PW%22">Duda PW</searchLink>; UCB Pharma, Cambridge, MA.<br /><searchLink fieldCode="AU" term="%22Farzaneh-Far+R%22">Farzaneh-Far R</searchLink>; UCB Pharma, Cambridge, MA.<br /><searchLink fieldCode="AU" term="%22Ragunathan+S%22">Ragunathan S</searchLink>; UCB Pharma, Cambridge, MA.<br /><searchLink fieldCode="AU" term="%22Sayegh+CE%22">Sayegh CE</searchLink>; UCB Pharma, Cambridge, MA.<br /><searchLink fieldCode="AU" term="%22Vadysirisack+DD%22">Vadysirisack DD</searchLink>; UCB Pharma, Cambridge, MA.<br /><searchLink fieldCode="AU" term="%22Schrezenmeier+H%22">Schrezenmeier H</searchLink>; University of Ulm, Institute of Transfusion Medicine, and Institute of Transfusion Medicine and Immunogenetics Ulm, Red Cross Blood Transfusion Service Baden-Württemberg-Hessen and University Hospital Ulm, Ulm. h.schrezenmeier@blutspende.de.
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  Data: <searchLink fieldCode="JN" term="%220417435%22">Haematologica</searchLink> [Haematologica] 2024 Mar 01; Vol. 109 (3), pp. 929-935. <i>Date of Electronic Publication: </i>2024 Mar 01.
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  Data: Clinical Trial, Phase II; Letter; Research Support, Non-U.S. Gov't
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Ferrata+Storti+Foundation%22">Ferrata Storti Foundation </searchLink><i>Country of Publication: </i>Italy <i>NLM ID: </i>0417435 <i>Publication Model: </i>Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1592-8721 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2203906078%22">03906078 </searchLink><i>NLM ISO Abbreviation: </i>Haematologica <i>Subsets: </i>MEDLINE
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        Value: 10.3324/haematol.2022.281780
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              Text: 2024 Mar 01
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