Effects of PK-guided prophylaxis on clinical outcomes and FVIII consumption for patients with moderate to severe Haemophilia A.

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Title: Effects of PK-guided prophylaxis on clinical outcomes and FVIII consumption for patients with moderate to severe Haemophilia A.
Authors: Young G; Children's Hospital Los Angeles, University of Southern California Keck School of Medicine, Los Angeles, California, USA., Callaghan MU; Children's Hospital of Michigan, Detroit, Michigan, USA., Balasa V; Hemotology/Oncology, Valley Children's Healthcare, Madera, California, USA., Soni A; Center for Inherited Blood Disorders, Orange, California, USA., Ahuja S; UH Rainbow Babies and Children's Hospital, Cleveland, Ohio, USA., Roberts JC; Bleeding & Clotting Disorders Institute, Peoria, Illinois, USA., Simpson ML; Rush University Medical Center, Chicago, Illinois, USA., Kizilocak H; Children's Hospital Los Angeles, University of Southern California Keck School of Medicine, Los Angeles, California, USA., Frick A; Trio Health Inc., Louisville, Colorado, USA., Mokdad AG; Takeda Pharmaceuticals U.S.A, 95 Hayden Ave, Cambridge, Massachusetts, USA., Xing S; Takeda Pharmaceuticals U.S.A, 95 Hayden Ave, Cambridge, Massachusetts, USA., Caicedo J; Takeda Pharmaceuticals U.S.A, 95 Hayden Ave, Cambridge, Massachusetts, USA.
Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2023 Sep; Vol. 29 (5), pp. 1234-1242. Date of Electronic Publication: 2023 Aug 08.
Publication Type: Journal Article
Journal Info: Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE
Database: MEDLINE Ultimate
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Description
ISSN:1365-2516
DOI:10.1111/hae.14826