Early treatment of type II SMA slows rate of progression of scoliosis.

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Title: Early treatment of type II SMA slows rate of progression of scoliosis.
Authors: Coratti G; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Lenkowicz J; Gemelli Generator, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy., Pera MC; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., D'Amico A; Department of Neurosciences, Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children's Hospital IRCCS, Roma, Italy., Bruno C; Center of Translational and Experimental Myology, and Dept. of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genova, IRCCS Istituto Giannina Gaslini, Genova, Italy., Gullì C; Department of Radiological and Hematological Sciences, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Brolatti N; Center of Translational and Experimental Myology, and Dept. of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genova, IRCCS Istituto Giannina Gaslini, Genova, Italy., Pedemonte M; Center of Translational and Experimental Myology, and Dept. of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genova, IRCCS Istituto Giannina Gaslini, Genova, Italy., Antonaci L; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Ricci M; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Capasso A; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Cicala G; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Cutrona C; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy., de Sanctis R; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Carnicella S; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Forcina N; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Cateruccia M; Department of Neurosciences, Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children's Hospital IRCCS, Roma, Italy., Damasio MB; Department of Radiology, IRCCS Istituto Giannina Gaslini, Genova, Italy., Labianca L; Department of Trauma and Orthopaedics, University of Rome La Sapienza, Rome, Italy., Manfroni F; Division of traumatology, spine surgery unit, Department of surgery and transplant, Bambino Gesù Children's Hospital IRCCS, Roma, Italy., Leone A; Department of Radiological and Hematological Sciences, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Bertini E; Department of Neurosciences, Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children's Hospital IRCCS, Roma, Italy., Pane M; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy., Patarnello S; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy., Valentini V; Department of Bioimaging Radiation Oncology and Hematology, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Università Cattolica S. Cuore, Roma, Italy., Mercuri E; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy eugeniomaria.mercuri@unicatt.it.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.
Source: Journal of neurology, neurosurgery, and psychiatry [J Neurol Neurosurg Psychiatry] 2024 Feb 14; Vol. 95 (3), pp. 235-240. Date of Electronic Publication: 2024 Feb 14.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: BMJ Publishing Group Country of Publication: England NLM ID: 2985191R Publication Model: Electronic Cited Medium: Internet ISSN: 1468-330X (Electronic) Linking ISSN: 00223050 NLM ISO Abbreviation: J Neurol Neurosurg Psychiatry Subsets: MEDLINE
Database: MEDLINE Ultimate
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PubType: Academic Journal
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  Data: Early treatment of type II SMA slows rate of progression of scoliosis.
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  Data: <searchLink fieldCode="AU" term="%22Coratti+G%22">Coratti G</searchLink>; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Lenkowicz+J%22">Lenkowicz J</searchLink>; Gemelli Generator, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Pera+MC%22">Pera MC</searchLink>; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22D'Amico+A%22">D'Amico A</searchLink>; Department of Neurosciences, Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children's Hospital IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Bruno+C%22">Bruno C</searchLink>; Center of Translational and Experimental Myology, and Dept. of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genova, IRCCS Istituto Giannina Gaslini, Genova, Italy.<br /><searchLink fieldCode="AU" term="%22Gullì+C%22">Gullì C</searchLink>; Department of Radiological and Hematological Sciences, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Brolatti+N%22">Brolatti N</searchLink>; Center of Translational and Experimental Myology, and Dept. of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genova, IRCCS Istituto Giannina Gaslini, Genova, Italy.<br /><searchLink fieldCode="AU" term="%22Pedemonte+M%22">Pedemonte M</searchLink>; Center of Translational and Experimental Myology, and Dept. of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genova, IRCCS Istituto Giannina Gaslini, Genova, Italy.<br /><searchLink fieldCode="AU" term="%22Antonaci+L%22">Antonaci L</searchLink>; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Ricci+M%22">Ricci M</searchLink>; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Capasso+A%22">Capasso A</searchLink>; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Cicala+G%22">Cicala G</searchLink>; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Cutrona+C%22">Cutrona C</searchLink>; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22de+Sanctis+R%22">de Sanctis R</searchLink>; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Carnicella+S%22">Carnicella S</searchLink>; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Forcina+N%22">Forcina N</searchLink>; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Cateruccia+M%22">Cateruccia M</searchLink>; Department of Neurosciences, Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children's Hospital IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Damasio+MB%22">Damasio MB</searchLink>; Department of Radiology, IRCCS Istituto Giannina Gaslini, Genova, Italy.<br /><searchLink fieldCode="AU" term="%22Labianca+L%22">Labianca L</searchLink>; Department of Trauma and Orthopaedics, University of Rome La Sapienza, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Manfroni+F%22">Manfroni F</searchLink>; Division of traumatology, spine surgery unit, Department of surgery and transplant, Bambino Gesù Children's Hospital IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Leone+A%22">Leone A</searchLink>; Department of Radiological and Hematological Sciences, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Bertini+E%22">Bertini E</searchLink>; Department of Neurosciences, Unit of Neuromuscular and Neurodegenerative Disorders, Bambino Gesù Children's Hospital IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Pane+M%22">Pane M</searchLink>; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Patarnello+S%22">Patarnello S</searchLink>; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Valentini+V%22">Valentini V</searchLink>; Department of Bioimaging Radiation Oncology and Hematology, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Università Cattolica S. Cuore, Roma, Italy.<br /><searchLink fieldCode="AU" term="%22Mercuri+E%22">Mercuri E</searchLink>; Pediatric Neurology, Università Cattolica del Sacro Cuore, Roma, Italy eugeniomaria.mercuri@unicatt.it.; Centro Clinico Nemo Pediatrico, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.
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  Data: <searchLink fieldCode="JN" term="%222985191R%22">Journal of neurology, neurosurgery, and psychiatry</searchLink> [J Neurol Neurosurg Psychiatry] 2024 Feb 14; Vol. 95 (3), pp. 235-240. <i>Date of Electronic Publication: </i>2024 Feb 14.
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