Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review.

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Title: Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review.
Authors: Szwec S; Institute of Human Biology and Evolution, Faculty of Biology, Adam Mickiewicz University, ul. Uniwersytetu Poznańskiego 6, 61-614, Poznań, Poland., Kapłucha Z; Institute of Human Biology and Evolution, Faculty of Biology, Adam Mickiewicz University, ul. Uniwersytetu Poznańskiego 6, 61-614, Poznań, Poland., Chamberlain JS; Department of Neurology, University of Washington School of Medicine, Seattle, WA, 98109-8055, USA.; Senator Paul D. Wellstone Muscular Dystrophy Specialized Research Center, University of Washington School of Medicine, Seattle, WA, 98109-8055, USA.; Department of Biochemistry, University of Washington School of Medicine, Seattle, WA, 98109-8055, USA.; Department of Medicine, University of Washington School of Medicine, Seattle, WA, 98109-8055, USA., Konieczny P; Institute of Human Biology and Evolution, Faculty of Biology, Adam Mickiewicz University, ul. Uniwersytetu Poznańskiego 6, 61-614, Poznań, Poland. patryk.konieczny@amu.edu.pl.
Source: BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy [BioDrugs] 2024 Jan; Vol. 38 (1), pp. 95-119. Date of Electronic Publication: 2023 Nov 02.
Publication Type: Comparative Study; Journal Article; Review
Journal Info: Publisher: Adis, Springer International Country of Publication: New Zealand NLM ID: 9705305 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1179-190X (Electronic) Linking ISSN: 11738804 NLM ISO Abbreviation: BioDrugs Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1179-190X
DOI:10.1007/s40259-023-00632-3