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Predicted deleterious variants in the human genome relevant to gene therapy with adeno-associated virus vectors.

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Bibliographic Details
Title:	Predicted deleterious variants in the human genome relevant to gene therapy with adeno-associated virus vectors.
Authors:	Rostami MR; Department of Genetic Medicine, Weill Cornell Medicine, New York, NY, USA., Leopold PL; Department of Genetic Medicine, Weill Cornell Medicine, New York, NY, USA., Vasquez JM; Department of Genetic Medicine, Weill Cornell Medicine, New York, NY, USA., de Mulder Rougvie M; Department of Genetic Medicine, Weill Cornell Medicine, New York, NY, USA., Al Shakaki A; Department of Genetic Medicine, Weill Cornell Medicine - Qatar, Doha, Qatar., Hssain AA; Hamad Medical Corporation, Doha, Qatar., Robay A; Department of Genetic Medicine, Weill Cornell Medicine - Qatar, Doha, Qatar., Hackett NR; Department of Genetic Medicine, Weill Cornell Medicine, New York, NY, USA., Mezey JG; Department of Genetic Medicine, Weill Cornell Medicine, New York, NY, USA.; Department of Biological Statistics and Computational Biology, Cornell University, Ithaca, NY, USA., Crystal RG; Department of Genetic Medicine, Weill Cornell Medicine, New York, NY, USA.
Source:	Molecular therapy. Methods & clinical development [Mol Ther Methods Clin Dev] 2023 Oct 13; Vol. 31, pp. 101136. Date of Electronic Publication: 2023 Oct 13 (Print Publication: 2023).
Publication Type:	Journal Article
Journal Info:	Publisher: Cell Press Country of Publication: United States NLM ID: 101624857 Publication Model: eCollection Cited Medium: Print ISSN: 2329-0501 (Print) Linking ISSN: 23290501 NLM ISO Abbreviation: Mol Ther Methods Clin Dev Subsets: PubMed not MEDLINE
Database:	MEDLINE Ultimate

Description
ISSN:	2329-0501
DOI:	10.1016/j.omtm.2023.101136