Pubertal development of transfusion-dependent thalassemia patients in the era of oral chelation with deferasirox: results from the French registry.

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Title: Pubertal development of transfusion-dependent thalassemia patients in the era of oral chelation with deferasirox: results from the French registry.
Authors: Broccia MV; Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille, France; Centre de Reference MCGRE, Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille. Mathilde.veneziano-broccia@ap-hm.fr., Vergier J; Service de Pediatrie Multidisciplinaire, Hopital de la Timone Enfants, AP-HM, Marseille., Benoit A; National Thalassemia Registry (NaThalY), Service de Genetique, Hopital La Timone Enfants, APHM, Marseille., Huguenin Y; Service d'Oncologie et d'Hematologie Pediatrique, Hopital Pellegrin, CHU de Bordeaux, Bordeaux., Lambilliotte A; Service d'Hematologie et d'Oncologie Pediatrique, Centre Hospitalo-Universitaire de Lille, Lille., Castex MP; Service d'Hemato-Oncologie Pediatrique, Hopital des Enfants, Toulouse., Gourdon S; Service d'Oncologie et Hematologie Pediatrique, Centre Hospitalier Universitaire de La Reunion, Saint Denis., Ithier G; Centre de Reference MCGRE, Unite d'Hematologie, Hopital Robert Debre, Assistance Publique-Hopitaux de Paris (AP-HP), Paris., Kebaili K; Institut d'Hematologie et d'Oncologie Pediatrique, Hospices Civils de Lyon, Lyon., Rohrlich P; Service d'Hematologie Pediatrique, CHU de Nice, Nice., Pondarre C; Centre de Reference MCGRE, Service de pediatrie, centre hospitalier intercommunal de Creteil, Creteil ; Inserm U955, Universite Paris-XII, Creteil., Chamouine A; Centre de Reference MCGRE, Service de Pediatrie, Centre Hospitalier de Mayotte, Mamoudzou,Mayotte., Simon P; Service d'Hematologie Pediatrique, CHU de Besanc_on, Besanc_on., Kpati KPA; Service de Pediatrie-Neonatologie-Medecine de l'Adolescent, GHEF-Site de Marne La Vallee, Jossigny., Allali S; Centre de Reference MCGRE, service de Pediatrie Generale, Hopital Necker-Enfants malades, AP-HP, Paris., Baron-Joly S; Service de Pediatrie, CHU de Nimes, Nimes., Bayart S; Service d'Hematologie Pediatrique, CHU de Rennes, Rennes., Billaud N; Service de Pediatrie, CHR Metz-Thionville, Metz., Brousse V; Centre de Référence MCGRE, Service d'Hematologie-Immunologie, Hopital Robert Debre, AP-HP, Paris., Dumesnil C; Service d'Hematologie Pediatrique, CHU de Rouen, Rouen., Garnier N; Institut d'Hematologie et d'Oncologie Pediatrique, Hospices Civils de Lyon, Lyon., Guichard I; Service de Medecine Interne, Hopital Nord, Saint-Etienne., Joseph L; Centre de Reference MCGRE, CIC Biotherapie, Hopital Necker-Enfants malades, AP-HP, Paris France., Kamdem A; Centre de Reference MCGRE, Service de Pediatrie, Centre Hospitalier Intercommunal de Creteil (CHIC), Creteil., Maitre J; Service de Pediatrie, CHR d'Orleans, Orleans., Mathey C; Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille., Paillard C; Service d'Hematologie et d'Oncologie Pediatrique, Hopital Hautepierre, Strasbourg., Phulpin A; Service d'Onco-hematologie Pediatrique, CHRU Nancy, Vandoeuvre les Nancy., Renard C; Institut d'Hematologie et d'Oncologie Pediatrique, Hospices Civils de Lyon, Lyon., Stoven C; Service de Pediatrie, CHU La Reunion, Groupe Hospitalier Sud Reunion., Touati M; Service d'Hematologie Clinique, CHU Limoges, Limoges., Trochu C; Service de Pediatrie, Hopital d'Enfants, Roubaix., Nafissi SM; Hopitaux de Brabois, CHRU de Nancy, Vandoeuvre les Nancy., Badens C; National Thalassemia Registry (NaThalY), Service de Genetique, Hopital La Timone Enfants, APHM, Marseille., Szepetowski S; Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille, France; Centre de Reference MCGRE, Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille., Thuret I; Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille, France; Centre de Reference MCGRE, Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille.
Source: Haematologica [Haematologica] 2024 Jul 01; Vol. 109 (7), pp. 2271-2276. Date of Electronic Publication: 2024 Jul 01.
Publication Type: Letter; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Ferrata Storti Foundation Country of Publication: Italy NLM ID: 0417435 Publication Model: Electronic Cited Medium: Internet ISSN: 1592-8721 (Electronic) Linking ISSN: 03906078 NLM ISO Abbreviation: Haematologica Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Pubertal development of transfusion-dependent thalassemia patients in the era of oral chelation with deferasirox: results from the French registry.
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  Data: <searchLink fieldCode="AU" term="%22Broccia+MV%22">Broccia MV</searchLink>; Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille, France; Centre de Reference MCGRE, Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille. Mathilde.veneziano-broccia@ap-hm.fr.<br /><searchLink fieldCode="AU" term="%22Vergier+J%22">Vergier J</searchLink>; Service de Pediatrie Multidisciplinaire, Hopital de la Timone Enfants, AP-HM, Marseille.<br /><searchLink fieldCode="AU" term="%22Benoit+A%22">Benoit A</searchLink>; National Thalassemia Registry (NaThalY), Service de Genetique, Hopital La Timone Enfants, APHM, Marseille.<br /><searchLink fieldCode="AU" term="%22Huguenin+Y%22">Huguenin Y</searchLink>; Service d'Oncologie et d'Hematologie Pediatrique, Hopital Pellegrin, CHU de Bordeaux, Bordeaux.<br /><searchLink fieldCode="AU" term="%22Lambilliotte+A%22">Lambilliotte A</searchLink>; Service d'Hematologie et d'Oncologie Pediatrique, Centre Hospitalo-Universitaire de Lille, Lille.<br /><searchLink fieldCode="AU" term="%22Castex+MP%22">Castex MP</searchLink>; Service d'Hemato-Oncologie Pediatrique, Hopital des Enfants, Toulouse.<br /><searchLink fieldCode="AU" term="%22Gourdon+S%22">Gourdon S</searchLink>; Service d'Oncologie et Hematologie Pediatrique, Centre Hospitalier Universitaire de La Reunion, Saint Denis.<br /><searchLink fieldCode="AU" term="%22Ithier+G%22">Ithier G</searchLink>; Centre de Reference MCGRE, Unite d'Hematologie, Hopital Robert Debre, Assistance Publique-Hopitaux de Paris (AP-HP), Paris.<br /><searchLink fieldCode="AU" term="%22Kebaili+K%22">Kebaili K</searchLink>; Institut d'Hematologie et d'Oncologie Pediatrique, Hospices Civils de Lyon, Lyon.<br /><searchLink fieldCode="AU" term="%22Rohrlich+P%22">Rohrlich P</searchLink>; Service d'Hematologie Pediatrique, CHU de Nice, Nice.<br /><searchLink fieldCode="AU" term="%22Pondarre+C%22">Pondarre C</searchLink>; Centre de Reference MCGRE, Service de pediatrie, centre hospitalier intercommunal de Creteil, Creteil ; Inserm U955, Universite Paris-XII, Creteil.<br /><searchLink fieldCode="AU" term="%22Chamouine+A%22">Chamouine A</searchLink>; Centre de Reference MCGRE, Service de Pediatrie, Centre Hospitalier de Mayotte, Mamoudzou,Mayotte.<br /><searchLink fieldCode="AU" term="%22Simon+P%22">Simon P</searchLink>; Service d'Hematologie Pediatrique, CHU de Besanc_on, Besanc_on.<br /><searchLink fieldCode="AU" term="%22Kpati+KPA%22">Kpati KPA</searchLink>; Service de Pediatrie-Neonatologie-Medecine de l'Adolescent, GHEF-Site de Marne La Vallee, Jossigny.<br /><searchLink fieldCode="AU" term="%22Allali+S%22">Allali S</searchLink>; Centre de Reference MCGRE, service de Pediatrie Generale, Hopital Necker-Enfants malades, AP-HP, Paris.<br /><searchLink fieldCode="AU" term="%22Baron-Joly+S%22">Baron-Joly S</searchLink>; Service de Pediatrie, CHU de Nimes, Nimes.<br /><searchLink fieldCode="AU" term="%22Bayart+S%22">Bayart S</searchLink>; Service d'Hematologie Pediatrique, CHU de Rennes, Rennes.<br /><searchLink fieldCode="AU" term="%22Billaud+N%22">Billaud N</searchLink>; Service de Pediatrie, CHR Metz-Thionville, Metz.<br /><searchLink fieldCode="AU" term="%22Brousse+V%22">Brousse V</searchLink>; Centre de Référence MCGRE, Service d'Hematologie-Immunologie, Hopital Robert Debre, AP-HP, Paris.<br /><searchLink fieldCode="AU" term="%22Dumesnil+C%22">Dumesnil C</searchLink>; Service d'Hematologie Pediatrique, CHU de Rouen, Rouen.<br /><searchLink fieldCode="AU" term="%22Garnier+N%22">Garnier N</searchLink>; Institut d'Hematologie et d'Oncologie Pediatrique, Hospices Civils de Lyon, Lyon.<br /><searchLink fieldCode="AU" term="%22Guichard+I%22">Guichard I</searchLink>; Service de Medecine Interne, Hopital Nord, Saint-Etienne.<br /><searchLink fieldCode="AU" term="%22Joseph+L%22">Joseph L</searchLink>; Centre de Reference MCGRE, CIC Biotherapie, Hopital Necker-Enfants malades, AP-HP, Paris France.<br /><searchLink fieldCode="AU" term="%22Kamdem+A%22">Kamdem A</searchLink>; Centre de Reference MCGRE, Service de Pediatrie, Centre Hospitalier Intercommunal de Creteil (CHIC), Creteil.<br /><searchLink fieldCode="AU" term="%22Maitre+J%22">Maitre J</searchLink>; Service de Pediatrie, CHR d'Orleans, Orleans.<br /><searchLink fieldCode="AU" term="%22Mathey+C%22">Mathey C</searchLink>; Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille.<br /><searchLink fieldCode="AU" term="%22Paillard+C%22">Paillard C</searchLink>; Service d'Hematologie et d'Oncologie Pediatrique, Hopital Hautepierre, Strasbourg.<br /><searchLink fieldCode="AU" term="%22Phulpin+A%22">Phulpin A</searchLink>; Service d'Onco-hematologie Pediatrique, CHRU Nancy, Vandoeuvre les Nancy.<br /><searchLink fieldCode="AU" term="%22Renard+C%22">Renard C</searchLink>; Institut d'Hematologie et d'Oncologie Pediatrique, Hospices Civils de Lyon, Lyon.<br /><searchLink fieldCode="AU" term="%22Stoven+C%22">Stoven C</searchLink>; Service de Pediatrie, CHU La Reunion, Groupe Hospitalier Sud Reunion.<br /><searchLink fieldCode="AU" term="%22Touati+M%22">Touati M</searchLink>; Service d'Hematologie Clinique, CHU Limoges, Limoges.<br /><searchLink fieldCode="AU" term="%22Trochu+C%22">Trochu C</searchLink>; Service de Pediatrie, Hopital d'Enfants, Roubaix.<br /><searchLink fieldCode="AU" term="%22Nafissi+SM%22">Nafissi SM</searchLink>; Hopitaux de Brabois, CHRU de Nancy, Vandoeuvre les Nancy.<br /><searchLink fieldCode="AU" term="%22Badens+C%22">Badens C</searchLink>; National Thalassemia Registry (NaThalY), Service de Genetique, Hopital La Timone Enfants, APHM, Marseille.<br /><searchLink fieldCode="AU" term="%22Szepetowski+S%22">Szepetowski S</searchLink>; Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille, France; Centre de Reference MCGRE, Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille.<br /><searchLink fieldCode="AU" term="%22Thuret+I%22">Thuret I</searchLink>; Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille, France; Centre de Reference MCGRE, Service d'Hematologie, Immunologie et Oncologie Pediatrique, Hopital La Timone Enfants, AP-HM, Marseille.
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