Long-Term Comparative Efficacy and Safety of Risdiplam and Nusinersen in Children with Type 1 Spinal Muscular Atrophy.
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| Title: | Long-Term Comparative Efficacy and Safety of Risdiplam and Nusinersen in Children with Type 1 Spinal Muscular Atrophy. |
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| Authors: | Kokaliaris C; F. Hoffmann-La Roche Ltd, Grenzacherstrasse 124, 4070, Basel, Switzerland. christos.kokaliaris@roche.com., Evans R; Visible Analytics, Oxford, UK., Hawkins N; Visible Analytics, Oxford, UK.; Institute of Health & Wellbeing, University of Glasgow, Glasgow, UK., Mahajan A; Bridge Medical Consulting Ltd, London, UK., Scott DA; Visible Analytics, Oxford, UK., Sutherland CS; F. Hoffmann-La Roche Ltd, Grenzacherstrasse 124, 4070, Basel, Switzerland., Nam J; F. Hoffmann-La Roche Ltd, Grenzacherstrasse 124, 4070, Basel, Switzerland., Sajeev G; Analysis Group, Inc, Boston, MA, USA. |
| Source: | Advances in therapy [Adv Ther] 2024 Jun; Vol. 41 (6), pp. 2414-2434. Date of Electronic Publication: 2024 May 05. |
| Publication Type: | Journal Article; Comparative Study; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: Health Communications Inc Country of Publication: United States NLM ID: 8611864 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1865-8652 (Electronic) Linking ISSN: 0741238X NLM ISO Abbreviation: Adv Ther Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 38705943 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Long-Term Comparative Efficacy and Safety of Risdiplam and Nusinersen in Children with Type 1 Spinal Muscular Atrophy. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Kokaliaris+C%22">Kokaliaris C</searchLink>; F. Hoffmann-La Roche Ltd, Grenzacherstrasse 124, 4070, Basel, Switzerland. christos.kokaliaris@roche.com.<br /><searchLink fieldCode="AU" term="%22Evans+R%22">Evans R</searchLink>; Visible Analytics, Oxford, UK.<br /><searchLink fieldCode="AU" term="%22Hawkins+N%22">Hawkins N</searchLink>; Visible Analytics, Oxford, UK.; Institute of Health & Wellbeing, University of Glasgow, Glasgow, UK.<br /><searchLink fieldCode="AU" term="%22Mahajan+A%22">Mahajan A</searchLink>; Bridge Medical Consulting Ltd, London, UK.<br /><searchLink fieldCode="AU" term="%22Scott+DA%22">Scott DA</searchLink>; Visible Analytics, Oxford, UK.<br /><searchLink fieldCode="AU" term="%22Sutherland+CS%22">Sutherland CS</searchLink>; F. Hoffmann-La Roche Ltd, Grenzacherstrasse 124, 4070, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Nam+J%22">Nam J</searchLink>; F. Hoffmann-La Roche Ltd, Grenzacherstrasse 124, 4070, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Sajeev+G%22">Sajeev G</searchLink>; Analysis Group, Inc, Boston, MA, USA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%228611864%22">Advances in therapy</searchLink> [Adv Ther] 2024 Jun; Vol. 41 (6), pp. 2414-2434. <i>Date of Electronic Publication: </i>2024 May 05. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Comparative Study; Research Support, Non-U.S. Gov't – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Health+Communications+Inc%22">Health Communications Inc </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>8611864 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1865-8652 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%220741238X%22">0741238X </searchLink><i>NLM ISO Abbreviation: </i>Adv Ther <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=38705943 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1007/s12325-024-02845-6 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 2414 Titles: – TitleFull: Long-Term Comparative Efficacy and Safety of Risdiplam and Nusinersen in Children with Type 1 Spinal Muscular Atrophy. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Kokaliaris C – PersonEntity: Name: NameFull: Evans R – PersonEntity: Name: NameFull: Hawkins N – PersonEntity: Name: NameFull: Mahajan A – PersonEntity: Name: NameFull: Scott DA – PersonEntity: Name: NameFull: Sutherland CS – PersonEntity: Name: NameFull: Nam J – PersonEntity: Name: NameFull: Sajeev G IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 06 Text: 2024 Jun Type: published Y: 2024 Identifiers: – Type: issn-electronic Value: 1865-8652 Numbering: – Type: volume Value: 41 – Type: issue Value: 6 Titles: – TitleFull: Advances in therapy Type: main |
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