Synergism of dual AAV gene therapy and rapamycin rescues GSDIII phenotype in muscle and liver. - Jauze L; Vie M; Miagoux Q; Rossiaud L; Vidal P; Montalvo-Romeral V; Saliba H; Jarrige M; Polveche H; Nozi J; Le Brun PR; Bocchialini L; et al. (JCI insight, 2024)