Reduced doses of emicizumab achieve good efficacy: Results from a national-wide multicentre real-world study in China.

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Title: Reduced doses of emicizumab achieve good efficacy: Results from a national-wide multicentre real-world study in China.
Authors: Xu Y; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin, China.; Tianjin Institutes of Health Science, Tianjin, China., Wang Y; Department of Hematology and Oncology, Shenzhen Children's Hospital, Shenzhen, China., Wu R; Hematology Oncology Center, National Center for Children's Health, Beijing Children's Hospital, Capital Medical University, Beijing, China., Zheng C; Department of Hematology, The First Affiliated Hospital of USTC, Division of Life Sciences and Medicine, University of Science and Technology of China, Hefei, China., Zhang L; Department of Hematology, Children's Hospital of Chongqing Medical University, Chongqing, China., Xu W; Division/Center of Pediatric Hematology-Oncology, the Children's Hospital of Zhejiang University School of Medicine, Hangzhou, China., Feng X; Pediatrics, Nanfang Hospital, Southern Medical University, Guangzhou, China., Wang H; Department of Hematology and Oncology, Xi'an Children's Hospital, Xi'an, China., Cao X; Department of Hematology, Suzhou BenQ Medical Center, The Affiliated BenQ Hospital of Nanjing Medical University, Suzhou, China., He L; Department of Pediatric, Guangzhou Women and Children's Medical Center, Guangzhou Medical University, Guangzhou, China., Xue T; Pediatrics, Xuzhou Star Hospital, Xuzhou, China., Jin M; Pediatrics, Xuzhou Star Hospital, Xuzhou, China., Xie B; Department of Hematology, Wenzhou People's Hospital, Wenzhou, China., Ling J; Department of Hematology, Children's Hospital of Soochow University, Suzhou, China., Sun L; Department of Pediatrics, Affiliated Hospital of Qingdao University, Qingdao, China., Su R; Department of Hematology, The First Affiliated Hospital of Xiamen University, Xiamen, China., Cheng H; Department of Hematology, Jiangxi Provincial People's Hospital Affiliated to Nanchang University, Nanchang, China., Fang Y; Department of Hematology/Oncology, Children's Hospital of Nanjing Medical University, Nanjing, China., Poon MC; Departments of Medicine, Paediatrics and Oncology, Cumming School of Medicine, University of Calgary, Calgary, Alberta, Canada., Liu W; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin, China.; Tianjin Institutes of Health Science, Tianjin, China., Zhang L; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin, China.; Tianjin Institutes of Health Science, Tianjin, China., Xue F; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin, China.; Tianjin Institutes of Health Science, Tianjin, China., Yang R; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin, China.; Tianjin Institutes of Health Science, Tianjin, China.
Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2024 Jul; Vol. 30 (4), pp. 959-969. Date of Electronic Publication: 2024 Jun 09.
Publication Type: Journal Article; Multicenter Study
Journal Info: Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1365-2516
DOI:10.1111/hae.15062