A Systematic Literature Review of the Natural History of Respiratory, Swallowing, Feeding, and Speech Functions in Spinal Muscular Atrophy (SMA).
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| Title: | A Systematic Literature Review of the Natural History of Respiratory, Swallowing, Feeding, and Speech Functions in Spinal Muscular Atrophy (SMA). |
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| Authors: | Martí Y; F. Hoffmann-La Roche Ltd, Basel, Switzerland., Aponte Ribero V; F. Hoffmann-La Roche Ltd, Basel, Switzerland., Batson S; Mtech Access Limited, Bicester, UK., Mitchell S; Mtech Access Limited, Bicester, UK., Gorni K; F. Hoffmann-La Roche Ltd, Basel, Switzerland., Gusset N; SMA Europe, Freiburg, Germany.; SMA Schweiz, Heimberg, Switzerland., Oskoui M; Departments of Pediatrics and Neurology Neurosurgery, McGill University, Montreal, Canada., Servais L; MDUK Oxford Neuromuscular Centre & NIHR Oxford Biomedical Research Centre, University of Oxford, Oxford, UK.; Department of Pediatrics, Division of Child Neurology, Centre de Références des Maladies Neuromusculaires, University Hospital Liège & University of Liège, Liège, Belgium., Deconinck N; Neuromuscular Reference Center, UZ Gent, Ghent, Belgium.; Department Paediatric Neurology, Centre de Références des Maladies Neuromusculaires, Hôpital Universitaire des Enfants Reine Fabiola (HUDERF), Hôpital Universitaire de Bruxelles, Université Libre de Bruxelles, Brussels, Belgium., McGrattan KE; Department of Speech-Language-Hearing Science, University of Minnesota, Minneapolis, MN, USA.; Department of Rehabilitation, Masonic Children's Hospital, Minneapolis, MN, USA., Mercuri E; Pediatric Neurology Institute, Catholic University and Nemo Pediatrico, Fondazione Policlinico Gemelli IRCCS, Rome, Italy.; Centro Clinico Nemo, Fondazione Policlinico Gemelli, IRCCS, Rome, Italy., Sutherland CS; F. Hoffmann-La Roche Ltd, Basel, Switzerland. |
| Source: | Journal of neuromuscular diseases [J Neuromuscul Dis] 2024; Vol. 11 (5), pp. 889-904. |
| Publication Type: | Journal Article; Systematic Review |
| Journal Info: | Publisher: SAGE Publications Country of Publication: United States NLM ID: 101649948 Publication Model: Print Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 38943396 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: A Systematic Literature Review of the Natural History of Respiratory, Swallowing, Feeding, and Speech Functions in Spinal Muscular Atrophy (SMA). – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Martí+Y%22">Martí Y</searchLink>; F. Hoffmann-La Roche Ltd, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Aponte+Ribero+V%22">Aponte Ribero V</searchLink>; F. Hoffmann-La Roche Ltd, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Batson+S%22">Batson S</searchLink>; Mtech Access Limited, Bicester, UK.<br /><searchLink fieldCode="AU" term="%22Mitchell+S%22">Mitchell S</searchLink>; Mtech Access Limited, Bicester, UK.<br /><searchLink fieldCode="AU" term="%22Gorni+K%22">Gorni K</searchLink>; F. Hoffmann-La Roche Ltd, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Gusset+N%22">Gusset N</searchLink>; SMA Europe, Freiburg, Germany.; SMA Schweiz, Heimberg, Switzerland.<br /><searchLink fieldCode="AU" term="%22Oskoui+M%22">Oskoui M</searchLink>; Departments of Pediatrics and Neurology Neurosurgery, McGill University, Montreal, Canada.<br /><searchLink fieldCode="AU" term="%22Servais+L%22">Servais L</searchLink>; MDUK Oxford Neuromuscular Centre & NIHR Oxford Biomedical Research Centre, University of Oxford, Oxford, UK.; Department of Pediatrics, Division of Child Neurology, Centre de Références des Maladies Neuromusculaires, University Hospital Liège & University of Liège, Liège, Belgium.<br /><searchLink fieldCode="AU" term="%22Deconinck+N%22">Deconinck N</searchLink>; Neuromuscular Reference Center, UZ Gent, Ghent, Belgium.; Department Paediatric Neurology, Centre de Références des Maladies Neuromusculaires, Hôpital Universitaire des Enfants Reine Fabiola (HUDERF), Hôpital Universitaire de Bruxelles, Université Libre de Bruxelles, Brussels, Belgium.<br /><searchLink fieldCode="AU" term="%22McGrattan+KE%22">McGrattan KE</searchLink>; Department of Speech-Language-Hearing Science, University of Minnesota, Minneapolis, MN, USA.; Department of Rehabilitation, Masonic Children's Hospital, Minneapolis, MN, USA.<br /><searchLink fieldCode="AU" term="%22Mercuri+E%22">Mercuri E</searchLink>; Pediatric Neurology Institute, Catholic University and Nemo Pediatrico, Fondazione Policlinico Gemelli IRCCS, Rome, Italy.; Centro Clinico Nemo, Fondazione Policlinico Gemelli, IRCCS, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Sutherland+CS%22">Sutherland CS</searchLink>; F. Hoffmann-La Roche Ltd, Basel, Switzerland. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101649948%22">Journal of neuromuscular diseases</searchLink> [J Neuromuscul Dis] 2024; Vol. 11 (5), pp. 889-904. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Systematic Review – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22SAGE+Publications%22">SAGE Publications </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101649948 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>2214-3602 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2222143599%22">22143599 </searchLink><i>NLM ISO Abbreviation: </i>J Neuromuscul Dis <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=38943396 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.3233/JND-230248 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 889 Titles: – TitleFull: A Systematic Literature Review of the Natural History of Respiratory, Swallowing, Feeding, and Speech Functions in Spinal Muscular Atrophy (SMA). Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Martí Y – PersonEntity: Name: NameFull: Aponte Ribero V – PersonEntity: Name: NameFull: Batson S – PersonEntity: Name: NameFull: Mitchell S – PersonEntity: Name: NameFull: Gorni K – PersonEntity: Name: NameFull: Gusset N – PersonEntity: Name: NameFull: Oskoui M – PersonEntity: Name: NameFull: Servais L – PersonEntity: Name: NameFull: Deconinck N – PersonEntity: Name: NameFull: McGrattan KE – PersonEntity: Name: NameFull: Mercuri E – PersonEntity: Name: NameFull: Sutherland CS IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 01 Text: 2024 Type: published Y: 2024 Identifiers: – Type: issn-electronic Value: 2214-3602 Numbering: – Type: volume Value: 11 – Type: issue Value: 5 Titles: – TitleFull: Journal of neuromuscular diseases Type: main |
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