Targeted knock-in of NCF1 cDNA into the NCF2 locus leads to myeloid phenotypic correction of p47 phox -deficient chronic granulomatous disease.
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| Title: | Targeted knock-in of NCF1 cDNA into the NCF2 locus leads to myeloid phenotypic correction of p47 phox -deficient chronic granulomatous disease. |
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| Authors: | Siow KM; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland., Güngör M; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland., Wrona D; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland., Raimondi F; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland., Pastukhov O; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland., Tsapogas P; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland., Menzi T; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland., Schmitz M; Department of Biochemistry, University of Zurich, 8057 Zurich, Switzerland., Kulcsár PI; Institute of Pharmacology and Toxicology, University of Zurich, 8057 Zurich, Switzerland., Schwank G; Institute of Pharmacology and Toxicology, University of Zurich, 8057 Zurich, Switzerland., Schulz A; Department of Pediatrics, University Medical Center Ulm, 89075 Ulm, Germany., Jinek M; Department of Biochemistry, University of Zurich, 8057 Zurich, Switzerland., Modlich U; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland., Siler U; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.; School of Life Sciences, Institute for Pharma Technology, University of Applied Sciences and Arts Northwestern Switzerland, 4132 Muttenz, Switzerland., Reichenbach J; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.; Department of Somatic Gene Therapy, University Children's Hospital Zurich, 8032 Zurich, Switzerland.; Center for Applied Biotechnology and Molecular Medicine (CABMM), University of Zurich, 8057 Zurich, Switzerland. |
| Source: | Molecular therapy. Nucleic acids [Mol Ther Nucleic Acids] 2024 May 24; Vol. 35 (3), pp. 102229. Date of Electronic Publication: 2024 May 24 (Print Publication: 2024). |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Cell Press Country of Publication: United States NLM ID: 101581621 Publication Model: eCollection Cited Medium: Print ISSN: 2162-2531 (Print) Linking ISSN: 21622531 NLM ISO Abbreviation: Mol Ther Nucleic Acids Subsets: PubMed not MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 38952440 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Targeted knock-in of NCF1 cDNA into the NCF2 locus leads to myeloid phenotypic correction of p47 <superscript>phox</superscript> -deficient chronic granulomatous disease. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Siow+KM%22">Siow KM</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Güngör+M%22">Güngör M</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Wrona+D%22">Wrona D</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Raimondi+F%22">Raimondi F</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Pastukhov+O%22">Pastukhov O</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Tsapogas+P%22">Tsapogas P</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Menzi+T%22">Menzi T</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Schmitz+M%22">Schmitz M</searchLink>; Department of Biochemistry, University of Zurich, 8057 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Kulcsár+PI%22">Kulcsár PI</searchLink>; Institute of Pharmacology and Toxicology, University of Zurich, 8057 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Schwank+G%22">Schwank G</searchLink>; Institute of Pharmacology and Toxicology, University of Zurich, 8057 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Schulz+A%22">Schulz A</searchLink>; Department of Pediatrics, University Medical Center Ulm, 89075 Ulm, Germany.<br /><searchLink fieldCode="AU" term="%22Jinek+M%22">Jinek M</searchLink>; Department of Biochemistry, University of Zurich, 8057 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Modlich+U%22">Modlich U</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Siler+U%22">Siler U</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.; School of Life Sciences, Institute for Pharma Technology, University of Applied Sciences and Arts Northwestern Switzerland, 4132 Muttenz, Switzerland.<br /><searchLink fieldCode="AU" term="%22Reichenbach+J%22">Reichenbach J</searchLink>; Division of Gene and Cell Therapy, Institute for Regenerative Medicine, University of Zurich, Schlieren, 8952 Zurich, Switzerland.; Department of Somatic Gene Therapy, University Children's Hospital Zurich, 8032 Zurich, Switzerland.; Center for Applied Biotechnology and Molecular Medicine (CABMM), University of Zurich, 8057 Zurich, Switzerland. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101581621%22">Molecular therapy. Nucleic acids</searchLink> [Mol Ther Nucleic Acids] 2024 May 24; Vol. 35 (3), pp. 102229. <i>Date of Electronic Publication: </i>2024 May 24 (<i>Print Publication: </i>2024). – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101581621 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Print <i>ISSN: </i>2162-2531 (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2221622531%22">21622531 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther Nucleic Acids <i>Subsets: </i>PubMed not MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=38952440 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1016/j.omtn.2024.102229 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 102229 Titles: – TitleFull: Targeted knock-in of NCF1 cDNA into the NCF2 locus leads to myeloid phenotypic correction of p47 phox -deficient chronic granulomatous disease. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Siow KM – PersonEntity: Name: NameFull: Güngör M – PersonEntity: Name: NameFull: Wrona D – PersonEntity: Name: NameFull: Raimondi F – PersonEntity: Name: NameFull: Pastukhov O – PersonEntity: Name: NameFull: Tsapogas P – PersonEntity: Name: NameFull: Menzi T – PersonEntity: Name: NameFull: Schmitz M – PersonEntity: Name: NameFull: Kulcsár PI – PersonEntity: Name: NameFull: Schwank G – PersonEntity: Name: NameFull: Schulz A – PersonEntity: Name: NameFull: Jinek M – PersonEntity: Name: NameFull: Modlich U – PersonEntity: Name: NameFull: Siler U – PersonEntity: Name: NameFull: Reichenbach J IsPartOfRelationships: – BibEntity: Dates: – D: 24 M: 05 Text: 2024 May 24 Type: published Y: 2024 Identifiers: – Type: issn-print Value: 2162-2531 Numbering: – Type: volume Value: 35 – Type: issue Value: 3 Titles: – TitleFull: Molecular therapy. Nucleic acids Type: main |
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