Setrusumab for the treatment of osteogenesis imperfecta: 12-month results from the phase 2b asteroid study.

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Title: Setrusumab for the treatment of osteogenesis imperfecta: 12-month results from the phase 2b asteroid study.
Authors: Glorieux FH; Departments of Surgery, Pediatrics and Human Genetics, Shriners Hospitals for Children, McGill University, Montreal, Quebec H4A 0A9, Canada., Langdahl B; Department of Endocrinology and Internal Medicine, Aarhus University Hospital, Aarhus, Middle Jutland 8200, Denmark.; Department of Clinical Medicine, Aarhus University, Aarhus, Middle Jutland 8200, Denmark., Chapurlat R; Inserm UMR 1033, Edouard Herriot Hospital, 69372 Lyon cedex 08, France., De Beur SJ; Department of Medicine, Johns Hopkins University School of Medicine, Baltimore, MD 21287, United States., Sutton VR; Department of Molecular & Human Genetics, Baylor College of Medicine & Texas Children's Hospital, Houston, TX 77030, United States., Poole KES; Department of Medicine & Cambridge NIHR Biomedical Research Centre, University of Cambridge, Cambridge CB3 0FA, United Kingdom., Dahir KM; Division of Endocrinology, Vanderbilt University Medical Center, Nashville, TN 37232, United States., Orwoll ES; Division of Endocrinology, Diabetes and Clinical Nutrition, School of Medicine, Oregon Health & Sciences University, Portland, OR 97239, United States., Willie BM; Faculty of Dental Medicine and Oral Health Sciences, McGill University, Montreal H3A 2T5, Canada.; Shriners Hospitals for Children, Montreal, Quebec H4A 0A9, Canada., Mikolajewicz N; Faculty of Dental Medicine and Oral Health Sciences, McGill University, Montreal H3A 2T5, Canada.; Shriners Hospitals for Children, Montreal, Quebec H4A 0A9, Canada., Zimmermann E; Faculty of Dental Medicine and Oral Health Sciences, McGill University, Montreal H3A 2T5, Canada.; Shriners Hospitals for Children, Montreal, Quebec H4A 0A9, Canada., Hosseinitabatabaei S; Faculty of Dental Medicine and Oral Health Sciences, McGill University, Montreal H3A 2T5, Canada.; Shriners Hospitals for Children, Montreal, Quebec H4A 0A9, Canada., Ominsky MS; Ultragenyx Pharmaceutical Inc., Novato, CA 94949, United States., Saville C; ICON Plc, Leopardstown, Dublin D 18, Ireland., Clancy J; Mereo BioPharma, London W16 0QF, United Kingdom., MacKinnon A; Mereo BioPharma, London W16 0QF, United Kingdom., Mistry A; Mereo BioPharma, London W16 0QF, United Kingdom., Javaid MK; Nuffield Department of Orthopaedics, Rheumatology and Musculoskeletal Sciences (NDORMS), University of Oxford, Wellington Square, Oxford OX1 2JD, United Kingdom.
Source: Journal of bone and mineral research : the official journal of the American Society for Bone and Mineral Research [J Bone Miner Res] 2024 Sep 02; Vol. 39 (9), pp. 1215-1228.
Publication Type: Journal Article; Clinical Trial, Phase II; Randomized Controlled Trial; Multicenter Study; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 8610640 Publication Model: Print Cited Medium: Internet ISSN: 1523-4681 (Electronic) Linking ISSN: 08840431 NLM ISO Abbreviation: J Bone Miner Res Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Setrusumab for the treatment of osteogenesis imperfecta: 12-month results from the phase 2b asteroid study.
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  Data: <searchLink fieldCode="AU" term="%22Glorieux+FH%22">Glorieux FH</searchLink>; Departments of Surgery, Pediatrics and Human Genetics, Shriners Hospitals for Children, McGill University, Montreal, Quebec H4A 0A9, Canada.<br /><searchLink fieldCode="AU" term="%22Langdahl+B%22">Langdahl B</searchLink>; Department of Endocrinology and Internal Medicine, Aarhus University Hospital, Aarhus, Middle Jutland 8200, Denmark.; Department of Clinical Medicine, Aarhus University, Aarhus, Middle Jutland 8200, Denmark.<br /><searchLink fieldCode="AU" term="%22Chapurlat+R%22">Chapurlat R</searchLink>; Inserm UMR 1033, Edouard Herriot Hospital, 69372 Lyon cedex 08, France.<br /><searchLink fieldCode="AU" term="%22De+Beur+SJ%22">De Beur SJ</searchLink>; Department of Medicine, Johns Hopkins University School of Medicine, Baltimore, MD 21287, United States.<br /><searchLink fieldCode="AU" term="%22Sutton+VR%22">Sutton VR</searchLink>; Department of Molecular & Human Genetics, Baylor College of Medicine & Texas Children's Hospital, Houston, TX 77030, United States.<br /><searchLink fieldCode="AU" term="%22Poole+KES%22">Poole KES</searchLink>; Department of Medicine & Cambridge NIHR Biomedical Research Centre, University of Cambridge, Cambridge CB3 0FA, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Dahir+KM%22">Dahir KM</searchLink>; Division of Endocrinology, Vanderbilt University Medical Center, Nashville, TN 37232, United States.<br /><searchLink fieldCode="AU" term="%22Orwoll+ES%22">Orwoll ES</searchLink>; Division of Endocrinology, Diabetes and Clinical Nutrition, School of Medicine, Oregon Health & Sciences University, Portland, OR 97239, United States.<br /><searchLink fieldCode="AU" term="%22Willie+BM%22">Willie BM</searchLink>; Faculty of Dental Medicine and Oral Health Sciences, McGill University, Montreal H3A 2T5, Canada.; Shriners Hospitals for Children, Montreal, Quebec H4A 0A9, Canada.<br /><searchLink fieldCode="AU" term="%22Mikolajewicz+N%22">Mikolajewicz N</searchLink>; Faculty of Dental Medicine and Oral Health Sciences, McGill University, Montreal H3A 2T5, Canada.; Shriners Hospitals for Children, Montreal, Quebec H4A 0A9, Canada.<br /><searchLink fieldCode="AU" term="%22Zimmermann+E%22">Zimmermann E</searchLink>; Faculty of Dental Medicine and Oral Health Sciences, McGill University, Montreal H3A 2T5, Canada.; Shriners Hospitals for Children, Montreal, Quebec H4A 0A9, Canada.<br /><searchLink fieldCode="AU" term="%22Hosseinitabatabaei+S%22">Hosseinitabatabaei S</searchLink>; Faculty of Dental Medicine and Oral Health Sciences, McGill University, Montreal H3A 2T5, Canada.; Shriners Hospitals for Children, Montreal, Quebec H4A 0A9, Canada.<br /><searchLink fieldCode="AU" term="%22Ominsky+MS%22">Ominsky MS</searchLink>; Ultragenyx Pharmaceutical Inc., Novato, CA 94949, United States.<br /><searchLink fieldCode="AU" term="%22Saville+C%22">Saville C</searchLink>; ICON Plc, Leopardstown, Dublin D 18, Ireland.<br /><searchLink fieldCode="AU" term="%22Clancy+J%22">Clancy J</searchLink>; Mereo BioPharma, London W16 0QF, United Kingdom.<br /><searchLink fieldCode="AU" term="%22MacKinnon+A%22">MacKinnon A</searchLink>; Mereo BioPharma, London W16 0QF, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Mistry+A%22">Mistry A</searchLink>; Mereo BioPharma, London W16 0QF, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Javaid+MK%22">Javaid MK</searchLink>; Nuffield Department of Orthopaedics, Rheumatology and Musculoskeletal Sciences (NDORMS), University of Oxford, Wellington Square, Oxford OX1 2JD, United Kingdom.
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  Data: <searchLink fieldCode="JN" term="%228610640%22">Journal of bone and mineral research : the official journal of the American Society for Bone and Mineral Research</searchLink> [J Bone Miner Res] 2024 Sep 02; Vol. 39 (9), pp. 1215-1228.
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  Data: Journal Article; Clinical Trial, Phase II; Randomized Controlled Trial; Multicenter Study; Research Support, Non-U.S. Gov't
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Oxford+University+Press%22">Oxford University Press </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>8610640 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>1523-4681 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2208840431%22">08840431 </searchLink><i>NLM ISO Abbreviation: </i>J Bone Miner Res <i>Subsets: </i>MEDLINE
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        Value: 10.1093/jbmr/zjae112
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        Text: English
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