Ribosomal Frameshifting Selectively Modulates the Assembly, Function, and Pharmacological Rescue of a Misfolded CFTR Variant.

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Title: Ribosomal Frameshifting Selectively Modulates the Assembly, Function, and Pharmacological Rescue of a Misfolded CFTR Variant.
Authors: Carmody P; Department of Chemistry, Indiana University Bloomington, Bloomington, IN, USA 47401., Roushar FJ; Department of Chemistry, Indiana University Bloomington, Bloomington, IN, USA 47401., Tedman A; The James Tarpo Jr. and Margaret Tarpo Department of Chemistry, Purdue University, West Lafayette, IN, USA 47907., Wang W; Department of Medicine, University of Alabama at Birmingham, Birmingham, AL, USA 35233., Herwig M; Department of Chemistry, Vanderbilt University, Nashville, TN, USA 37240., Kim M; Department of Chemistry, Vanderbilt University, Nashville, TN, USA 37240.; Program in Chemical and Physical Biology, Vanderbilt University, Nashville, TN, USA 37240., McDonald EF; Department of Chemistry, Vanderbilt University, Nashville, TN, USA 37240., Noguera K; Department of Chemistry, Indiana University Bloomington, Bloomington, IN, USA 47401., Wong-Roushar J; Department of Chemistry, Indiana University Bloomington, Bloomington, IN, USA 47401., Poirier JL; Department of Chemistry, Indiana University Bloomington, Bloomington, IN, USA 47401., Zelt NB; Department of Chemistry, Indiana University Bloomington, Bloomington, IN, USA 47401., Pockrass BT; Department of Chemistry, Indiana University Bloomington, Bloomington, IN, USA 47401., McKee AG; Department of Chemistry, Indiana University Bloomington, Bloomington, IN, USA 47401., Kuntz CP; The James Tarpo Jr. and Margaret Tarpo Department of Chemistry, Purdue University, West Lafayette, IN, USA 47907., Raju SV; Department of Medicine, University of Alabama at Birmingham, Birmingham, AL, USA 35233., Plate L; Department of Chemistry, Vanderbilt University, Nashville, TN, USA 37240.; Department of Biological Sciences, Vanderbilt University, Nashville, TN, USA 37240., Penn WD; Department of Chemistry, Indiana University Bloomington, Bloomington, IN, USA 47401., Schlebach JP; The James Tarpo Jr. and Margaret Tarpo Department of Chemistry, Purdue University, West Lafayette, IN, USA 47907.
Source: BioRxiv : the preprint server for biology [bioRxiv] 2024 Jul 23. Date of Electronic Publication: 2024 Jul 23.
Publication Type: Journal Article; Preprint
Journal Info: Country of Publication: United States NLM ID: 101680187 Publication Model: Electronic Cited Medium: Internet ISSN: 2692-8205 (Electronic) Linking ISSN: 26928205 NLM ISO Abbreviation: bioRxiv Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2692-8205
DOI:10.1101/2023.05.02.539166