Targeting the transferrin receptor to transport antisense oligonucleotides across the mammalian blood-brain barrier.
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| Title: | Targeting the transferrin receptor to transport antisense oligonucleotides across the mammalian blood-brain barrier. |
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| Authors: | Barker SJ; Denali Therapeutics Inc., South San Francisco, CA, USA., Thayer MB; Denali Therapeutics Inc., South San Francisco, CA, USA., Kim C; Denali Therapeutics Inc., South San Francisco, CA, USA., Tatarakis D; Denali Therapeutics Inc., South San Francisco, CA, USA., Simon MJ; Denali Therapeutics Inc., South San Francisco, CA, USA., Dial R; Denali Therapeutics Inc., South San Francisco, CA, USA., Nilewski L; Denali Therapeutics Inc., South San Francisco, CA, USA., Wells RC; Denali Therapeutics Inc., South San Francisco, CA, USA., Zhou Y; Denali Therapeutics Inc., South San Francisco, CA, USA., Afetian M; Ionis Pharmaceuticals, Carlsbad, CA, USA., Akkapeddi P; Denali Therapeutics Inc., South San Francisco, CA, USA., Chappell A; Ionis Pharmaceuticals, Carlsbad, CA, USA., Chew KS; Denali Therapeutics Inc., South San Francisco, CA, USA., Chow J; Denali Therapeutics Inc., South San Francisco, CA, USA., Clemens A; Denali Therapeutics Inc., South San Francisco, CA, USA., Discenza CB; Denali Therapeutics Inc., South San Francisco, CA, USA., Dugas JC; Denali Therapeutics Inc., South San Francisco, CA, USA., Dwyer C; Ionis Pharmaceuticals, Carlsbad, CA, USA., Earr T; Denali Therapeutics Inc., South San Francisco, CA, USA., Ha C; Denali Therapeutics Inc., South San Francisco, CA, USA., Ho YS; Denali Therapeutics Inc., South San Francisco, CA, USA., Huynh D; Denali Therapeutics Inc., South San Francisco, CA, USA., Lozano EI; Denali Therapeutics Inc., South San Francisco, CA, USA., Jayaraman S; Denali Therapeutics Inc., South San Francisco, CA, USA., Kwan W; Denali Therapeutics Inc., South San Francisco, CA, USA., Mahon C; Denali Therapeutics Inc., South San Francisco, CA, USA., Pizzo M; Denali Therapeutics Inc., South San Francisco, CA, USA., Robles-Colmenares Y; Denali Therapeutics Inc., South San Francisco, CA, USA., Roche E; Denali Therapeutics Inc., South San Francisco, CA, USA., Sanders L; Denali Therapeutics Inc., South San Francisco, CA, USA., Stergioulis A; Denali Therapeutics Inc., South San Francisco, CA, USA., Tong R; Denali Therapeutics Inc., South San Francisco, CA, USA., Tran H; Denali Therapeutics Inc., South San Francisco, CA, USA., Zuchero Y; Denali Therapeutics Inc., South San Francisco, CA, USA., Estrada AA; Denali Therapeutics Inc., South San Francisco, CA, USA., Gadkar K; Denali Therapeutics Inc., South San Francisco, CA, USA., Koth CMM; Denali Therapeutics Inc., South San Francisco, CA, USA., Sanchez PE; Denali Therapeutics Inc., South San Francisco, CA, USA., Thorne RG; Denali Therapeutics Inc., South San Francisco, CA, USA., Watts RJ; Denali Therapeutics Inc., South San Francisco, CA, USA., Sandmann T; Denali Therapeutics Inc., South San Francisco, CA, USA., Kane LA; Denali Therapeutics Inc., South San Francisco, CA, USA., Rigo F; Ionis Pharmaceuticals, Carlsbad, CA, USA., Dennis MS; Denali Therapeutics Inc., South San Francisco, CA, USA., Lewcock JW; Denali Therapeutics Inc., South San Francisco, CA, USA., DeVos SL; Denali Therapeutics Inc., South San Francisco, CA, USA. |
| Source: | Science translational medicine [Sci Transl Med] 2024 Aug 14; Vol. 16 (760), pp. eadi2245. Date of Electronic Publication: 2024 Aug 14. |
| Publication Type: | Journal Article; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: American Association for the Advancement of Science Country of Publication: United States NLM ID: 101505086 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1946-6242 (Electronic) Linking ISSN: 19466234 NLM ISO Abbreviation: Sci Transl Med Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 39141703 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Targeting the transferrin receptor to transport antisense oligonucleotides across the mammalian blood-brain barrier. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Barker+SJ%22">Barker SJ</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Thayer+MB%22">Thayer MB</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Kim+C%22">Kim C</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Tatarakis+D%22">Tatarakis D</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Simon+MJ%22">Simon MJ</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Dial+R%22">Dial R</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Nilewski+L%22">Nilewski L</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Wells+RC%22">Wells RC</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Zhou+Y%22">Zhou Y</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Afetian+M%22">Afetian M</searchLink>; Ionis Pharmaceuticals, Carlsbad, CA, USA.<br /><searchLink fieldCode="AU" term="%22Akkapeddi+P%22">Akkapeddi P</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Chappell+A%22">Chappell A</searchLink>; Ionis Pharmaceuticals, Carlsbad, CA, USA.<br /><searchLink fieldCode="AU" term="%22Chew+KS%22">Chew KS</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Chow+J%22">Chow J</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Clemens+A%22">Clemens A</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Discenza+CB%22">Discenza CB</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Dugas+JC%22">Dugas JC</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Dwyer+C%22">Dwyer C</searchLink>; Ionis Pharmaceuticals, Carlsbad, CA, USA.<br /><searchLink fieldCode="AU" term="%22Earr+T%22">Earr T</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Ha+C%22">Ha C</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Ho+YS%22">Ho YS</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Huynh+D%22">Huynh D</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Lozano+EI%22">Lozano EI</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Jayaraman+S%22">Jayaraman S</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Kwan+W%22">Kwan W</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Mahon+C%22">Mahon C</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Pizzo+M%22">Pizzo M</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Robles-Colmenares+Y%22">Robles-Colmenares Y</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Roche+E%22">Roche E</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Sanders+L%22">Sanders L</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Stergioulis+A%22">Stergioulis A</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Tong+R%22">Tong R</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Tran+H%22">Tran H</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Zuchero+Y%22">Zuchero Y</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Estrada+AA%22">Estrada AA</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Gadkar+K%22">Gadkar K</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Koth+CMM%22">Koth CMM</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Sanchez+PE%22">Sanchez PE</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Thorne+RG%22">Thorne RG</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Watts+RJ%22">Watts RJ</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Sandmann+T%22">Sandmann T</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Kane+LA%22">Kane LA</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Rigo+F%22">Rigo F</searchLink>; Ionis Pharmaceuticals, Carlsbad, CA, USA.<br /><searchLink fieldCode="AU" term="%22Dennis+MS%22">Dennis MS</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Lewcock+JW%22">Lewcock JW</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22DeVos+SL%22">DeVos SL</searchLink>; Denali Therapeutics Inc., South San Francisco, CA, USA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101505086%22">Science translational medicine</searchLink> [Sci Transl Med] 2024 Aug 14; Vol. 16 (760), pp. eadi2245. <i>Date of Electronic Publication: </i>2024 Aug 14. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Research Support, Non-U.S. Gov't – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22American+Association+for+the+Advancement+of+Science%22">American Association for the Advancement of Science </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101505086 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1946-6242 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2219466234%22">19466234 </searchLink><i>NLM ISO Abbreviation: </i>Sci Transl Med <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=39141703 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1126/scitranslmed.adi2245 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: eadi2245 Titles: – TitleFull: Targeting the transferrin receptor to transport antisense oligonucleotides across the mammalian blood-brain barrier. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Barker SJ – PersonEntity: Name: NameFull: Thayer MB – PersonEntity: Name: NameFull: Kim C – PersonEntity: Name: NameFull: Tatarakis D – PersonEntity: Name: NameFull: Simon MJ – PersonEntity: Name: NameFull: Dial R – PersonEntity: Name: NameFull: Nilewski L – PersonEntity: Name: NameFull: Wells RC – PersonEntity: Name: NameFull: Zhou Y – PersonEntity: Name: NameFull: Afetian M – PersonEntity: Name: NameFull: Akkapeddi P – PersonEntity: Name: NameFull: Chappell A – PersonEntity: Name: NameFull: Chew KS – PersonEntity: Name: NameFull: Chow J – PersonEntity: Name: NameFull: Clemens A – PersonEntity: Name: NameFull: Discenza CB – PersonEntity: Name: NameFull: Dugas JC – PersonEntity: Name: NameFull: Dwyer C – PersonEntity: Name: NameFull: Earr T – PersonEntity: Name: NameFull: Ha C – PersonEntity: Name: NameFull: Ho YS – PersonEntity: Name: NameFull: Huynh D – PersonEntity: Name: NameFull: Lozano EI – PersonEntity: Name: NameFull: Jayaraman S – PersonEntity: Name: NameFull: Kwan W – PersonEntity: Name: NameFull: Mahon C – PersonEntity: Name: NameFull: Pizzo M – PersonEntity: Name: NameFull: Robles-Colmenares Y – PersonEntity: Name: NameFull: Roche E – PersonEntity: Name: NameFull: Sanders L – PersonEntity: Name: NameFull: Stergioulis A – PersonEntity: Name: NameFull: Tong R – PersonEntity: Name: NameFull: Tran H – PersonEntity: Name: NameFull: Zuchero Y – PersonEntity: Name: NameFull: Estrada AA – PersonEntity: Name: NameFull: Gadkar K – PersonEntity: Name: NameFull: Koth CMM – PersonEntity: Name: NameFull: Sanchez PE – PersonEntity: Name: NameFull: Thorne RG – PersonEntity: Name: NameFull: Watts RJ – PersonEntity: Name: NameFull: Sandmann T – PersonEntity: Name: NameFull: Kane LA – PersonEntity: Name: NameFull: Rigo F – PersonEntity: Name: NameFull: Dennis MS – PersonEntity: Name: NameFull: Lewcock JW – PersonEntity: Name: NameFull: DeVos SL IsPartOfRelationships: – BibEntity: Dates: – D: 14 M: 08 Text: 2024 Aug 14 Type: published Y: 2024 Identifiers: – Type: issn-electronic Value: 1946-6242 Numbering: – Type: volume Value: 16 – Type: issue Value: 760 Titles: – TitleFull: Science translational medicine Type: main |
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