Characterization and natural history of patients with LMNA-related dilated cardiomyopathy in the phase 3 REALM-DCM trial.

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Title: Characterization and natural history of patients with LMNA-related dilated cardiomyopathy in the phase 3 REALM-DCM trial.
Authors: Garcia-Pavia P; Hospital Universitario Puerta de Hierro Majadahonda, Madrid, Spain.; Instituto de Investigación Sanitaria Puerta de Hierro-Segovia de Arana (IDIPHISA), Madrid, Spain.; Centro de Investigación en Red en Enfermedades Cardiovasculares (CIBERCV), Madrid, Spain.; Universidad Francisco de Vitoria (UFV), Madrid, Spain.; Centro Nacional de Investigaciones Cardiovasculares (CNIC), Madrid, Spain., Lakdawala NK; Brigham and Women's Hospital, Boston, Massachusetts, USA.; Harvard Medical School, Boston, Massachusetts, USA., Sinagra G; Cardiothoracovascular Department, Azienda Sanitaria Universitaria Giuliano Isontina (ASUGI), University of Trieste, Trieste, Italy., Ripoll-Vera T; Hospital Universitario Son Llatzer, Mallorca, Spain.; Health Research Institute of the Balearic Islands (IdISBa), Mallorca, Spain.; Department of Medicine, University of the Balearic Islands, Mallorca, Spain.; Centro de Investigación Biomédica en Red de Fisiopatología de la Obesidad y Nutrición (CIBERobn), Institute of Health Carlos III, Madrid, Spain., Afshar K; Intermountain Heart Institute, Salt Lake City, Utah, USA., Priori SG; Centro Nacional de Investigaciones Cardiovasculares (CNIC), Madrid, Spain.; IRCCS Istituti Clinici Scientifici Maugeri SpA SB of Pavia, Pavia, Italy.; Department of Molecular Medicine, University of Pavia, Pavia, Italy., Ware JS; National Heart & Lung Institute and MRC London Institute of Medical Sciences, Imperial College London, London, UK.; Royal Brompton & Harefield Hospitals, Guy's and St Thomas' NHS Foundation Trust, London, UK., Owens A; University of Pennsylvania Heart and Vascular Center, Philadelphia, Pennsylvania, USA., Li H; Pfizer Inc., Collegeville, Pennsylvania, USA., Angeli FS; Pfizer Inc., Collegeville, Pennsylvania, USA., Elliott P; University College London, London, UK., MacRae CA; Brigham and Women's Hospital, Boston, Massachusetts, USA.; Harvard Medical School, Boston, Massachusetts, USA., Judge DP; Cardiovascular Genetics, Medical University of South Carolina, Charleston, South Carolina, USA.
Source: ESC heart failure [ESC Heart Fail] 2024 Dec; Vol. 11 (6), pp. 4201-4208. Date of Electronic Publication: 2024 Aug 15.
Publication Type: Journal Article; Clinical Trial, Phase III; Randomized Controlled Trial; Multicenter Study
Journal Info: Publisher: John Wiley & Sons Ltd on behalf of the European Society of Cardiology Country of Publication: England NLM ID: 101669191 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2055-5822 (Electronic) Linking ISSN: 20555822 NLM ISO Abbreviation: ESC Heart Fail Subsets: MEDLINE
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  Data: Characterization and natural history of patients with LMNA-related dilated cardiomyopathy in the phase 3 REALM-DCM trial.
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  Data: <searchLink fieldCode="AU" term="%22Garcia-Pavia+P%22">Garcia-Pavia P</searchLink>; Hospital Universitario Puerta de Hierro Majadahonda, Madrid, Spain.; Instituto de Investigación Sanitaria Puerta de Hierro-Segovia de Arana (IDIPHISA), Madrid, Spain.; Centro de Investigación en Red en Enfermedades Cardiovasculares (CIBERCV), Madrid, Spain.; Universidad Francisco de Vitoria (UFV), Madrid, Spain.; Centro Nacional de Investigaciones Cardiovasculares (CNIC), Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Lakdawala+NK%22">Lakdawala NK</searchLink>; Brigham and Women's Hospital, Boston, Massachusetts, USA.; Harvard Medical School, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Sinagra+G%22">Sinagra G</searchLink>; Cardiothoracovascular Department, Azienda Sanitaria Universitaria Giuliano Isontina (ASUGI), University of Trieste, Trieste, Italy.<br /><searchLink fieldCode="AU" term="%22Ripoll-Vera+T%22">Ripoll-Vera T</searchLink>; Hospital Universitario Son Llatzer, Mallorca, Spain.; Health Research Institute of the Balearic Islands (IdISBa), Mallorca, Spain.; Department of Medicine, University of the Balearic Islands, Mallorca, Spain.; Centro de Investigación Biomédica en Red de Fisiopatología de la Obesidad y Nutrición (CIBERobn), Institute of Health Carlos III, Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Afshar+K%22">Afshar K</searchLink>; Intermountain Heart Institute, Salt Lake City, Utah, USA.<br /><searchLink fieldCode="AU" term="%22Priori+SG%22">Priori SG</searchLink>; Centro Nacional de Investigaciones Cardiovasculares (CNIC), Madrid, Spain.; IRCCS Istituti Clinici Scientifici Maugeri SpA SB of Pavia, Pavia, Italy.; Department of Molecular Medicine, University of Pavia, Pavia, Italy.<br /><searchLink fieldCode="AU" term="%22Ware+JS%22">Ware JS</searchLink>; National Heart & Lung Institute and MRC London Institute of Medical Sciences, Imperial College London, London, UK.; Royal Brompton & Harefield Hospitals, Guy's and St Thomas' NHS Foundation Trust, London, UK.<br /><searchLink fieldCode="AU" term="%22Owens+A%22">Owens A</searchLink>; University of Pennsylvania Heart and Vascular Center, Philadelphia, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Li+H%22">Li H</searchLink>; Pfizer Inc., Collegeville, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Angeli+FS%22">Angeli FS</searchLink>; Pfizer Inc., Collegeville, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Elliott+P%22">Elliott P</searchLink>; University College London, London, UK.<br /><searchLink fieldCode="AU" term="%22MacRae+CA%22">MacRae CA</searchLink>; Brigham and Women's Hospital, Boston, Massachusetts, USA.; Harvard Medical School, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Judge+DP%22">Judge DP</searchLink>; Cardiovascular Genetics, Medical University of South Carolina, Charleston, South Carolina, USA.
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  Data: <searchLink fieldCode="JN" term="%22101669191%22">ESC heart failure</searchLink> [ESC Heart Fail] 2024 Dec; Vol. 11 (6), pp. 4201-4208. <i>Date of Electronic Publication: </i>2024 Aug 15.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22John+Wiley+%26+Sons+Ltd+on+behalf+of+the+European+Society+of+Cardiology%22">John Wiley & Sons Ltd on behalf of the European Society of Cardiology </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>101669191 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2055-5822 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2220555822%22">20555822 </searchLink><i>NLM ISO Abbreviation: </i>ESC Heart Fail <i>Subsets: </i>MEDLINE
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              Text: 2024 Dec
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