| Authors: |
Savarirayan R; Murdoch Children's Research Institute, Royal Children's Hospital Victoria, University of Melbourne, Parkville, Victoria, Australia. Electronic address: ravi.savarirayan@mcri.edu.au., Irving M; Guy's and St Thomas' NHS Foundation Trust, Evelina Children's Hospital, London, United Kingdom., Wilcox WR; Emory University, Atlanta, GA., Bacino CA; Baylor College of Medicine, Houston, TX., Hoover-Fong JE; Johns Hopkins University School of Medicine, Baltimore, MD., Harmatz P; UCSF Benioff Children's Hospital Oakland, Oakland, CA., Polgreen LE; Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, Torrance, CA., Mohnike K; Otto-von-Guericke Universität, Universitätskinderklinik, Magdeburg, Germany., Prada CE; Division of Genetics, Genomics and Metabolism, Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, IL; Department of Pediatrics, Northwestern University Feinberg School of Medicine, Chicago, IL., Kubota T; Osaka University, Osaka, Japan., Arundel P; Sheffield Children's NHS Foundation Trust, Sheffield Children's Hospital, Sheffield, United Kingdom., Leiva-Gea A; Instituto de Investigación Biomédica de Málaga-Plataforma Bionand, Málaga, Andalucía, Spain; Hospital Universitario Virgen de la Victoria, Málaga, Spain., Rowell R; BioMarin Pharmaceutical Inc., Novato, CA., Low A; BioMarin (United Kingdom) Limited, London, United Kingdom., Sabir I; BioMarin (United Kingdom) Limited, London, United Kingdom., Huntsman-Labed A; BioMarin (United Kingdom) Limited, London, United Kingdom., Day J; BioMarin (United Kingdom) Limited, London, United Kingdom. |