A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results.

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Bibliographic Details
Title: A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results.
Authors: Hermans C; Cliniques universitaires saint-Luc, Université catholique de Louvain (UCLOuvain), Brussels, Belgium., Valentino LA; National Bleeding Disorders Foundation, New York City, New York, USA.; Hemophilia and Thrombophilia Center, Rush University, Chicago, Illinois, USA., Thornburg CD; Department of Pediatrics, University of California San Diego, La Jolla, California, USA.; Hemophilia and Thrombosis Treatment Cente, Rady Children's Hospital San Diego, San Diego, California, USA., Unzu C; DNA&RNA Medicine Division, CIMA-Universidad de Navarra, IdisNA, Pamplona, Spain., Kay MA; Pediatrics - Human Gene Therapy, Stanford University, Stanford, California, USA., Peyvandi F; Department of Pathophysiology and Transplantation, University of Milan, Milan, Italy., Smith P; Utah Center for Bleeding and Clotting Disorders, Salt Lake City, Utah, USA., Miesbach W; Department of Haemostaseology, University Hospital Frankfurt, Frankfurt, Germany., McKeown W; Care of Elderly Medicine, Antrim Area Hospital, Antrim, Northern Ireland., Pierce GF; World Federation of Hemophilia, Montreal, Quebec, Canada., Khair K; Haemnet, London, UK., Pipe SW; Pediatric Hematology-Oncology, University of Michigan, Ann Arbor, Michigan, USA., Starcevic K; Language Strategy, Maslansky and Partners, New York City, New York, USA., Pillai M; Language Strategy, Maslansky and Partners, New York City, New York, USA., Jones M; Regeneron Pharmaceuticals, Inc., Tarrytown, New York, USA., Chiao M; Regeneron Pharmaceuticals, Inc., Tarrytown, New York, USA., Antonino I; Intellia Therapeutics, Inc., Cambridge, Massachusetts, USA., Kessler C; Medicine and Pathology, Georgetown University, Washington, District of Columbia, USA.
Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2024 Nov; Vol. 30 (6), pp. 1272-1280. Date of Electronic Publication: 2024 Oct 22.
Publication Type: Journal Article
Journal Info: Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1365-2516
DOI:10.1111/hae.15108