A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results.

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Title: A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results.
Authors: Hermans C; Cliniques universitaires saint-Luc, Université catholique de Louvain (UCLOuvain), Brussels, Belgium., Valentino LA; National Bleeding Disorders Foundation, New York City, New York, USA.; Hemophilia and Thrombophilia Center, Rush University, Chicago, Illinois, USA., Thornburg CD; Department of Pediatrics, University of California San Diego, La Jolla, California, USA.; Hemophilia and Thrombosis Treatment Cente, Rady Children's Hospital San Diego, San Diego, California, USA., Unzu C; DNA&RNA Medicine Division, CIMA-Universidad de Navarra, IdisNA, Pamplona, Spain., Kay MA; Pediatrics - Human Gene Therapy, Stanford University, Stanford, California, USA., Peyvandi F; Department of Pathophysiology and Transplantation, University of Milan, Milan, Italy., Smith P; Utah Center for Bleeding and Clotting Disorders, Salt Lake City, Utah, USA., Miesbach W; Department of Haemostaseology, University Hospital Frankfurt, Frankfurt, Germany., McKeown W; Care of Elderly Medicine, Antrim Area Hospital, Antrim, Northern Ireland., Pierce GF; World Federation of Hemophilia, Montreal, Quebec, Canada., Khair K; Haemnet, London, UK., Pipe SW; Pediatric Hematology-Oncology, University of Michigan, Ann Arbor, Michigan, USA., Starcevic K; Language Strategy, Maslansky and Partners, New York City, New York, USA., Pillai M; Language Strategy, Maslansky and Partners, New York City, New York, USA., Jones M; Regeneron Pharmaceuticals, Inc., Tarrytown, New York, USA., Chiao M; Regeneron Pharmaceuticals, Inc., Tarrytown, New York, USA., Antonino I; Intellia Therapeutics, Inc., Cambridge, Massachusetts, USA., Kessler C; Medicine and Pathology, Georgetown University, Washington, District of Columbia, USA.
Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2024 Nov; Vol. 30 (6), pp. 1272-1280. Date of Electronic Publication: 2024 Oct 22.
Publication Type: Journal Article
Journal Info: Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary results.
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  Data: <searchLink fieldCode="AU" term="%22Hermans+C%22">Hermans C</searchLink>; Cliniques universitaires saint-Luc, Université catholique de Louvain (UCLOuvain), Brussels, Belgium.<br /><searchLink fieldCode="AU" term="%22Valentino+LA%22">Valentino LA</searchLink>; National Bleeding Disorders Foundation, New York City, New York, USA.; Hemophilia and Thrombophilia Center, Rush University, Chicago, Illinois, USA.<br /><searchLink fieldCode="AU" term="%22Thornburg+CD%22">Thornburg CD</searchLink>; Department of Pediatrics, University of California San Diego, La Jolla, California, USA.; Hemophilia and Thrombosis Treatment Cente, Rady Children's Hospital San Diego, San Diego, California, USA.<br /><searchLink fieldCode="AU" term="%22Unzu+C%22">Unzu C</searchLink>; DNA&RNA Medicine Division, CIMA-Universidad de Navarra, IdisNA, Pamplona, Spain.<br /><searchLink fieldCode="AU" term="%22Kay+MA%22">Kay MA</searchLink>; Pediatrics - Human Gene Therapy, Stanford University, Stanford, California, USA.<br /><searchLink fieldCode="AU" term="%22Peyvandi+F%22">Peyvandi F</searchLink>; Department of Pathophysiology and Transplantation, University of Milan, Milan, Italy.<br /><searchLink fieldCode="AU" term="%22Smith+P%22">Smith P</searchLink>; Utah Center for Bleeding and Clotting Disorders, Salt Lake City, Utah, USA.<br /><searchLink fieldCode="AU" term="%22Miesbach+W%22">Miesbach W</searchLink>; Department of Haemostaseology, University Hospital Frankfurt, Frankfurt, Germany.<br /><searchLink fieldCode="AU" term="%22McKeown+W%22">McKeown W</searchLink>; Care of Elderly Medicine, Antrim Area Hospital, Antrim, Northern Ireland.<br /><searchLink fieldCode="AU" term="%22Pierce+GF%22">Pierce GF</searchLink>; World Federation of Hemophilia, Montreal, Quebec, Canada.<br /><searchLink fieldCode="AU" term="%22Khair+K%22">Khair K</searchLink>; Haemnet, London, UK.<br /><searchLink fieldCode="AU" term="%22Pipe+SW%22">Pipe SW</searchLink>; Pediatric Hematology-Oncology, University of Michigan, Ann Arbor, Michigan, USA.<br /><searchLink fieldCode="AU" term="%22Starcevic+K%22">Starcevic K</searchLink>; Language Strategy, Maslansky and Partners, New York City, New York, USA.<br /><searchLink fieldCode="AU" term="%22Pillai+M%22">Pillai M</searchLink>; Language Strategy, Maslansky and Partners, New York City, New York, USA.<br /><searchLink fieldCode="AU" term="%22Jones+M%22">Jones M</searchLink>; Regeneron Pharmaceuticals, Inc., Tarrytown, New York, USA.<br /><searchLink fieldCode="AU" term="%22Chiao+M%22">Chiao M</searchLink>; Regeneron Pharmaceuticals, Inc., Tarrytown, New York, USA.<br /><searchLink fieldCode="AU" term="%22Antonino+I%22">Antonino I</searchLink>; Intellia Therapeutics, Inc., Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Kessler+C%22">Kessler C</searchLink>; Medicine and Pathology, Georgetown University, Washington, District of Columbia, USA.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Blackwell+Science%22">Blackwell Science </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9442916 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1365-2516 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2213518216%22">13518216 </searchLink><i>NLM ISO Abbreviation: </i>Haemophilia <i>Subsets: </i>MEDLINE
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