View in EDS

Repeated dosing of AAV-mediated liver gene therapy in juvenile rat and mouse models of Crigler-Najjar syndrome type I.

Saved in:
Bibliographic Details
Title: Repeated dosing of AAV-mediated liver gene therapy in juvenile rat and mouse models of Crigler-Najjar syndrome type I.
Authors: Shi X; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.; School of Life Sciences, Liaoning Provincial Key Laboratory of Biotechnology and Drug Discovery, Liaoning Normal University, Dalian 116082, P.R. China., Bortolussi G; International Centre for Genetic Engineering and Biotechnology (ICGEB), Padriciano 99, 34149 Trieste, Italy., Collaud F; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, Inserm, Genethon, Integrare Research Unit UMR_S951, 91000 Evry, France., Le Brun PR; Genethon, 91000 Evry, France., Bloemendaal LT; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Guerchet N; Genethon, 91000 Evry, France., Rudi de Waart D; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Sellier P; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, Inserm, Genethon, Integrare Research Unit UMR_S951, 91000 Evry, France., Duijst S; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Veron P; Genethon, 91000 Evry, France., Mingozzi F; Genethon, 91000 Evry, France., Kishimoto TK; Selecta Biosciences, Watertown, MA 02472, USA., Ronzitti G; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, Inserm, Genethon, Integrare Research Unit UMR_S951, 91000 Evry, France., Bosma P; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Muro AF; International Centre for Genetic Engineering and Biotechnology (ICGEB), Padriciano 99, 34149 Trieste, Italy.
Source: Molecular therapy. Methods & clinical development [Mol Ther Methods Clin Dev] 2024 Oct 28; Vol. 32 (4), pp. 101363. Date of Electronic Publication: 2024 Oct 28 (Print Publication: 2024).
Publication Type: Journal Article
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101624857 Publication Model: eCollection Cited Medium: Print ISSN: 2329-0501 (Print) Linking ISSN: 23290501 NLM ISO Abbreviation: Mol Ther Methods Clin Dev Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
FullText Text:
  Availability: 0
Header DbId: mdl
DbLabel: MEDLINE Ultimate
An: 39618425
AccessLevel: 2
PubType: Academic Journal
PubTypeId: academicJournal
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: Repeated dosing of AAV-mediated liver gene therapy in juvenile rat and mouse models of Crigler-Najjar syndrome type I.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AU" term="%22Shi+X%22">Shi X</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.; School of Life Sciences, Liaoning Provincial Key Laboratory of Biotechnology and Drug Discovery, Liaoning Normal University, Dalian 116082, P.R. China.<br /><searchLink fieldCode="AU" term="%22Bortolussi+G%22">Bortolussi G</searchLink>; International Centre for Genetic Engineering and Biotechnology (ICGEB), Padriciano 99, 34149 Trieste, Italy.<br /><searchLink fieldCode="AU" term="%22Collaud+F%22">Collaud F</searchLink>; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, Inserm, Genethon, Integrare Research Unit UMR_S951, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Le+Brun+PR%22">Le Brun PR</searchLink>; Genethon, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Bloemendaal+LT%22">Bloemendaal LT</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Guerchet+N%22">Guerchet N</searchLink>; Genethon, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Rudi+de+Waart+D%22">Rudi de Waart D</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Sellier+P%22">Sellier P</searchLink>; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, Inserm, Genethon, Integrare Research Unit UMR_S951, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Duijst+S%22">Duijst S</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Veron+P%22">Veron P</searchLink>; Genethon, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Mingozzi+F%22">Mingozzi F</searchLink>; Genethon, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Kishimoto+TK%22">Kishimoto TK</searchLink>; Selecta Biosciences, Watertown, MA 02472, USA.<br /><searchLink fieldCode="AU" term="%22Ronzitti+G%22">Ronzitti G</searchLink>; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, Inserm, Genethon, Integrare Research Unit UMR_S951, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Bosma+P%22">Bosma P</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AG&M, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Muro+AF%22">Muro AF</searchLink>; International Centre for Genetic Engineering and Biotechnology (ICGEB), Padriciano 99, 34149 Trieste, Italy.
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%22101624857%22">Molecular therapy. Methods & clinical development</searchLink> [Mol Ther Methods Clin Dev] 2024 Oct 28; Vol. 32 (4), pp. 101363. <i>Date of Electronic Publication: </i>2024 Oct 28 (<i>Print Publication: </i>2024).
– Name: TypePub
  Label: Publication Type
  Group: TypPub
  Data: Journal Article
– Name: TitleSource
  Label: Journal Info
  Group: Src
  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101624857 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Print <i>ISSN: </i>2329-0501 (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2223290501%22">23290501 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther Methods Clin Dev <i>Subsets: </i>PubMed not MEDLINE
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=39618425
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1016/j.omtm.2024.101363
    Languages:
      – Code: eng
        Text: English
    PhysicalDescription:
      Pagination:
        StartPage: 101363
    Titles:
      – TitleFull: Repeated dosing of AAV-mediated liver gene therapy in juvenile rat and mouse models of Crigler-Najjar syndrome type I.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Shi X
      – PersonEntity:
          Name:
            NameFull: Bortolussi G
      – PersonEntity:
          Name:
            NameFull: Collaud F
      – PersonEntity:
          Name:
            NameFull: Le Brun PR
      – PersonEntity:
          Name:
            NameFull: Bloemendaal LT
      – PersonEntity:
          Name:
            NameFull: Guerchet N
      – PersonEntity:
          Name:
            NameFull: Rudi de Waart D
      – PersonEntity:
          Name:
            NameFull: Sellier P
      – PersonEntity:
          Name:
            NameFull: Duijst S
      – PersonEntity:
          Name:
            NameFull: Veron P
      – PersonEntity:
          Name:
            NameFull: Mingozzi F
      – PersonEntity:
          Name:
            NameFull: Kishimoto TK
      – PersonEntity:
          Name:
            NameFull: Ronzitti G
      – PersonEntity:
          Name:
            NameFull: Bosma P
      – PersonEntity:
          Name:
            NameFull: Muro AF
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 28
              M: 10
              Text: 2024 Oct 28
              Type: published
              Y: 2024
          Identifiers:
            – Type: issn-print
              Value: 2329-0501
          Numbering:
            – Type: volume
              Value: 32
            – Type: issue
              Value: 4
          Titles:
            – TitleFull: Molecular therapy. Methods & clinical development
              Type: main
ResultId 1