Real-world use of emicizumab in Chinese children with hemophilia A: Retrospective data from a comprehensive care center.

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Title: Real-world use of emicizumab in Chinese children with hemophilia A: Retrospective data from a comprehensive care center.
Authors: Mao Q; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China., Chen Z; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China., Liu G; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China., Li G; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China., Zhen Y; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China., Cheng X; Department of Pharmacy Beijing Children's Hospital, Capital Medical University, National Center for Children's Health Beijing China., Li Z; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China., Yao W; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China., Ai D; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China., Li Z; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China., Wang N; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China., Poon MC; Departments of Medicine, Foothills Medical Centre University of Calgary 1403-29th Street NW Calgary T2N 2T9 Alberta Canada., Wu R; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.
Source: Pediatric investigation [Pediatr Investig] 2024 Jul 22; Vol. 8 (4), pp. 244-252. Date of Electronic Publication: 2024 Jul 22 (Print Publication: 2024).
Publication Type: Journal Article
Journal Info: Publisher: John Wiley & Sons Country of Publication: United States NLM ID: 101731527 Publication Model: eCollection Cited Medium: Internet ISSN: 2574-2272 (Electronic) Linking ISSN: 25742272 NLM ISO Abbreviation: Pediatr Investig Subsets: PubMed not MEDLINE
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  Data: Real-world use of emicizumab in Chinese children with hemophilia A: Retrospective data from a comprehensive care center.
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  Data: <searchLink fieldCode="AU" term="%22Mao+Q%22">Mao Q</searchLink>; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Chen+Z%22">Chen Z</searchLink>; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Liu+G%22">Liu G</searchLink>; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Li+G%22">Li G</searchLink>; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Zhen+Y%22">Zhen Y</searchLink>; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Cheng+X%22">Cheng X</searchLink>; Department of Pharmacy Beijing Children's Hospital, Capital Medical University, National Center for Children's Health Beijing China.<br /><searchLink fieldCode="AU" term="%22Li+Z%22">Li Z</searchLink>; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Yao+W%22">Yao W</searchLink>; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Ai+D%22">Ai D</searchLink>; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Li+Z%22">Li Z</searchLink>; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Wang+N%22">Wang N</searchLink>; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.; Hematologic Disease Laboratory, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, Ministry of Education, Beijing Pediatric Research Institute, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Beijing Children's Hospital, Capital Medical University Beijing China.<br /><searchLink fieldCode="AU" term="%22Poon+MC%22">Poon MC</searchLink>; Departments of Medicine, Foothills Medical Centre University of Calgary 1403-29th Street NW Calgary T2N 2T9 Alberta Canada.<br /><searchLink fieldCode="AU" term="%22Wu+R%22">Wu R</searchLink>; Hematology Department, Hemophilia Comprehensive Care Center, Hematology Center, Beijing Key Laboratory of Pediatric Hematology-Oncology, Key Laboratory of Major Diseases in Children, National Center for Children's Health National Key Discipline of Pediatrics (Capital Medical University), Ministry of Education, Beijing Children's Hospital, Capital Medical University Beijing China.
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  Data: <searchLink fieldCode="JN" term="%22101731527%22">Pediatric investigation</searchLink> [Pediatr Investig] 2024 Jul 22; Vol. 8 (4), pp. 244-252. <i>Date of Electronic Publication: </i>2024 Jul 22 (<i>Print Publication: </i>2024).
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