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Sustained growth-promoting effects of vosoritide in children with achondroplasia from an ongoing phase 3 extension study.

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Title: Sustained growth-promoting effects of vosoritide in children with achondroplasia from an ongoing phase 3 extension study.
Authors: Savarirayan R; Murdoch Children's Research Institute, Royal Children's Hospital Victoria, University of Melbourne, Parkville, VIC, Australia. Electronic address: ravi.savarirayan@mcri.edu.au., Irving M; Guy's and St. Thomas' NHS Foundation Trust, Evelina Children's Hospital, London, UK., Wilcox WR; Department of Human Genetics, Emory University School of Medicine, Atlanta, GA, USA., Bacino CA; Baylor College of Medicine, Houston, TX, USA., Hoover-Fong JE; Johns Hopkins University School of Medicine, Baltimore, MD, USA., Harmatz P; UCSF Benioff Children's Hospital Oakland, Oakland, CA, USA., Polgreen LE; Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, Torrance, CA, USA., Palm K; Otto-von-Guericke Universität, Universitätskinderklinik, Magdeburg, Germany., Prada CE; Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, IL, USA., Kubota T; Osaka University, Osaka, Japan., Arundel P; Sheffield Children's NHS Foundation Trust, Sheffield Children's Hospital, Sheffield, UK., Kotani Y; Tokushima University Hospital, Tokushima, Japan., Leiva-Gea A; Hospital Universitario Virgen de la Victoria, Instituto de Investigación Biomédica de Málaga, Málaga, Spain., Bober MB; Nemours-Alfred I. du Pont Hospital for Children, Wilmington, DE, USA., Hecht JT; McGovern Medical School and School of Dentistry, University of Texas Health, Houston, TX, USA., Legare JM; University of Wisconsin School of Medicine and Public Health, Madison, WI, USA., Lawrinson S; BioMarin (UK) Limited, Ltd., London, UK., Low A; BioMarin (UK) Limited, Ltd., London, UK., Sabir I; BioMarin (UK) Limited, Ltd., London, UK., Huntsman-Labed A; BioMarin (UK) Limited, Ltd., London, UK., Day JRS; BioMarin (UK) Limited, Ltd., London, UK.
Source: Med (New York, N.Y.) [Med] 2025 May 09; Vol. 6 (5), pp. 100566. Date of Electronic Publication: 2024 Dec 30.
Publication Type: Journal Article; Clinical Trial, Phase III; Randomized Controlled Trial; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101769215 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2666-6340 (Electronic) Linking ISSN: 26666340 NLM ISO Abbreviation: Med Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Sustained growth-promoting effects of vosoritide in children with achondroplasia from an ongoing phase 3 extension study.
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  Data: <searchLink fieldCode="AU" term="%22Savarirayan+R%22">Savarirayan R</searchLink>; Murdoch Children's Research Institute, Royal Children's Hospital Victoria, University of Melbourne, Parkville, VIC, Australia. Electronic address: ravi.savarirayan@mcri.edu.au.<br /><searchLink fieldCode="AU" term="%22Irving+M%22">Irving M</searchLink>; Guy's and St. Thomas' NHS Foundation Trust, Evelina Children's Hospital, London, UK.<br /><searchLink fieldCode="AU" term="%22Wilcox+WR%22">Wilcox WR</searchLink>; Department of Human Genetics, Emory University School of Medicine, Atlanta, GA, USA.<br /><searchLink fieldCode="AU" term="%22Bacino+CA%22">Bacino CA</searchLink>; Baylor College of Medicine, Houston, TX, USA.<br /><searchLink fieldCode="AU" term="%22Hoover-Fong+JE%22">Hoover-Fong JE</searchLink>; Johns Hopkins University School of Medicine, Baltimore, MD, USA.<br /><searchLink fieldCode="AU" term="%22Harmatz+P%22">Harmatz P</searchLink>; UCSF Benioff Children's Hospital Oakland, Oakland, CA, USA.<br /><searchLink fieldCode="AU" term="%22Polgreen+LE%22">Polgreen LE</searchLink>; Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, Torrance, CA, USA.<br /><searchLink fieldCode="AU" term="%22Palm+K%22">Palm K</searchLink>; Otto-von-Guericke Universität, Universitätskinderklinik, Magdeburg, Germany.<br /><searchLink fieldCode="AU" term="%22Prada+CE%22">Prada CE</searchLink>; Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, IL, USA.<br /><searchLink fieldCode="AU" term="%22Kubota+T%22">Kubota T</searchLink>; Osaka University, Osaka, Japan.<br /><searchLink fieldCode="AU" term="%22Arundel+P%22">Arundel P</searchLink>; Sheffield Children's NHS Foundation Trust, Sheffield Children's Hospital, Sheffield, UK.<br /><searchLink fieldCode="AU" term="%22Kotani+Y%22">Kotani Y</searchLink>; Tokushima University Hospital, Tokushima, Japan.<br /><searchLink fieldCode="AU" term="%22Leiva-Gea+A%22">Leiva-Gea A</searchLink>; Hospital Universitario Virgen de la Victoria, Instituto de Investigación Biomédica de Málaga, Málaga, Spain.<br /><searchLink fieldCode="AU" term="%22Bober+MB%22">Bober MB</searchLink>; Nemours-Alfred I. du Pont Hospital for Children, Wilmington, DE, USA.<br /><searchLink fieldCode="AU" term="%22Hecht+JT%22">Hecht JT</searchLink>; McGovern Medical School and School of Dentistry, University of Texas Health, Houston, TX, USA.<br /><searchLink fieldCode="AU" term="%22Legare+JM%22">Legare JM</searchLink>; University of Wisconsin School of Medicine and Public Health, Madison, WI, USA.<br /><searchLink fieldCode="AU" term="%22Lawrinson+S%22">Lawrinson S</searchLink>; BioMarin (UK) Limited, Ltd., London, UK.<br /><searchLink fieldCode="AU" term="%22Low+A%22">Low A</searchLink>; BioMarin (UK) Limited, Ltd., London, UK.<br /><searchLink fieldCode="AU" term="%22Sabir+I%22">Sabir I</searchLink>; BioMarin (UK) Limited, Ltd., London, UK.<br /><searchLink fieldCode="AU" term="%22Huntsman-Labed+A%22">Huntsman-Labed A</searchLink>; BioMarin (UK) Limited, Ltd., London, UK.<br /><searchLink fieldCode="AU" term="%22Day+JRS%22">Day JRS</searchLink>; BioMarin (UK) Limited, Ltd., London, UK.
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