Analysis of Exon Skipping Applicability for Dysferlinopathies.

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Bibliographic Details
Title: Analysis of Exon Skipping Applicability for Dysferlinopathies.
Authors: Leckie J; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB T6G 2H7, Canada., Rodriguez SH; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB T6G 2H7, Canada., Krahn M; INSERM, Marseille Medical Genetics, U1251, Aix-Marseille University, APHM, 13385 Marseille, France.; Medical Genetics Department, Timone Hospital, APHM, 13005 Marseille, France., Yokota T; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB T6G 2H7, Canada.; The Friends of Garrett Cumming Research & Muscular Dystrophy Canada HM Toupin Neurological Sciences Research, Edmonton, AB T6G 2H7, Canada.
Source: Cells [Cells] 2025 Jan 24; Vol. 14 (3). Date of Electronic Publication: 2025 Jan 24.
Publication Type: Journal Article; Review; Research Support, U.S. Gov't, Non-P.H.S.; Research Support, Non-U.S. Gov't
Journal Info: Publisher: MDPI Country of Publication: Switzerland NLM ID: 101600052 Publication Model: Electronic Cited Medium: Internet ISSN: 2073-4409 (Electronic) Linking ISSN: 20734409 NLM ISO Abbreviation: Cells Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:2073-4409
DOI:10.3390/cells14030177