Evaluating elexacaftor/tezacaftor/ivacaftor (ETI; Trikafta™) for treatment of patients with non-cystic fibrosis bronchiectasis (NCFBE): A clinical study protocol.
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| Title: | Evaluating elexacaftor/tezacaftor/ivacaftor (ETI; Trikafta™) for treatment of patients with non-cystic fibrosis bronchiectasis (NCFBE): A clinical study protocol. |
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| Authors: | Swenson CE; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America., Hunt WR; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America., Manfredi C; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America., Beltran DJ; Georgia Clinical & Translational Science Alliance, Emory University, Atlanta, GA, United States of America., Hong JS; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America., Davis BR; Division of Pulmonary, Allergy & Critical Care Medicine, University of Alabama at Birmingham Heersink School of Medicine, Birmingham, AL, United States of America., Suzuki S; Division of Pulmonary, Allergy & Critical Care Medicine, University of Alabama at Birmingham Heersink School of Medicine, Birmingham, AL, United States of America., Barillá C; Division of Pulmonary, Allergy & Critical Care Medicine, University of Alabama at Birmingham Heersink School of Medicine, Birmingham, AL, United States of America., Rab A; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America., Chico C; Georgia Clinical & Translational Science Alliance, Emory University, Atlanta, GA, United States of America., Dangerfield J; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America., Streby A; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America., Barton E; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America., Cox EM; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America., Stecenko AA; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America., Westbrook A; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America., Kapolka R; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America., Sorscher EJ; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America. |
| Source: | PloS one [PLoS One] 2025 Feb 14; Vol. 20 (2), pp. e0316721. Date of Electronic Publication: 2025 Feb 14 (Print Publication: 2025). |
| Publication Type: | Journal Article; Clinical Trial Protocol |
| Journal Info: | Publisher: Public Library of Science Country of Publication: United States NLM ID: 101285081 Publication Model: eCollection Cited Medium: Internet ISSN: 1932-6203 (Electronic) Linking ISSN: 19326203 NLM ISO Abbreviation: PLoS One Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 39951444 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Evaluating elexacaftor/tezacaftor/ivacaftor (ETI; Trikafta™) for treatment of patients with non-cystic fibrosis bronchiectasis (NCFBE): A clinical study protocol. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Swenson+CE%22">Swenson CE</searchLink>; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Hunt+WR%22">Hunt WR</searchLink>; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Manfredi+C%22">Manfredi C</searchLink>; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Beltran+DJ%22">Beltran DJ</searchLink>; Georgia Clinical & Translational Science Alliance, Emory University, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Hong+JS%22">Hong JS</searchLink>; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Davis+BR%22">Davis BR</searchLink>; Division of Pulmonary, Allergy & Critical Care Medicine, University of Alabama at Birmingham Heersink School of Medicine, Birmingham, AL, United States of America.<br /><searchLink fieldCode="AU" term="%22Suzuki+S%22">Suzuki S</searchLink>; Division of Pulmonary, Allergy & Critical Care Medicine, University of Alabama at Birmingham Heersink School of Medicine, Birmingham, AL, United States of America.<br /><searchLink fieldCode="AU" term="%22Barillá+C%22">Barillá C</searchLink>; Division of Pulmonary, Allergy & Critical Care Medicine, University of Alabama at Birmingham Heersink School of Medicine, Birmingham, AL, United States of America.<br /><searchLink fieldCode="AU" term="%22Rab+A%22">Rab A</searchLink>; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Chico+C%22">Chico C</searchLink>; Georgia Clinical & Translational Science Alliance, Emory University, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Dangerfield+J%22">Dangerfield J</searchLink>; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Streby+A%22">Streby A</searchLink>; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Barton+E%22">Barton E</searchLink>; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Cox+EM%22">Cox EM</searchLink>; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Stecenko+AA%22">Stecenko AA</searchLink>; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Westbrook+A%22">Westbrook A</searchLink>; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Kapolka+R%22">Kapolka R</searchLink>; Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America.<br /><searchLink fieldCode="AU" term="%22Sorscher+EJ%22">Sorscher EJ</searchLink>; Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children's Healthcare of Atlanta, Atlanta, GA, United States of America. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101285081%22">PloS one</searchLink> [PLoS One] 2025 Feb 14; Vol. 20 (2), pp. e0316721. <i>Date of Electronic Publication: </i>2025 Feb 14 (<i>Print Publication: </i>2025). – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Clinical Trial Protocol – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Public+Library+of+Science%22">Public Library of Science </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101285081 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Internet <i>ISSN: </i>1932-6203 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2219326203%22">19326203 </searchLink><i>NLM ISO Abbreviation: </i>PLoS One <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=39951444 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1371/journal.pone.0316721 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: e0316721 Titles: – TitleFull: Evaluating elexacaftor/tezacaftor/ivacaftor (ETI; Trikafta™) for treatment of patients with non-cystic fibrosis bronchiectasis (NCFBE): A clinical study protocol. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Swenson CE – PersonEntity: Name: NameFull: Hunt WR – PersonEntity: Name: NameFull: Manfredi C – PersonEntity: Name: NameFull: Beltran DJ – PersonEntity: Name: NameFull: Hong JS – PersonEntity: Name: NameFull: Davis BR – PersonEntity: Name: NameFull: Suzuki S – PersonEntity: Name: NameFull: Barillá C – PersonEntity: Name: NameFull: Rab A – PersonEntity: Name: NameFull: Chico C – PersonEntity: Name: NameFull: Dangerfield J – PersonEntity: Name: NameFull: Streby A – PersonEntity: Name: NameFull: Barton E – PersonEntity: Name: NameFull: Cox EM – PersonEntity: Name: NameFull: Stecenko AA – PersonEntity: Name: NameFull: Westbrook A – PersonEntity: Name: NameFull: Kapolka R – PersonEntity: Name: NameFull: Sorscher EJ IsPartOfRelationships: – BibEntity: Dates: – D: 14 M: 02 Text: 2025 Feb 14 Type: published Y: 2025 Identifiers: – Type: issn-electronic Value: 1932-6203 Numbering: – Type: volume Value: 20 – Type: issue Value: 2 Titles: – TitleFull: PloS one Type: main |
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