Patisiran in ATTRv amyloidosis with polyneuropathy: "PatisiranItaly" multicenter observational study.

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Title: Patisiran in ATTRv amyloidosis with polyneuropathy: "PatisiranItaly" multicenter observational study.
Authors: Di Stefano V; Department of Biomedicine, Neuroscience and Advanced Diagnostics (BIND), University of Palermo, Palermo, Italy., Guaraldi P; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy., Romano A; Dipartimento di Neuroscienze, Organi di Senso e Torace, UOC Neurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Largo Agostino Gemelli, 8, 00168, Rome, Italy., Antonini G; Department of Neurology Mental Health and Sensory Organs (NESMOS), Faculty of Medicine and Psychology, 'Sapienza' University of Rome and UniCamillus-Saint Camillus International University of Health Sciences, Rome, Italy., Barilaro A; AOU Careggi and Department of Neurosciences, Drug and Child Health, University of Florence, Florence, Italy., Briani C; Neurology Unit, Department of Neuroscience, University of Padua, Padua, Italy., Burattini M; Neurology Unit, Ospedale Santa Croce di Fano, Fano, Italy., Cani I; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy., Carlini G; Neurological Clinic, Department of Experimental and Clinical Medicine, Marche Polytechnic University, Ancona, Italy., Ceccanti M; Department of Human Neuroscience, Sapienza University of Rome, Rome, Italy., Cianci V; Neurology Unit, Great Metropolitan Hospital 'Bianchi Melacrino Morelli', Reggio Calabria, Italy., Cortelli P; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy., Currò Dossi M; Department of Neurology, Infermi Hospital, Rimini, Italy., Di Lisi D; Division of Cardiology, University Hospital Paolo Giaccone, Palermo, Italy., Di Muzio A; Department of Neuroscience, Imaging and Clinical Sciences, 'G. D'Annunzio' University, Chieti, Italy., Falzone Y; Division of Neuroscience, Department of Neurology, Institute of Experimental Neurology, San Raffaele Scientific Institute, Milan, Italy., Filosto M; Department of Clinical and Experimental Sciences, University of Brescia, Brescia, Italy.; NeMO-Brescia Clinical Center for Neuromuscular Diseases, Brescia, Italy., Gasverde S; ASL TO4, Ciriè, Italy., Gemelli C; IRCCS Ospedale Policlinico San Martino, Genoa, Italy., Gentile L; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy., Goglia M; Neuromuscular Diseases Unit, Department of Systems Medicine, Tor Vergata University of Rome, Rome, Italy., Leonardi L; Neuromuscular and Rare Disease Centre, Neurology Unit, Sant'Andrea Hospital, Rome, Italy., Longhi S; Cardiology Unit, Cardiac Thoracic and Vascular Department, IRCCS Azienda Ospedaliero-Universitaria di Bologna, Bologna, Italy., Lotti A; AOU Careggi and Department of Neurosciences, Drug and Child Health, University of Florence, Florence, Italy., Manganelli F; Department of Neuroscience, Reproductive and Odontostomatological Science, University of Naples 'Federico II', Naples, Italy., Mazzeo A; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy., Milella G; Neurology Unit, Department of Basic Medical Sciences, Neurosciences and Sense Organs, University of Bari Aldo Moro, Bari, Italy., Novo G; Division of Cardiology, University Hospital Paolo Giaccone, Palermo, Italy., Fenu S; S.C. Malattie Neurologiche Rare, Dipartimento di Neuroscienze Cliniche, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy., Palumbo G; Department of Neuroscience, Reproductive and Odontostomatological Science, University of Naples 'Federico II', Naples, Italy., Petrelli C; Neurology Unit, AV3, ASUR Marche, Macerata, Italy., Poli L; Unit of Neurology, ASST Spedali Civili, 25100, Brescia, Italy., Pradotto LG; Department of Neuroscience 'Rita Levi Montalcini', University of Turin, Turin, Italy.; IRCCS Istituto Auxologico Italiano, Piancavallo (Vb), Milan, Italy., Russo M; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy., Salvalaggio A; Neurology Unit, Department of Neuroscience, University of Padua, Padua, Italy., Sciarrone MA; Department of Neuroscience, Università Cattolica del Sacro Cuore, Rome, Italy., Sellitti L; IRCCS Istituto Auxologico Italiano, Piancavallo (Vb), Milan, Italy., Tagliapietra M; Department of Neuroscience, Biomedicina e Movimento, Università di Verona, Verona, Italy., Tozza S; Department of Neuroscience, Reproductive and Odontostomatological Science, University of Naples 'Federico II', Naples, Italy., Turri M; Dipartimento di Neurologia/Stroke Unit, Ospedale di Bolzano, Bolzano, Italy., Verriello L; Neurology Unit, Department of Neurosciences, University Hospital Santa Maria della Misericordia, Udine, Italy., Vitali F; Department of Neuroscience, Università Cattolica del Sacro Cuore, Rome, Italy., Brighina F; Department of Biomedicine, Neuroscience and Advanced Diagnostics (BIND), University of Palermo, Palermo, Italy., Luigetti M; Dipartimento di Neuroscienze, Organi di Senso e Torace, UOC Neurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Largo Agostino Gemelli, 8, 00168, Rome, Italy. mluigetti@gmail.com.; Department of Neuroscience, Università Cattolica del Sacro Cuore, Rome, Italy. mluigetti@gmail.com.
Source: Journal of neurology [J Neurol] 2025 Feb 15; Vol. 272 (3), pp. 209. Date of Electronic Publication: 2025 Feb 15.
Publication Type: Journal Article; Multicenter Study; Observational Study
Journal Info: Publisher: Springer-Verlag Country of Publication: Germany NLM ID: 0423161 Publication Model: Electronic Cited Medium: Internet ISSN: 1432-1459 (Electronic) Linking ISSN: 03405354 NLM ISO Abbreviation: J Neurol Subsets: MEDLINE
Database: MEDLINE Ultimate
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An: 39954098
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PubType: Academic Journal
PubTypeId: academicJournal
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  Data: Patisiran in ATTRv amyloidosis with polyneuropathy: "PatisiranItaly" multicenter observational study.
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  Data: <searchLink fieldCode="AU" term="%22Di+Stefano+V%22">Di Stefano V</searchLink>; Department of Biomedicine, Neuroscience and Advanced Diagnostics (BIND), University of Palermo, Palermo, Italy.<br /><searchLink fieldCode="AU" term="%22Guaraldi+P%22">Guaraldi P</searchLink>; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy.<br /><searchLink fieldCode="AU" term="%22Romano+A%22">Romano A</searchLink>; Dipartimento di Neuroscienze, Organi di Senso e Torace, UOC Neurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Largo Agostino Gemelli, 8, 00168, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Antonini+G%22">Antonini G</searchLink>; Department of Neurology Mental Health and Sensory Organs (NESMOS), Faculty of Medicine and Psychology, 'Sapienza' University of Rome and UniCamillus-Saint Camillus International University of Health Sciences, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Barilaro+A%22">Barilaro A</searchLink>; AOU Careggi and Department of Neurosciences, Drug and Child Health, University of Florence, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Briani+C%22">Briani C</searchLink>; Neurology Unit, Department of Neuroscience, University of Padua, Padua, Italy.<br /><searchLink fieldCode="AU" term="%22Burattini+M%22">Burattini M</searchLink>; Neurology Unit, Ospedale Santa Croce di Fano, Fano, Italy.<br /><searchLink fieldCode="AU" term="%22Cani+I%22">Cani I</searchLink>; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy.<br /><searchLink fieldCode="AU" term="%22Carlini+G%22">Carlini G</searchLink>; Neurological Clinic, Department of Experimental and Clinical Medicine, Marche Polytechnic University, Ancona, Italy.<br /><searchLink fieldCode="AU" term="%22Ceccanti+M%22">Ceccanti M</searchLink>; Department of Human Neuroscience, Sapienza University of Rome, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Cianci+V%22">Cianci V</searchLink>; Neurology Unit, Great Metropolitan Hospital 'Bianchi Melacrino Morelli', Reggio Calabria, Italy.<br /><searchLink fieldCode="AU" term="%22Cortelli+P%22">Cortelli P</searchLink>; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy.<br /><searchLink fieldCode="AU" term="%22Currò+Dossi+M%22">Currò Dossi M</searchLink>; Department of Neurology, Infermi Hospital, Rimini, Italy.<br /><searchLink fieldCode="AU" term="%22Di+Lisi+D%22">Di Lisi D</searchLink>; Division of Cardiology, University Hospital Paolo Giaccone, Palermo, Italy.<br /><searchLink fieldCode="AU" term="%22Di+Muzio+A%22">Di Muzio A</searchLink>; Department of Neuroscience, Imaging and Clinical Sciences, 'G. D'Annunzio' University, Chieti, Italy.<br /><searchLink fieldCode="AU" term="%22Falzone+Y%22">Falzone Y</searchLink>; Division of Neuroscience, Department of Neurology, Institute of Experimental Neurology, San Raffaele Scientific Institute, Milan, Italy.<br /><searchLink fieldCode="AU" term="%22Filosto+M%22">Filosto M</searchLink>; Department of Clinical and Experimental Sciences, University of Brescia, Brescia, Italy.; NeMO-Brescia Clinical Center for Neuromuscular Diseases, Brescia, Italy.<br /><searchLink fieldCode="AU" term="%22Gasverde+S%22">Gasverde S</searchLink>; ASL TO4, Ciriè, Italy.<br /><searchLink fieldCode="AU" term="%22Gemelli+C%22">Gemelli C</searchLink>; IRCCS Ospedale Policlinico San Martino, Genoa, Italy.<br /><searchLink fieldCode="AU" term="%22Gentile+L%22">Gentile L</searchLink>; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.<br /><searchLink fieldCode="AU" term="%22Goglia+M%22">Goglia M</searchLink>; Neuromuscular Diseases Unit, Department of Systems Medicine, Tor Vergata University of Rome, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Leonardi+L%22">Leonardi L</searchLink>; Neuromuscular and Rare Disease Centre, Neurology Unit, Sant'Andrea Hospital, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Longhi+S%22">Longhi S</searchLink>; Cardiology Unit, Cardiac Thoracic and Vascular Department, IRCCS Azienda Ospedaliero-Universitaria di Bologna, Bologna, Italy.<br /><searchLink fieldCode="AU" term="%22Lotti+A%22">Lotti A</searchLink>; AOU Careggi and Department of Neurosciences, Drug and Child Health, University of Florence, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Manganelli+F%22">Manganelli F</searchLink>; Department of Neuroscience, Reproductive and Odontostomatological Science, University of Naples 'Federico II', Naples, Italy.<br /><searchLink fieldCode="AU" term="%22Mazzeo+A%22">Mazzeo A</searchLink>; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.<br /><searchLink fieldCode="AU" term="%22Milella+G%22">Milella G</searchLink>; Neurology Unit, Department of Basic Medical Sciences, Neurosciences and Sense Organs, University of Bari Aldo Moro, Bari, Italy.<br /><searchLink fieldCode="AU" term="%22Novo+G%22">Novo G</searchLink>; Division of Cardiology, University Hospital Paolo Giaccone, Palermo, Italy.<br /><searchLink fieldCode="AU" term="%22Fenu+S%22">Fenu S</searchLink>; S.C. Malattie Neurologiche Rare, Dipartimento di Neuroscienze Cliniche, Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy.<br /><searchLink fieldCode="AU" term="%22Palumbo+G%22">Palumbo G</searchLink>; Department of Neuroscience, Reproductive and Odontostomatological Science, University of Naples 'Federico II', Naples, Italy.<br /><searchLink fieldCode="AU" term="%22Petrelli+C%22">Petrelli C</searchLink>; Neurology Unit, AV3, ASUR Marche, Macerata, Italy.<br /><searchLink fieldCode="AU" term="%22Poli+L%22">Poli L</searchLink>; Unit of Neurology, ASST Spedali Civili, 25100, Brescia, Italy.<br /><searchLink fieldCode="AU" term="%22Pradotto+LG%22">Pradotto LG</searchLink>; Department of Neuroscience 'Rita Levi Montalcini', University of Turin, Turin, Italy.; IRCCS Istituto Auxologico Italiano, Piancavallo (Vb), Milan, Italy.<br /><searchLink fieldCode="AU" term="%22Russo+M%22">Russo M</searchLink>; Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.<br /><searchLink fieldCode="AU" term="%22Salvalaggio+A%22">Salvalaggio A</searchLink>; Neurology Unit, Department of Neuroscience, University of Padua, Padua, Italy.<br /><searchLink fieldCode="AU" term="%22Sciarrone+MA%22">Sciarrone MA</searchLink>; Department of Neuroscience, Università Cattolica del Sacro Cuore, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Sellitti+L%22">Sellitti L</searchLink>; IRCCS Istituto Auxologico Italiano, Piancavallo (Vb), Milan, Italy.<br /><searchLink fieldCode="AU" term="%22Tagliapietra+M%22">Tagliapietra M</searchLink>; Department of Neuroscience, Biomedicina e Movimento, Università di Verona, Verona, Italy.<br /><searchLink fieldCode="AU" term="%22Tozza+S%22">Tozza S</searchLink>; Department of Neuroscience, Reproductive and Odontostomatological Science, University of Naples 'Federico II', Naples, Italy.<br /><searchLink fieldCode="AU" term="%22Turri+M%22">Turri M</searchLink>; Dipartimento di Neurologia/Stroke Unit, Ospedale di Bolzano, Bolzano, Italy.<br /><searchLink fieldCode="AU" term="%22Verriello+L%22">Verriello L</searchLink>; Neurology Unit, Department of Neurosciences, University Hospital Santa Maria della Misericordia, Udine, Italy.<br /><searchLink fieldCode="AU" term="%22Vitali+F%22">Vitali F</searchLink>; Department of Neuroscience, Università Cattolica del Sacro Cuore, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Brighina+F%22">Brighina F</searchLink>; Department of Biomedicine, Neuroscience and Advanced Diagnostics (BIND), University of Palermo, Palermo, Italy.<br /><searchLink fieldCode="AU" term="%22Luigetti+M%22">Luigetti M</searchLink>; Dipartimento di Neuroscienze, Organi di Senso e Torace, UOC Neurologia, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Largo Agostino Gemelli, 8, 00168, Rome, Italy. mluigetti@gmail.com.; Department of Neuroscience, Università Cattolica del Sacro Cuore, Rome, Italy. mluigetti@gmail.com.
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