HLA-haploidentical stem cell transplantation for chronic granulomatous disease: an EBMT-IEWP retrospective study.

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Title: HLA-haploidentical stem cell transplantation for chronic granulomatous disease: an EBMT-IEWP retrospective study.
Authors: Riller Q; Pediatric Unit of Immunology, Hematology, and Rheumatology, Necker Hospital, Paris, France., Hauri M; Department of Stem Cell Transplantation, University Children's Hospital, Zürich, Switzerland., Lum SH; Translational and Clinical Research Institute, Newcastle University, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom., Knippenberg J; European Bone Marrow Transplantation, Leiden Study Unit, Leiden, The Netherlands., Sirait T; European Bone Marrow Transplantation, Leiden Study Unit, Leiden, The Netherlands., Laberko A; Department of Pediatric Hematology, Oncology, and Immunology, Dmitry Rogachev National Medical Research Center, Moscow, Russia., Halahleh K; Adult Bone Marrow Transplantation Program, King Hussein Cancer Centre, Amman, Jordan., Hashem H; Division of Pediatric Blood and Marrow Transplantation, Department of Pediatrics, King Hussein Cancer Center, Amman, Jordan., Karakukcu M; Department of Pediatric Hematology and Oncology, Faculty of Medicine, Erciyes University, Kayseri, Turkey., Sengeloev H; Department of Pediatrics and Adolescent Medicine, Rigshospitalet, Copenhagen, Denmark., Porta F; Department of Pediatric Hematology, Universitá degli Studi di Brescia, Brescia, Italy., Bruno B; Unité d'Hématologie Pédiatrique, Lille University Hospital, Lille, France., Zecca M; Pediatric Hematology/Oncology, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy., Aksoylar S; Division of Pediatric Hemathology and Oncology, Department of Pediatrics, Ege University Medical Faculty, Izmir, Turkey., Barlogis V; Pediatric Haematology Department, Timone Enfant, Assistance Publique-Hôpitaux de Marseilles, Aix-Marseille University, Marseille, France., Schuetz C; Department of Pediatrics, Medizinische Fakultät Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.; German Center for Child and Adolescent Health, Dresden, Germany., Buechner J; Department of Pediatric Hematology and Oncology, Oslo University Hospital, Oslo, Norway., Faraci M; Department of Hematology, Oncology, and Stem Cell Transplantation, IRCCS Istituto Giannina Gaslini, Genoa, Italy., Wehr C; Department of Hematology, Oncology, and Stem Cell Transplantation, Faculty of Medicine and Medical Center, University of Freiburg, Freiburg im Breisgau, Germany., Holter W; Department of Pediatric Haematology and Oncology, St. Anna Children's Hospital, Department of Pediatrics and Adolescent Medicine, Medical University of Vienna, Vienna, Austria., Mellgren K; Pediatric Clinical Unit, Queen Silvia Children's Hospital, Gothenburg, Sweden.; Department of Paediatrics, Institute for Clinical Sciences, Sahlgrenska Academy, University of Gothenburg, Gothenburg, Sweden., Locatelli F; Department of Paediatric Hematology and Oncology, Bambino Gesù Children's Hospital, Istituto di Ricovero e Cura a Carattere Scientifico and Catholic University of the Sacred Heart, Rome, Italy., Martinez AP; Department of Paediatric Hemato-Oncology, Hospital Universitario La Paz, Madrid, Spain., Suarez F; Department of Adult Hematology, Necker-Enfants Malades University Hospital and Centre de Référence des déficits Immunitaires Héréditaires, Assistance Publique-Hôpitaux de Paris, INSERM U1163, Imagine Institute, Université Paris Cité, Paris, France., Moshous D; Pediatric Unit of Immunology, Hematology, and Rheumatology, Necker Hospital, Paris, France., Gennery AR; Translational and Clinical Research Institute, Newcastle University, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom., Balashov D; Department of Pediatric Hematology, Oncology, and Immunology, Dmitry Rogachev National Medical Research Center, Moscow, Russia., Albert MH; Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, Ludwig Maximillian University of Munich, Munich, Germany., Slatter M; Translational and Clinical Research Institute, Newcastle University, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom., Güngör T; Department of Stem Cell Transplantation, University Children's Hospital, Zürich, Switzerland., Neven B; Pediatric Unit of Immunology, Hematology, and Rheumatology, Necker Hospital, Paris, France.
Source: Blood [Blood] 2025 May 22; Vol. 145 (21), pp. 2518-2527.
Publication Type: Journal Article; Multicenter Study
Journal Info: Publisher: Elsevier Country of Publication: United States NLM ID: 7603509 Publication Model: Print Cited Medium: Internet ISSN: 1528-0020 (Electronic) Linking ISSN: 00064971 NLM ISO Abbreviation: Blood Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: HLA-haploidentical stem cell transplantation for chronic granulomatous disease: an EBMT-IEWP retrospective study.
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  Data: <searchLink fieldCode="AU" term="%22Riller+Q%22">Riller Q</searchLink>; Pediatric Unit of Immunology, Hematology, and Rheumatology, Necker Hospital, Paris, France.<br /><searchLink fieldCode="AU" term="%22Hauri+M%22">Hauri M</searchLink>; Department of Stem Cell Transplantation, University Children's Hospital, Zürich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Lum+SH%22">Lum SH</searchLink>; Translational and Clinical Research Institute, Newcastle University, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Knippenberg+J%22">Knippenberg J</searchLink>; European Bone Marrow Transplantation, Leiden Study Unit, Leiden, The Netherlands.<br /><searchLink fieldCode="AU" term="%22Sirait+T%22">Sirait T</searchLink>; European Bone Marrow Transplantation, Leiden Study Unit, Leiden, The Netherlands.<br /><searchLink fieldCode="AU" term="%22Laberko+A%22">Laberko A</searchLink>; Department of Pediatric Hematology, Oncology, and Immunology, Dmitry Rogachev National Medical Research Center, Moscow, Russia.<br /><searchLink fieldCode="AU" term="%22Halahleh+K%22">Halahleh K</searchLink>; Adult Bone Marrow Transplantation Program, King Hussein Cancer Centre, Amman, Jordan.<br /><searchLink fieldCode="AU" term="%22Hashem+H%22">Hashem H</searchLink>; Division of Pediatric Blood and Marrow Transplantation, Department of Pediatrics, King Hussein Cancer Center, Amman, Jordan.<br /><searchLink fieldCode="AU" term="%22Karakukcu+M%22">Karakukcu M</searchLink>; Department of Pediatric Hematology and Oncology, Faculty of Medicine, Erciyes University, Kayseri, Turkey.<br /><searchLink fieldCode="AU" term="%22Sengeloev+H%22">Sengeloev H</searchLink>; Department of Pediatrics and Adolescent Medicine, Rigshospitalet, Copenhagen, Denmark.<br /><searchLink fieldCode="AU" term="%22Porta+F%22">Porta F</searchLink>; Department of Pediatric Hematology, Universitá degli Studi di Brescia, Brescia, Italy.<br /><searchLink fieldCode="AU" term="%22Bruno+B%22">Bruno B</searchLink>; Unité d'Hématologie Pédiatrique, Lille University Hospital, Lille, France.<br /><searchLink fieldCode="AU" term="%22Zecca+M%22">Zecca M</searchLink>; Pediatric Hematology/Oncology, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy.<br /><searchLink fieldCode="AU" term="%22Aksoylar+S%22">Aksoylar S</searchLink>; Division of Pediatric Hemathology and Oncology, Department of Pediatrics, Ege University Medical Faculty, Izmir, Turkey.<br /><searchLink fieldCode="AU" term="%22Barlogis+V%22">Barlogis V</searchLink>; Pediatric Haematology Department, Timone Enfant, Assistance Publique-Hôpitaux de Marseilles, Aix-Marseille University, Marseille, France.<br /><searchLink fieldCode="AU" term="%22Schuetz+C%22">Schuetz C</searchLink>; Department of Pediatrics, Medizinische Fakultät Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.; German Center for Child and Adolescent Health, Dresden, Germany.<br /><searchLink fieldCode="AU" term="%22Buechner+J%22">Buechner J</searchLink>; Department of Pediatric Hematology and Oncology, Oslo University Hospital, Oslo, Norway.<br /><searchLink fieldCode="AU" term="%22Faraci+M%22">Faraci M</searchLink>; Department of Hematology, Oncology, and Stem Cell Transplantation, IRCCS Istituto Giannina Gaslini, Genoa, Italy.<br /><searchLink fieldCode="AU" term="%22Wehr+C%22">Wehr C</searchLink>; Department of Hematology, Oncology, and Stem Cell Transplantation, Faculty of Medicine and Medical Center, University of Freiburg, Freiburg im Breisgau, Germany.<br /><searchLink fieldCode="AU" term="%22Holter+W%22">Holter W</searchLink>; Department of Pediatric Haematology and Oncology, St. Anna Children's Hospital, Department of Pediatrics and Adolescent Medicine, Medical University of Vienna, Vienna, Austria.<br /><searchLink fieldCode="AU" term="%22Mellgren+K%22">Mellgren K</searchLink>; Pediatric Clinical Unit, Queen Silvia Children's Hospital, Gothenburg, Sweden.; Department of Paediatrics, Institute for Clinical Sciences, Sahlgrenska Academy, University of Gothenburg, Gothenburg, Sweden.<br /><searchLink fieldCode="AU" term="%22Locatelli+F%22">Locatelli F</searchLink>; Department of Paediatric Hematology and Oncology, Bambino Gesù Children's Hospital, Istituto di Ricovero e Cura a Carattere Scientifico and Catholic University of the Sacred Heart, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Martinez+AP%22">Martinez AP</searchLink>; Department of Paediatric Hemato-Oncology, Hospital Universitario La Paz, Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Suarez+F%22">Suarez F</searchLink>; Department of Adult Hematology, Necker-Enfants Malades University Hospital and Centre de Référence des déficits Immunitaires Héréditaires, Assistance Publique-Hôpitaux de Paris, INSERM U1163, Imagine Institute, Université Paris Cité, Paris, France.<br /><searchLink fieldCode="AU" term="%22Moshous+D%22">Moshous D</searchLink>; Pediatric Unit of Immunology, Hematology, and Rheumatology, Necker Hospital, Paris, France.<br /><searchLink fieldCode="AU" term="%22Gennery+AR%22">Gennery AR</searchLink>; Translational and Clinical Research Institute, Newcastle University, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Balashov+D%22">Balashov D</searchLink>; Department of Pediatric Hematology, Oncology, and Immunology, Dmitry Rogachev National Medical Research Center, Moscow, Russia.<br /><searchLink fieldCode="AU" term="%22Albert+MH%22">Albert MH</searchLink>; Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, Ludwig Maximillian University of Munich, Munich, Germany.<br /><searchLink fieldCode="AU" term="%22Slatter+M%22">Slatter M</searchLink>; Translational and Clinical Research Institute, Newcastle University, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Güngör+T%22">Güngör T</searchLink>; Department of Stem Cell Transplantation, University Children's Hospital, Zürich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Neven+B%22">Neven B</searchLink>; Pediatric Unit of Immunology, Hematology, and Rheumatology, Necker Hospital, Paris, France.
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