COVID- 19 in patients affected by red blood cell disorders, results from the European registry ERN-EuroBloodNet.

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Title: COVID- 19 in patients affected by red blood cell disorders, results from the European registry ERN-EuroBloodNet.
Authors: Velasco Puyo P; Pediatric Oncology and Hematology, Vall d'Hebron Barcelona Hospital, Passeig Vall Hebron 129, 08035, Barcelona, Spain. Pablo.velascopuyo@vallhebron.cat., Christou S; Thalassaemia Clinic, Archbishop Makarios III Hospital (NAMIII), Nicosia, Cyprus., Campisi S; Medical Area Department, ASP 8 - P.O. Umberto I, Siracusa, Italy., Rodríguez-Sánchez MA; Rare Anemia Disorders Research Laboratory, Cancer and Blood Disorders in Children, Vall d'Hebron Research Institute, Barcelona, Spain., Reidel S; Rare Anemia Disorders Research Laboratory, Cancer and Blood Disorders in Children, Vall d'Hebron Research Institute, Barcelona, Spain., Perez-Hoyo S; Biostatistics and Bioinformatics Unit, Vall d'Hebron Research Unit (VHIR), Barcelona, Spain., Mota M; Biostatistics and Bioinformatics Unit, Vall d'Hebron Research Unit (VHIR), Barcelona, Spain., Savvidou I; Thalassaemia Clinic, Archbishop Makarios III Hospital (NAMIII), Nicosia, Cyprus., Rekleiti A; Thalassaemia Clinic, Archbishop Makarios III Hospital (NAMIII), Nicosia, Cyprus., Salvo A; Medical Area Department, ASP 8 - P.O. Umberto I, Siracusa, Italy., Voi V; Department of Clinical and Biological Science, AOU San Luigi Gonzaga, University of Turin, Turin, Italy., Ferrero GB; Department of Clinical and Biological Science, AOU San Luigi Gonzaga, University of Turin, Turin, Italy., Mandrile G; Department of Clinical and Biological Science, AOU San Luigi Gonzaga, University of Turin, Turin, Italy., Gaglioti CM; Department of Clinical and Biological Science, AOU San Luigi Gonzaga, University of Turin, Turin, Italy., Cela E; Pediatric Hematology and Oncology Unit, Hospital General Universitario Gregorio Marañón, Universidad Complutense de Madrid, Madrid, Spain., Ponce-Salas B; Pediatric Hematology and Oncology Unit, Hospital General Universitario Gregorio Marañón, Universidad Complutense de Madrid, Madrid, Spain., Bardón-Cancho EJ; Pediatric Hematology and Oncology Unit, Hospital General Universitario Gregorio Marañón, Universidad Complutense de Madrid, Madrid, Spain., Flevari P; Centre of Excellence in Rare Hematological Diseases-Hemoglobinopathies, 'Laiko' General Hospital of Athens, Athens, Greece., Voskaridou-Dimoula E; Centre of Excellence in Rare Hematological Diseases-Hemoglobinopathies, 'Laiko' General Hospital of Athens, Athens, Greece., Nur E; Clinical Hematology, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands., Biemond BJ; Clinical Hematology, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands., Delaporta P; First Department of Pediatrics, Thalassemia Unit, National and Kapodistrian University of Athens, Athens, Greece.; Aghia Sophia' Children's Hospital, ERN-EuroBloodNet Center, Athens, Greece., Beneitez-Pastor D; Hematology Department, Hospital Universitari Vall d'Hebron, Barcelona, Spain., Collado Gimbert A; Pediatric Oncology and Hematology, Vall d'Hebron Barcelona Hospital, Passeig Vall Hebron 129, 08035, Barcelona, Spain., Spasiano A; Malalttie Rare del Globulo Rosso, AORN A. Cardarelli, Naples, Italy., Besse-Hammer T; Clinical Research, CHU Brugmann, Brussels, Belgium., Lafiatis IG; Thalassemia and Sickle Cell Disease Unit, 'Vostanio' General Hospital of Mytilene, Mytilene, Greece., Dedeken L; Pediatric Hemato-Oncology, Hôpital Universitaire Des Enfants Reine Fabiola, H.U.B., Brussels, Belgium., Raso S; Department of Hematology and Rare Diseases, V Cervello Hospital, Azienda Ospedaliera Ospedali Riuniti Villa Sofia-Cervello, Palermo, Italy., Ruiz-Llobet A; Service of Pediatric Hematology, Hospital Sant Joan de Déu, Universitat de Barcelona, Institut de Recerca Hospital Sant Joan de Déu, ERN-EuroBloodNet Member, Barcelona, Spain., Bagnato S; Talasemia, Ospedale di Lentini, Lentini, Italy., Labarque V; Department of Pediatric Hemato-Oncology, University Hospitals Leuven, Louvain, Belgium.; Department of Cardiovascular Sciences, Centre for Molecular and Vascular Biology, KU Leuven, Louvain, Belgium., Glenthøj A; Department of Hematology, Copenhagen University Hospital - Rigshospitalet, Copenhagen, Denmark., Ruffo GB; U.O. Ematologia Con Talassemia, ARNAS Civico di Cristina Benfratelli, Palermo, Italy., Guerzoni ME; Pediatrics Unit, Department of Medical and Surgical Sciences for Mother Children and Adults, University of Modena and Reggio Emilia, Modena, Italy., Hafraoui K; Hematology, CHU Liège, Liège, Belgium., Pistoia L; Department of Radiology, Fondazione G. Monasterio CNR - Regione Toscana, Pisa, Italy., Rosso R; UOSD Talassemia, AOU Policlinico 'G. Rodolico - San Marco', Catania, Italy., Tagliaferri L; Department of Pediatric Oncology, Hematology and Immunology, Hopp-Children's Cancer Center (KiTZ) Heidelberg, University of Heidelberg, Heidelberg, Germany., Gonzalez-Urdiales P; Pediatric Oncology and Hematology Department, Hospital Universitario Cruces, Barakaldo, Spain., Benghiat FS; Clinic of Red Blood Cell Pathologies, Hematology Unit, Hôpital Erasme, Brussels, Belgium., de Montalembert M; Reference Centre for Sickle Cell Disease, Department of General Pediatrics and Pediatric Infectious Diseases, Necker-Enfants Malades Hospital, Assistance Publique-Hôpitaux de Paris (AP-HP), Université Paris Cité, Paris, France., Teles MJ; Laboratory Hematology, Centro Hospitalar Universitario de Santo Antonio, Porto, Portugal., Vanderfaeillie A; Pediatrics, UMC St Pierre, Brussels, Belgium., Bertoni E; Pediatric Onco-Hematology and Bone Marrow Transplant Unit, Children's Hospital, ASST Spedali Civili, Brescia, Italy., Cuzzubbo D; HSCT and Cellular Therapy Unit, Department of Paediatric Haematology-Oncology, 'Anna Meyer' Children's Hospital, Florence, Italy., Ferreira T; Pediatric Department, Hospital Fernando Fonseca, Amadora, Portugal., Saunders CJ; Haematology Department, Hospital Santo António Dos Capuchos - Centro Hospitalar Universitário Lisboa Central, Lisbon, Portugal., Stiakaki E; Department of Pediatric Hematology-Oncology and Autologous Hematopoietic Stem Cell Transplantation Unit, University Hospital of Heraklion, University of Crete, Heraklion, Greece., Van de Velde AL; HematologyAntwerp University Hospital, University of Antwerp, Edegem, Belgium., Diamantidis MD; Department of Haematology, Thalassemia and Sickle Cell Disease Unit, General Hospital of Larissa, Larissa, Greece., Kerkhoffs JH; Hematology, HagaZiekenhuis, The Hague, The Netherlands., Oliveira MI; Pediatric Hematology Unit, Hospital D. Estefânia, ULS S. José, Lisbon, Portugal., Quota A; Medicine Department, UOSD Talasemia Vittorio Emanuele Hospital, Gela, Italy., Russo R; Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Naples, Italy.; CEINGE - Biotecnologie Avanzate Franco Salvatore, Naples, Italy., Van Damme A; Department of Pediatric Hematology and Oncology, Saint Luc University Hospital, Brussels, Belgium., Argüello Marina M; Hematology, Hospital Universitario Príncipe de Asturias, Madrid, Spain., Lorite Reggiori M; Pediatric Oncology Unit, Pediatric Service, Son Espases Hospital, Palma, Spain., Rijneveld AW; Hematology, Erasmus MC, Rotterdam, The Netherlands., Rodríguez Gallego A; Ethics Committees Support Unit, Vall d'Hebron Research Institute, Barcelona, Spain.; Clinical Pharmacology Service, Hospital Universitari Vall d'Hebron, Barcelona, Spain., Colombatti R; Department of Women's and Children's Health, Azienda Ospedale-Università di Padova, Padua, Italy., Iolascon A; Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Naples, Italy.; CEINGE - Biotecnologie Avanzate Franco Salvatore, Naples, Italy., Taher A; Division of Hematology and Oncology, Department of Internal Medicine, American University of Beirut Medical Center, Beirut, Lebanon., Gulbis B; Hôpital Universitaire de Bruxelles, Université Libre de Bruxelles, LHUB-ULB, Brussels, Belgium., Roy NBA; Oxford University Hospitals NHS Foundation Trust, Oxford, UK.; University of Oxford, Oxford, UK., Mañú-Pereira MDM; Pediatric Oncology and Hematology, Vall d'Hebron Barcelona Hospital, Passeig Vall Hebron 129, 08035, Barcelona, Spain.; Rare Anemia Disorders Research Laboratory, Cancer and Blood Disorders in Children, Vall d'Hebron Research Institute, Barcelona, Spain.
Source: Orphanet journal of rare diseases [Orphanet J Rare Dis] 2025 Apr 16; Vol. 20 (1), pp. 183. Date of Electronic Publication: 2025 Apr 16.
Publication Type: Journal Article
Journal Info: Publisher: BioMed Central Country of Publication: England NLM ID: 101266602 Publication Model: Electronic Cited Medium: Internet ISSN: 1750-1172 (Electronic) Linking ISSN: 17501172 NLM ISO Abbreviation: Orphanet J Rare Dis Subsets: MEDLINE
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  Data: COVID- 19 in patients affected by red blood cell disorders, results from the European registry ERN-EuroBloodNet.
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  Data: <searchLink fieldCode="AU" term="%22Velasco+Puyo+P%22">Velasco Puyo P</searchLink>; Pediatric Oncology and Hematology, Vall d'Hebron Barcelona Hospital, Passeig Vall Hebron 129, 08035, Barcelona, Spain. Pablo.velascopuyo@vallhebron.cat.<br /><searchLink fieldCode="AU" term="%22Christou+S%22">Christou S</searchLink>; Thalassaemia Clinic, Archbishop Makarios III Hospital (NAMIII), Nicosia, Cyprus.<br /><searchLink fieldCode="AU" term="%22Campisi+S%22">Campisi S</searchLink>; Medical Area Department, ASP 8 - P.O. Umberto I, Siracusa, Italy.<br /><searchLink fieldCode="AU" term="%22Rodríguez-Sánchez+MA%22">Rodríguez-Sánchez MA</searchLink>; Rare Anemia Disorders Research Laboratory, Cancer and Blood Disorders in Children, Vall d'Hebron Research Institute, Barcelona, Spain.<br /><searchLink fieldCode="AU" term="%22Reidel+S%22">Reidel S</searchLink>; Rare Anemia Disorders Research Laboratory, Cancer and Blood Disorders in Children, Vall d'Hebron Research Institute, Barcelona, Spain.<br /><searchLink fieldCode="AU" term="%22Perez-Hoyo+S%22">Perez-Hoyo S</searchLink>; Biostatistics and Bioinformatics Unit, Vall d'Hebron Research Unit (VHIR), Barcelona, Spain.<br /><searchLink fieldCode="AU" term="%22Mota+M%22">Mota M</searchLink>; Biostatistics and Bioinformatics Unit, Vall d'Hebron Research Unit (VHIR), Barcelona, Spain.<br /><searchLink fieldCode="AU" term="%22Savvidou+I%22">Savvidou I</searchLink>; Thalassaemia Clinic, Archbishop Makarios III Hospital (NAMIII), Nicosia, Cyprus.<br /><searchLink fieldCode="AU" term="%22Rekleiti+A%22">Rekleiti A</searchLink>; Thalassaemia Clinic, Archbishop Makarios III Hospital (NAMIII), Nicosia, Cyprus.<br /><searchLink fieldCode="AU" term="%22Salvo+A%22">Salvo A</searchLink>; Medical Area Department, ASP 8 - P.O. Umberto I, Siracusa, Italy.<br /><searchLink fieldCode="AU" term="%22Voi+V%22">Voi V</searchLink>; Department of Clinical and Biological Science, AOU San Luigi Gonzaga, University of Turin, Turin, Italy.<br /><searchLink fieldCode="AU" term="%22Ferrero+GB%22">Ferrero GB</searchLink>; Department of Clinical and Biological Science, AOU San Luigi Gonzaga, University of Turin, Turin, Italy.<br /><searchLink fieldCode="AU" term="%22Mandrile+G%22">Mandrile G</searchLink>; Department of Clinical and Biological Science, AOU San Luigi Gonzaga, University of Turin, Turin, Italy.<br /><searchLink fieldCode="AU" term="%22Gaglioti+CM%22">Gaglioti CM</searchLink>; Department of Clinical and Biological Science, AOU San Luigi Gonzaga, University of Turin, Turin, Italy.<br /><searchLink fieldCode="AU" term="%22Cela+E%22">Cela E</searchLink>; Pediatric Hematology and Oncology Unit, Hospital General Universitario Gregorio Marañón, Universidad Complutense de Madrid, Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Ponce-Salas+B%22">Ponce-Salas B</searchLink>; Pediatric Hematology and Oncology Unit, Hospital General Universitario Gregorio Marañón, Universidad Complutense de Madrid, Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Bardón-Cancho+EJ%22">Bardón-Cancho EJ</searchLink>; Pediatric Hematology and Oncology Unit, Hospital General Universitario Gregorio Marañón, Universidad Complutense de Madrid, Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Flevari+P%22">Flevari P</searchLink>; Centre of Excellence in Rare Hematological Diseases-Hemoglobinopathies, 'Laiko' General Hospital of Athens, Athens, Greece.<br /><searchLink fieldCode="AU" term="%22Voskaridou-Dimoula+E%22">Voskaridou-Dimoula E</searchLink>; Centre of Excellence in Rare Hematological Diseases-Hemoglobinopathies, 'Laiko' General Hospital of Athens, Athens, Greece.<br /><searchLink fieldCode="AU" term="%22Nur+E%22">Nur E</searchLink>; Clinical Hematology, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.<br /><searchLink fieldCode="AU" term="%22Biemond+BJ%22">Biemond BJ</searchLink>; Clinical Hematology, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands.<br /><searchLink fieldCode="AU" term="%22Delaporta+P%22">Delaporta P</searchLink>; First Department of Pediatrics, Thalassemia Unit, National and Kapodistrian University of Athens, Athens, Greece.; Aghia Sophia' Children's Hospital, ERN-EuroBloodNet Center, Athens, Greece.<br /><searchLink fieldCode="AU" term="%22Beneitez-Pastor+D%22">Beneitez-Pastor D</searchLink>; Hematology Department, Hospital Universitari Vall d'Hebron, Barcelona, Spain.<br /><searchLink fieldCode="AU" term="%22Collado+Gimbert+A%22">Collado Gimbert A</searchLink>; Pediatric Oncology and Hematology, Vall d'Hebron Barcelona Hospital, Passeig Vall Hebron 129, 08035, Barcelona, Spain.<br /><searchLink fieldCode="AU" term="%22Spasiano+A%22">Spasiano A</searchLink>; Malalttie Rare del Globulo Rosso, AORN A. Cardarelli, Naples, Italy.<br /><searchLink fieldCode="AU" term="%22Besse-Hammer+T%22">Besse-Hammer T</searchLink>; Clinical Research, CHU Brugmann, Brussels, Belgium.<br /><searchLink fieldCode="AU" term="%22Lafiatis+IG%22">Lafiatis IG</searchLink>; Thalassemia and Sickle Cell Disease Unit, 'Vostanio' General Hospital of Mytilene, Mytilene, Greece.<br /><searchLink fieldCode="AU" term="%22Dedeken+L%22">Dedeken L</searchLink>; Pediatric Hemato-Oncology, Hôpital Universitaire Des Enfants Reine Fabiola, H.U.B., Brussels, Belgium.<br /><searchLink fieldCode="AU" term="%22Raso+S%22">Raso S</searchLink>; Department of Hematology and Rare Diseases, V Cervello Hospital, Azienda Ospedaliera Ospedali Riuniti Villa Sofia-Cervello, Palermo, Italy.<br /><searchLink fieldCode="AU" term="%22Ruiz-Llobet+A%22">Ruiz-Llobet A</searchLink>; Service of Pediatric Hematology, Hospital Sant Joan de Déu, Universitat de Barcelona, Institut de Recerca Hospital Sant Joan de Déu, ERN-EuroBloodNet Member, Barcelona, Spain.<br /><searchLink fieldCode="AU" term="%22Bagnato+S%22">Bagnato S</searchLink>; Talasemia, Ospedale di Lentini, Lentini, Italy.<br /><searchLink fieldCode="AU" term="%22Labarque+V%22">Labarque V</searchLink>; Department of Pediatric Hemato-Oncology, University Hospitals Leuven, Louvain, Belgium.; Department of Cardiovascular Sciences, Centre for Molecular and Vascular Biology, KU Leuven, Louvain, Belgium.<br /><searchLink fieldCode="AU" term="%22Glenthøj+A%22">Glenthøj A</searchLink>; Department of Hematology, Copenhagen University Hospital - Rigshospitalet, Copenhagen, Denmark.<br /><searchLink fieldCode="AU" term="%22Ruffo+GB%22">Ruffo GB</searchLink>; U.O. Ematologia Con Talassemia, ARNAS Civico di Cristina Benfratelli, Palermo, Italy.<br /><searchLink fieldCode="AU" term="%22Guerzoni+ME%22">Guerzoni ME</searchLink>; Pediatrics Unit, Department of Medical and Surgical Sciences for Mother Children and Adults, University of Modena and Reggio Emilia, Modena, Italy.<br /><searchLink fieldCode="AU" term="%22Hafraoui+K%22">Hafraoui K</searchLink>; Hematology, CHU Liège, Liège, Belgium.<br /><searchLink fieldCode="AU" term="%22Pistoia+L%22">Pistoia L</searchLink>; Department of Radiology, Fondazione G. Monasterio CNR - Regione Toscana, Pisa, Italy.<br /><searchLink fieldCode="AU" term="%22Rosso+R%22">Rosso R</searchLink>; UOSD Talassemia, AOU Policlinico 'G. Rodolico - San Marco', Catania, Italy.<br /><searchLink fieldCode="AU" term="%22Tagliaferri+L%22">Tagliaferri L</searchLink>; Department of Pediatric Oncology, Hematology and Immunology, Hopp-Children's Cancer Center (KiTZ) Heidelberg, University of Heidelberg, Heidelberg, Germany.<br /><searchLink fieldCode="AU" term="%22Gonzalez-Urdiales+P%22">Gonzalez-Urdiales P</searchLink>; Pediatric Oncology and Hematology Department, Hospital Universitario Cruces, Barakaldo, Spain.<br /><searchLink fieldCode="AU" term="%22Benghiat+FS%22">Benghiat FS</searchLink>; Clinic of Red Blood Cell Pathologies, Hematology Unit, Hôpital Erasme, Brussels, Belgium.<br /><searchLink fieldCode="AU" term="%22de+Montalembert+M%22">de Montalembert M</searchLink>; Reference Centre for Sickle Cell Disease, Department of General Pediatrics and Pediatric Infectious Diseases, Necker-Enfants Malades Hospital, Assistance Publique-Hôpitaux de Paris (AP-HP), Université Paris Cité, Paris, France.<br /><searchLink fieldCode="AU" term="%22Teles+MJ%22">Teles MJ</searchLink>; Laboratory Hematology, Centro Hospitalar Universitario de Santo Antonio, Porto, Portugal.<br /><searchLink fieldCode="AU" term="%22Vanderfaeillie+A%22">Vanderfaeillie A</searchLink>; Pediatrics, UMC St Pierre, Brussels, Belgium.<br /><searchLink fieldCode="AU" term="%22Bertoni+E%22">Bertoni E</searchLink>; Pediatric Onco-Hematology and Bone Marrow Transplant Unit, Children's Hospital, ASST Spedali Civili, Brescia, Italy.<br /><searchLink fieldCode="AU" term="%22Cuzzubbo+D%22">Cuzzubbo D</searchLink>; HSCT and Cellular Therapy Unit, Department of Paediatric Haematology-Oncology, 'Anna Meyer' Children's Hospital, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Ferreira+T%22">Ferreira T</searchLink>; Pediatric Department, Hospital Fernando Fonseca, Amadora, Portugal.<br /><searchLink fieldCode="AU" term="%22Saunders+CJ%22">Saunders CJ</searchLink>; Haematology Department, Hospital Santo António Dos Capuchos - Centro Hospitalar Universitário Lisboa Central, Lisbon, Portugal.<br /><searchLink fieldCode="AU" term="%22Stiakaki+E%22">Stiakaki E</searchLink>; Department of Pediatric Hematology-Oncology and Autologous Hematopoietic Stem Cell Transplantation Unit, University Hospital of Heraklion, University of Crete, Heraklion, Greece.<br /><searchLink fieldCode="AU" term="%22Van+de+Velde+AL%22">Van de Velde AL</searchLink>; HematologyAntwerp University Hospital, University of Antwerp, Edegem, Belgium.<br /><searchLink fieldCode="AU" term="%22Diamantidis+MD%22">Diamantidis MD</searchLink>; Department of Haematology, Thalassemia and Sickle Cell Disease Unit, General Hospital of Larissa, Larissa, Greece.<br /><searchLink fieldCode="AU" term="%22Kerkhoffs+JH%22">Kerkhoffs JH</searchLink>; Hematology, HagaZiekenhuis, The Hague, The Netherlands.<br /><searchLink fieldCode="AU" term="%22Oliveira+MI%22">Oliveira MI</searchLink>; Pediatric Hematology Unit, Hospital D. Estefânia, ULS S. José, Lisbon, Portugal.<br /><searchLink fieldCode="AU" term="%22Quota+A%22">Quota A</searchLink>; Medicine Department, UOSD Talasemia Vittorio Emanuele Hospital, Gela, Italy.<br /><searchLink fieldCode="AU" term="%22Russo+R%22">Russo R</searchLink>; Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Naples, Italy.; CEINGE - Biotecnologie Avanzate Franco Salvatore, Naples, Italy.<br /><searchLink fieldCode="AU" term="%22Van+Damme+A%22">Van Damme A</searchLink>; Department of Pediatric Hematology and Oncology, Saint Luc University Hospital, Brussels, Belgium.<br /><searchLink fieldCode="AU" term="%22Argüello+Marina+M%22">Argüello Marina M</searchLink>; Hematology, Hospital Universitario Príncipe de Asturias, Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Lorite+Reggiori+M%22">Lorite Reggiori M</searchLink>; Pediatric Oncology Unit, Pediatric Service, Son Espases Hospital, Palma, Spain.<br /><searchLink fieldCode="AU" term="%22Rijneveld+AW%22">Rijneveld AW</searchLink>; Hematology, Erasmus MC, Rotterdam, The Netherlands.<br /><searchLink fieldCode="AU" term="%22Rodríguez+Gallego+A%22">Rodríguez Gallego A</searchLink>; Ethics Committees Support Unit, Vall d'Hebron Research Institute, Barcelona, Spain.; Clinical Pharmacology Service, Hospital Universitari Vall d'Hebron, Barcelona, Spain.<br /><searchLink fieldCode="AU" term="%22Colombatti+R%22">Colombatti R</searchLink>; Department of Women's and Children's Health, Azienda Ospedale-Università di Padova, Padua, Italy.<br /><searchLink fieldCode="AU" term="%22Iolascon+A%22">Iolascon A</searchLink>; Department of Molecular Medicine and Medical Biotechnology, University of Naples Federico II, Naples, Italy.; CEINGE - Biotecnologie Avanzate Franco Salvatore, Naples, Italy.<br /><searchLink fieldCode="AU" term="%22Taher+A%22">Taher A</searchLink>; Division of Hematology and Oncology, Department of Internal Medicine, American University of Beirut Medical Center, Beirut, Lebanon.<br /><searchLink fieldCode="AU" term="%22Gulbis+B%22">Gulbis B</searchLink>; Hôpital Universitaire de Bruxelles, Université Libre de Bruxelles, LHUB-ULB, Brussels, Belgium.<br /><searchLink fieldCode="AU" term="%22Roy+NBA%22">Roy NBA</searchLink>; Oxford University Hospitals NHS Foundation Trust, Oxford, UK.; University of Oxford, Oxford, UK.<br /><searchLink fieldCode="AU" term="%22Mañú-Pereira+MDM%22">Mañú-Pereira MDM</searchLink>; Pediatric Oncology and Hematology, Vall d'Hebron Barcelona Hospital, Passeig Vall Hebron 129, 08035, Barcelona, Spain.; Rare Anemia Disorders Research Laboratory, Cancer and Blood Disorders in Children, Vall d'Hebron Research Institute, Barcelona, Spain.
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  Data: <searchLink fieldCode="JN" term="%22101266602%22">Orphanet journal of rare diseases</searchLink> [Orphanet J Rare Dis] 2025 Apr 16; Vol. 20 (1), pp. 183. <i>Date of Electronic Publication: </i>2025 Apr 16.
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          Dates:
            – D: 16
              M: 04
              Text: 2025 Apr 16
              Type: published
              Y: 2025
          Identifiers:
            – Type: issn-electronic
              Value: 1750-1172
          Numbering:
            – Type: volume
              Value: 20
            – Type: issue
              Value: 1
          Titles:
            – TitleFull: Orphanet journal of rare diseases
              Type: main
ResultId 1