Mapping administration route-dependent transduction profiles of commonly used AAV variants in mice by barcode amplicon sequencing.

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Title: Mapping administration route-dependent transduction profiles of commonly used AAV variants in mice by barcode amplicon sequencing.
Authors: Abele S; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Alanis-Lobato G; Global Computational Biology & Digital Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Oti M; Global Computational Biology & Digital Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Rust W; Global Computational Biology & Digital Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Blazevic D; Eye Health & Research Beyond Borders, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Danner-Liskus J; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Mayer C; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Zimmermann G; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Zuckschwerdt K; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Schönberger T; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Gross P; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Lempp C; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Michelfelder S; Eye Health & Research Beyond Borders, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany., Strobel B; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.
Source: Molecular therapy. Methods & clinical development [Mol Ther Methods Clin Dev] 2025 Apr 14; Vol. 33 (2), pp. 101468. Date of Electronic Publication: 2025 Apr 14 (Print Publication: 2025).
Publication Type: Journal Article
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101624857 Publication Model: eCollection Cited Medium: Print ISSN: 2329-0501 (Print) Linking ISSN: 23290501 NLM ISO Abbreviation: Mol Ther Methods Clin Dev Subsets: PubMed not MEDLINE
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  Data: Mapping administration route-dependent transduction profiles of commonly used AAV variants in mice by barcode amplicon sequencing.
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  Data: <searchLink fieldCode="AU" term="%22Abele+S%22">Abele S</searchLink>; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Alanis-Lobato+G%22">Alanis-Lobato G</searchLink>; Global Computational Biology & Digital Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Oti+M%22">Oti M</searchLink>; Global Computational Biology & Digital Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Rust+W%22">Rust W</searchLink>; Global Computational Biology & Digital Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Blazevic+D%22">Blazevic D</searchLink>; Eye Health & Research Beyond Borders, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Danner-Liskus+J%22">Danner-Liskus J</searchLink>; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Mayer+C%22">Mayer C</searchLink>; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Zimmermann+G%22">Zimmermann G</searchLink>; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Zuckschwerdt+K%22">Zuckschwerdt K</searchLink>; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Schönberger+T%22">Schönberger T</searchLink>; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Gross+P%22">Gross P</searchLink>; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Lempp+C%22">Lempp C</searchLink>; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Michelfelder+S%22">Michelfelder S</searchLink>; Eye Health & Research Beyond Borders, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.<br /><searchLink fieldCode="AU" term="%22Strobel+B%22">Strobel B</searchLink>; Global Drug Discovery Sciences, Boehringer Ingelheim Pharma GmbH & Co. KG, 88397 Biberach, Germany.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101624857 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Print <i>ISSN: </i>2329-0501 (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2223290501%22">23290501 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther Methods Clin Dev <i>Subsets: </i>PubMed not MEDLINE
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              Text: 2025 Apr 14
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