| Authors: |
Stratton MP; Center for Genetic Diseases, Chicago Medical School, Rosalind Franklin University of Medicine and Science, North Chicago, IL, 60064, USA.; School of Graduate and Postdoctoral Studies, Rosalind Franklin University of Medicine and Science, North Chicago, IL, 60064, USA., Centa JL; Center for Genetic Diseases, Chicago Medical School, Rosalind Franklin University of Medicine and Science, North Chicago, IL, 60064, USA.; Department of Pharmacology, University of Michigan Medical School, Ann Arbor, MI, 48109, USA., Swier VJ; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, 57104, USA., Pfeifer WL; Department of Ophthalmology and Visual Sciences, Institute for Vision Research, Carver College of Medicine, University of Iowa, Iowa City, IA, 52242, USA., Booth CD; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, 57104, USA., Albert K; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, 57104, USA., Hunyara JL; Ionis Pharmaceuticals, Carlsbad, CA, 92010, USA., Rechtzigel MJ; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, 57104, USA., Duelli FJ; Department of Pharmacology, University of Michigan Medical School, Ann Arbor, MI, 48109, USA., Leppert HG; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, 57104, USA., Rigo F; Ionis Pharmaceuticals, Carlsbad, CA, 92010, USA., Smit T; Exemplar Genetics, Coralville, IA 52241, USA., Jafar-Nejad P; Ionis Pharmaceuticals, Carlsbad, CA, 92010, USA., Weimer JM; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD, 57104, USA.; Department of Pediatrics, Sanford School of Medicine, University of South Dakota, Sioux Falls, SD, 57104, USA., Drack AV; Department of Ophthalmology and Visual Sciences, Institute for Vision Research, Carver College of Medicine, University of Iowa, Iowa City, IA, 52242, USA.; Stead Family Department of Pediatrics, University of Iowa, Iowa City, IA, 52242, USA., Hastings ML; Center for Genetic Diseases, Chicago Medical School, Rosalind Franklin University of Medicine and Science, North Chicago, IL, 60064, USA.; Department of Pharmacology, University of Michigan Medical School, Ann Arbor, MI, 48109, USA. |