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Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts.

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Title: Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts.
Authors: Pasternak A; Department of Physical and Occupational Therapy Services, Boston Children's Hospital, MA., McDermott MP; Department of Biostatistics and Compulational Biology, University of Rochester, NY., Montes J; Department of Rehabilitation and Regenerative Medicine, Columbia University Irving Medical Center, New York, NY., Glanzman AM; Department of Physical Therapy, Children's Hospital of Philadelphia, PA., Coratti G; Centro Clinico Nemo, U.O.C. Neuropsichiatria Infantile Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy., Dunaway Young S; Departments of Neurology and Clinical Neurosciences, Stanford University, Palo Alto, CA., Duong TT; Departments of Neurology and Clinical Neurosciences, Stanford University, Palo Alto, CA., Martens WB; Department of Neurology, University of Rochester, NY., Day JW; Departments of Neurology and Clinical Neurosciences, Stanford University, Palo Alto, CA., Zolkipli-Cunningham Z; Division of Human Genetics, Children's Hospital of Philadelphia, University of Philadelphia, PA., Sansone VA; The NEMO Center in Milan, Neurorehabilitation Unit, University of Milan, ASST Niguarda Hospital, Italy., D'Amico A; Unit of Neuromuscular and Neurodegenerative Disorders, IRCCS Bambino Gesu Children's Hospital, Rome, Italy., Messina S; Department of Clinical and Experimental Medicine and Centro Clinico Nemo Sud, University of Messina, Italy., Bruno C; Center of Experimental and Translational Myology, IRCCS Isituto Giannina Gaslini, Genoa, Italy., Mercuri E; Centro Clinico Nemo, U.O.C. Neuropsichiatria Infantile Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy., De Vivo DC; Department of Neurology, Columbia University Irving Medical Center, New York, NY; and., Darras BT; Department of Neurology, Boston Children's Hospital, Harvard Medical School, MA.
Corporate Authors: as the Pediatric Neuromuscular Clinical Research (PNCR) Network and the International SMA Consortium (iSMAc)
Source: Neurology [Neurology] 2025 Jul 22; Vol. 105 (2), pp. e213839. Date of Electronic Publication: 2025 Jun 27.
Publication Type: Journal Article
Journal Info: Publisher: Lippincott Williams & Wilkins Country of Publication: United States NLM ID: 0401060 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1526-632X (Electronic) Linking ISSN: 00283878 NLM ISO Abbreviation: Neurology Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts.
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  Data: <searchLink fieldCode="AU" term="%22Pasternak+A%22">Pasternak A</searchLink>; Department of Physical and Occupational Therapy Services, Boston Children's Hospital, MA.<br /><searchLink fieldCode="AU" term="%22McDermott+MP%22">McDermott MP</searchLink>; Department of Biostatistics and Compulational Biology, University of Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Montes+J%22">Montes J</searchLink>; Department of Rehabilitation and Regenerative Medicine, Columbia University Irving Medical Center, New York, NY.<br /><searchLink fieldCode="AU" term="%22Glanzman+AM%22">Glanzman AM</searchLink>; Department of Physical Therapy, Children's Hospital of Philadelphia, PA.<br /><searchLink fieldCode="AU" term="%22Coratti+G%22">Coratti G</searchLink>; Centro Clinico Nemo, U.O.C. Neuropsichiatria Infantile Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Dunaway+Young+S%22">Dunaway Young S</searchLink>; Departments of Neurology and Clinical Neurosciences, Stanford University, Palo Alto, CA.<br /><searchLink fieldCode="AU" term="%22Duong+TT%22">Duong TT</searchLink>; Departments of Neurology and Clinical Neurosciences, Stanford University, Palo Alto, CA.<br /><searchLink fieldCode="AU" term="%22Martens+WB%22">Martens WB</searchLink>; Department of Neurology, University of Rochester, NY.<br /><searchLink fieldCode="AU" term="%22Day+JW%22">Day JW</searchLink>; Departments of Neurology and Clinical Neurosciences, Stanford University, Palo Alto, CA.<br /><searchLink fieldCode="AU" term="%22Zolkipli-Cunningham+Z%22">Zolkipli-Cunningham Z</searchLink>; Division of Human Genetics, Children's Hospital of Philadelphia, University of Philadelphia, PA.<br /><searchLink fieldCode="AU" term="%22Sansone+VA%22">Sansone VA</searchLink>; The NEMO Center in Milan, Neurorehabilitation Unit, University of Milan, ASST Niguarda Hospital, Italy.<br /><searchLink fieldCode="AU" term="%22D'Amico+A%22">D'Amico A</searchLink>; Unit of Neuromuscular and Neurodegenerative Disorders, IRCCS Bambino Gesu Children's Hospital, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22Messina+S%22">Messina S</searchLink>; Department of Clinical and Experimental Medicine and Centro Clinico Nemo Sud, University of Messina, Italy.<br /><searchLink fieldCode="AU" term="%22Bruno+C%22">Bruno C</searchLink>; Center of Experimental and Translational Myology, IRCCS Isituto Giannina Gaslini, Genoa, Italy.<br /><searchLink fieldCode="AU" term="%22Mercuri+E%22">Mercuri E</searchLink>; Centro Clinico Nemo, U.O.C. Neuropsichiatria Infantile Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.<br /><searchLink fieldCode="AU" term="%22De+Vivo+DC%22">De Vivo DC</searchLink>; Department of Neurology, Columbia University Irving Medical Center, New York, NY; and.<br /><searchLink fieldCode="AU" term="%22Darras+BT%22">Darras BT</searchLink>; Department of Neurology, Boston Children's Hospital, Harvard Medical School, MA.
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  Data: <searchLink fieldCode="JN" term="%220401060%22">Neurology</searchLink> [Neurology] 2025 Jul 22; Vol. 105 (2), pp. e213839. <i>Date of Electronic Publication: </i>2025 Jun 27.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Lippincott+Williams+%26+Wilkins%22">Lippincott Williams & Wilkins </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>0401060 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1526-632X (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2200283878%22">00283878 </searchLink><i>NLM ISO Abbreviation: </i>Neurology <i>Subsets: </i>MEDLINE
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