Realizing the therapeutic potential of rapid knockdown of transthyretin via RNA interference in transthyretin amyloidosis.

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Title: Realizing the therapeutic potential of rapid knockdown of transthyretin via RNA interference in transthyretin amyloidosis.
Authors: Grogan M; Cardiovascular Medicine Department, Mayo Clinic, Rochester, MN 55905, USA., Sheikh FH; MedStar Heart and Vascular Institute, MedStar Health/Georgetown University School of Medicine, Washington, DC 20007, USA., Sperry BW; Saint Luke's Mid America Heart Institute, Kansas City, MO 64111, USA., Sweetser MT; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA., Capocelli K; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA., Roblin S; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA., Witteles R; Division of Cardiovascular Medicine, Stanford University School of Medicine, Stanford, CA 94305, USA.
Source: Molecular therapy. Nucleic acids [Mol Ther Nucleic Acids] 2025 Jun 10; Vol. 36 (3), pp. 102590. Date of Electronic Publication: 2025 Jun 10 (Print Publication: 2025).
Publication Type: Journal Article; Review
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101581621 Publication Model: eCollection Cited Medium: Print ISSN: 2162-2531 (Print) Linking ISSN: 21622531 NLM ISO Abbreviation: Mol Ther Nucleic Acids Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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  Data: Realizing the therapeutic potential of rapid knockdown of transthyretin via RNA interference in transthyretin amyloidosis.
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  Data: <searchLink fieldCode="AU" term="%22Grogan+M%22">Grogan M</searchLink>; Cardiovascular Medicine Department, Mayo Clinic, Rochester, MN 55905, USA.<br /><searchLink fieldCode="AU" term="%22Sheikh+FH%22">Sheikh FH</searchLink>; MedStar Heart and Vascular Institute, MedStar Health/Georgetown University School of Medicine, Washington, DC 20007, USA.<br /><searchLink fieldCode="AU" term="%22Sperry+BW%22">Sperry BW</searchLink>; Saint Luke's Mid America Heart Institute, Kansas City, MO 64111, USA.<br /><searchLink fieldCode="AU" term="%22Sweetser+MT%22">Sweetser MT</searchLink>; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.<br /><searchLink fieldCode="AU" term="%22Capocelli+K%22">Capocelli K</searchLink>; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.<br /><searchLink fieldCode="AU" term="%22Roblin+S%22">Roblin S</searchLink>; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.<br /><searchLink fieldCode="AU" term="%22Witteles+R%22">Witteles R</searchLink>; Division of Cardiovascular Medicine, Stanford University School of Medicine, Stanford, CA 94305, USA.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101581621 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Print <i>ISSN: </i>2162-2531 (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2221622531%22">21622531 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther Nucleic Acids <i>Subsets: </i>PubMed not MEDLINE
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