Predicting Residual 21-Hydroxylase Enzymatic Activity in Pediatric and Adult Congenital Adrenal Hyperplasia Patients: Towards Individualized Therapy.

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Title: Predicting Residual 21-Hydroxylase Enzymatic Activity in Pediatric and Adult Congenital Adrenal Hyperplasia Patients: Towards Individualized Therapy.
Authors: Bindellini D; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.; Graduate Research Training Program PharMetrX, Berlin, Germany., Michelet R; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany., Mirasbekov Y; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.; Graduate Research Training Program PharMetrX, Berlin, Germany., Lao Q; National Institutes of Health Clinical Center, Bethesda, Maryland, USA., Sukin C; National Institutes of Health Clinical Center, Bethesda, Maryland, USA., Huisinga W; Graduate Research Training Program PharMetrX, Berlin, Germany.; Institute of Mathematics, University of Potsdam, Potsdam, Germany., Merke DP; National Institutes of Health Clinical Center, Bethesda, Maryland, USA.; Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA., Kloft C; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.; Graduate Research Training Program PharMetrX, Berlin, Germany.
Source: CPT: pharmacometrics & systems pharmacology [CPT Pharmacometrics Syst Pharmacol] 2025 Nov; Vol. 14 (11), pp. 1869-1881. Date of Electronic Publication: 2025 Jul 27.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Wiley Country of Publication: United States NLM ID: 101580011 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2163-8306 (Electronic) Linking ISSN: 21638306 NLM ISO Abbreviation: CPT Pharmacometrics Syst Pharmacol Subsets: MEDLINE
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  Data: Predicting Residual 21-Hydroxylase Enzymatic Activity in Pediatric and Adult Congenital Adrenal Hyperplasia Patients: Towards Individualized Therapy.
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  Data: <searchLink fieldCode="AU" term="%22Bindellini+D%22">Bindellini D</searchLink>; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.; Graduate Research Training Program PharMetrX, Berlin, Germany.<br /><searchLink fieldCode="AU" term="%22Michelet+R%22">Michelet R</searchLink>; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.<br /><searchLink fieldCode="AU" term="%22Mirasbekov+Y%22">Mirasbekov Y</searchLink>; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.; Graduate Research Training Program PharMetrX, Berlin, Germany.<br /><searchLink fieldCode="AU" term="%22Lao+Q%22">Lao Q</searchLink>; National Institutes of Health Clinical Center, Bethesda, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Sukin+C%22">Sukin C</searchLink>; National Institutes of Health Clinical Center, Bethesda, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Huisinga+W%22">Huisinga W</searchLink>; Graduate Research Training Program PharMetrX, Berlin, Germany.; Institute of Mathematics, University of Potsdam, Potsdam, Germany.<br /><searchLink fieldCode="AU" term="%22Merke+DP%22">Merke DP</searchLink>; National Institutes of Health Clinical Center, Bethesda, Maryland, USA.; Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Kloft+C%22">Kloft C</searchLink>; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.; Graduate Research Training Program PharMetrX, Berlin, Germany.
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  Data: <searchLink fieldCode="JN" term="%22101580011%22">CPT: pharmacometrics & systems pharmacology</searchLink> [CPT Pharmacometrics Syst Pharmacol] 2025 Nov; Vol. 14 (11), pp. 1869-1881. <i>Date of Electronic Publication: </i>2025 Jul 27.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Wiley%22">Wiley </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101580011 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2163-8306 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2221638306%22">21638306 </searchLink><i>NLM ISO Abbreviation: </i>CPT Pharmacometrics Syst Pharmacol <i>Subsets: </i>MEDLINE
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        Value: 10.1002/psp4.70086
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      – TitleFull: Predicting Residual 21-Hydroxylase Enzymatic Activity in Pediatric and Adult Congenital Adrenal Hyperplasia Patients: Towards Individualized Therapy.
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              Text: 2025 Nov
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