Predicting Residual 21-Hydroxylase Enzymatic Activity in Pediatric and Adult Congenital Adrenal Hyperplasia Patients: Towards Individualized Therapy.
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| Title: | Predicting Residual 21-Hydroxylase Enzymatic Activity in Pediatric and Adult Congenital Adrenal Hyperplasia Patients: Towards Individualized Therapy. |
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| Authors: | Bindellini D; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.; Graduate Research Training Program PharMetrX, Berlin, Germany., Michelet R; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany., Mirasbekov Y; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.; Graduate Research Training Program PharMetrX, Berlin, Germany., Lao Q; National Institutes of Health Clinical Center, Bethesda, Maryland, USA., Sukin C; National Institutes of Health Clinical Center, Bethesda, Maryland, USA., Huisinga W; Graduate Research Training Program PharMetrX, Berlin, Germany.; Institute of Mathematics, University of Potsdam, Potsdam, Germany., Merke DP; National Institutes of Health Clinical Center, Bethesda, Maryland, USA.; Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA., Kloft C; Department of Clinical Pharmacy and Biochemistry, Institute of Pharmacy, Freie Universitaet Berlin, Berlin, Germany.; Graduate Research Training Program PharMetrX, Berlin, Germany. |
| Source: | CPT: pharmacometrics & systems pharmacology [CPT Pharmacometrics Syst Pharmacol] 2025 Nov; Vol. 14 (11), pp. 1869-1881. Date of Electronic Publication: 2025 Jul 27. |
| Publication Type: | Journal Article; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: Wiley Country of Publication: United States NLM ID: 101580011 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2163-8306 (Electronic) Linking ISSN: 21638306 NLM ISO Abbreviation: CPT Pharmacometrics Syst Pharmacol Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 2163-8306 |
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| DOI: | 10.1002/psp4.70086 |