Transduction of hematopoietic stem and progenitor cells by an MECP2 lentiviral vector improves Rett syndrome phenotypes.
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| Title: | Transduction of hematopoietic stem and progenitor cells by an MECP2 lentiviral vector improves Rett syndrome phenotypes. |
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| Authors: | Anderson JS; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States., Silverman JL; Department of Psychiatry and Behavioral Sciences, University of California Davis Medical Center, Sacramento, CA, United States., Lodigiani AL; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States., Barbaduomo CM; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States., Beegle JR; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States. |
| Source: | Frontiers in drug discovery [Front Drug Discov (Lausanne)] 2025; Vol. 5. Date of Electronic Publication: 2025 Feb 20. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Frontiers Media S.A Country of Publication: Switzerland NLM ID: 9918350785506676 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2674-0338 (Electronic) Linking ISSN: 26740338 NLM ISO Abbreviation: Front Drug Discov (Lausanne) Subsets: PubMed not MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 2674-0338 |
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| DOI: | 10.3389/fddsv.2025.1545391 |