Transduction of hematopoietic stem and progenitor cells by an MECP2 lentiviral vector improves Rett syndrome phenotypes.

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Title: Transduction of hematopoietic stem and progenitor cells by an MECP2 lentiviral vector improves Rett syndrome phenotypes.
Authors: Anderson JS; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States., Silverman JL; Department of Psychiatry and Behavioral Sciences, University of California Davis Medical Center, Sacramento, CA, United States., Lodigiani AL; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States., Barbaduomo CM; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States., Beegle JR; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States.
Source: Frontiers in drug discovery [Front Drug Discov (Lausanne)] 2025; Vol. 5. Date of Electronic Publication: 2025 Feb 20.
Publication Type: Journal Article
Journal Info: Publisher: Frontiers Media S.A Country of Publication: Switzerland NLM ID: 9918350785506676 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2674-0338 (Electronic) Linking ISSN: 26740338 NLM ISO Abbreviation: Front Drug Discov (Lausanne) Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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  Data: Transduction of hematopoietic stem and progenitor cells by an MECP2 lentiviral vector improves Rett syndrome phenotypes.
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  Data: <searchLink fieldCode="AU" term="%22Anderson+JS%22">Anderson JS</searchLink>; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States.<br /><searchLink fieldCode="AU" term="%22Silverman+JL%22">Silverman JL</searchLink>; Department of Psychiatry and Behavioral Sciences, University of California Davis Medical Center, Sacramento, CA, United States.<br /><searchLink fieldCode="AU" term="%22Lodigiani+AL%22">Lodigiani AL</searchLink>; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States.<br /><searchLink fieldCode="AU" term="%22Barbaduomo+CM%22">Barbaduomo CM</searchLink>; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States.<br /><searchLink fieldCode="AU" term="%22Beegle+JR%22">Beegle JR</searchLink>; Department of Internal Medicine, University of California Davis Medical Center, Sacramento, CA, United States.
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  Data: <searchLink fieldCode="JN" term="%229918350785506676%22">Frontiers in drug discovery</searchLink> [Front Drug Discov (Lausanne)] 2025; Vol. 5. <i>Date of Electronic Publication: </i>2025 Feb 20.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Frontiers+Media+S%2EA%22">Frontiers Media S.A </searchLink><i>Country of Publication: </i>Switzerland <i>NLM ID: </i>9918350785506676 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2674-0338 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2226740338%22">26740338 </searchLink><i>NLM ISO Abbreviation: </i>Front Drug Discov (Lausanne) <i>Subsets: </i>PubMed not MEDLINE
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        Value: 10.3389/fddsv.2025.1545391
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      – Code: eng
        Text: English
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      – TitleFull: Transduction of hematopoietic stem and progenitor cells by an MECP2 lentiviral vector improves Rett syndrome phenotypes.
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              Text: 2025
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