DWORF Gene Therapy Improves Cardiac Calcium Handling and Mitochondrial Function.

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Title: DWORF Gene Therapy Improves Cardiac Calcium Handling and Mitochondrial Function.
Authors: Brito-Estrada O; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Molecular and Developmental Biology Graduate Program (O.B.-E., K.R.H.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH., Kuwabara Y; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH., Gibson AM; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH., Hassel KR; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Molecular and Developmental Biology Graduate Program (O.B.-E., K.R.H.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH., Kamradt ML; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH., Verry JP; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH., Blair NS; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH., Bround MJ; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH., Huo J; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH., Molkentin JD; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH., Makarewich CA; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH.
Source: Circulation research [Circ Res] 2025 Sep 26; Vol. 137 (8), pp. 1072-1088. Date of Electronic Publication: 2025 Sep 05.
Publication Type: Journal Article
Journal Info: Publisher: Lippincott Williams & Wilkins Country of Publication: United States NLM ID: 0047103 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1524-4571 (Electronic) Linking ISSN: 00097330 NLM ISO Abbreviation: Circ Res Subsets: MEDLINE
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  Data: DWORF Gene Therapy Improves Cardiac Calcium Handling and Mitochondrial Function.
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  Data: <searchLink fieldCode="AU" term="%22Brito-Estrada+O%22">Brito-Estrada O</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Molecular and Developmental Biology Graduate Program (O.B.-E., K.R.H.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Kuwabara+Y%22">Kuwabara Y</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Gibson+AM%22">Gibson AM</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Hassel+KR%22">Hassel KR</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Molecular and Developmental Biology Graduate Program (O.B.-E., K.R.H.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Kamradt+ML%22">Kamradt ML</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Verry+JP%22">Verry JP</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Blair+NS%22">Blair NS</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Bround+MJ%22">Bround MJ</searchLink>; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Huo+J%22">Huo J</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Molkentin+JD%22">Molkentin JD</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Makarewich+CA%22">Makarewich CA</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH.
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        Value: 10.1161/CIRCRESAHA.125.326550
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              Text: 2025 Sep 26
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