DWORF Gene Therapy Improves Cardiac Calcium Handling and Mitochondrial Function.
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| Title: | DWORF Gene Therapy Improves Cardiac Calcium Handling and Mitochondrial Function. |
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| Authors: | Brito-Estrada O; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Molecular and Developmental Biology Graduate Program (O.B.-E., K.R.H.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH., Kuwabara Y; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH., Gibson AM; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH., Hassel KR; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Molecular and Developmental Biology Graduate Program (O.B.-E., K.R.H.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH., Kamradt ML; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH., Verry JP; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH., Blair NS; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH., Bround MJ; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH., Huo J; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH., Molkentin JD; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH., Makarewich CA; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH. |
| Source: | Circulation research [Circ Res] 2025 Sep 26; Vol. 137 (8), pp. 1072-1088. Date of Electronic Publication: 2025 Sep 05. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Lippincott Williams & Wilkins Country of Publication: United States NLM ID: 0047103 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1524-4571 (Electronic) Linking ISSN: 00097330 NLM ISO Abbreviation: Circ Res Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 40910184 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: DWORF Gene Therapy Improves Cardiac Calcium Handling and Mitochondrial Function. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Brito-Estrada+O%22">Brito-Estrada O</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Molecular and Developmental Biology Graduate Program (O.B.-E., K.R.H.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Kuwabara+Y%22">Kuwabara Y</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Gibson+AM%22">Gibson AM</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Hassel+KR%22">Hassel KR</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Molecular and Developmental Biology Graduate Program (O.B.-E., K.R.H.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Kamradt+ML%22">Kamradt ML</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Verry+JP%22">Verry JP</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; College of Medicine (O.B.-E., K.R.H., J.P.V.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Blair+NS%22">Blair NS</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Bround+MJ%22">Bround MJ</searchLink>; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Huo+J%22">Huo J</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Molkentin+JD%22">Molkentin JD</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH.<br /><searchLink fieldCode="AU" term="%22Makarewich+CA%22">Makarewich CA</searchLink>; Division of Molecular Cardiovascular Biology, The Heart Institute (O.B.-E., Y.K., A.M.G., K.R.H., M.L.K., J.P.V., N.S.B., J.H., J.D.M., C.A.M.), Cincinnati Children's Hospital Medical Center, Cincinnati, OH.; Department of Pediatrics (Y.K., J.D.M., C.A.M.), University of Cincinnati College of Medicine, Cincinnati, OH. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%220047103%22">Circulation research</searchLink> [Circ Res] 2025 Sep 26; Vol. 137 (8), pp. 1072-1088. <i>Date of Electronic Publication: </i>2025 Sep 05. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Lippincott+Williams+%26+Wilkins%22">Lippincott Williams & Wilkins </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>0047103 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1524-4571 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2200097330%22">00097330 </searchLink><i>NLM ISO Abbreviation: </i>Circ Res <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=40910184 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1161/CIRCRESAHA.125.326550 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 1072 Titles: – TitleFull: DWORF Gene Therapy Improves Cardiac Calcium Handling and Mitochondrial Function. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Brito-Estrada O – PersonEntity: Name: NameFull: Kuwabara Y – PersonEntity: Name: NameFull: Gibson AM – PersonEntity: Name: NameFull: Hassel KR – PersonEntity: Name: NameFull: Kamradt ML – PersonEntity: Name: NameFull: Verry JP – PersonEntity: Name: NameFull: Blair NS – PersonEntity: Name: NameFull: Bround MJ – PersonEntity: Name: NameFull: Huo J – PersonEntity: Name: NameFull: Molkentin JD – PersonEntity: Name: NameFull: Makarewich CA IsPartOfRelationships: – BibEntity: Dates: – D: 26 M: 09 Text: 2025 Sep 26 Type: published Y: 2025 Identifiers: – Type: issn-electronic Value: 1524-4571 Numbering: – Type: volume Value: 137 – Type: issue Value: 8 Titles: – TitleFull: Circulation research Type: main |
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