Efficient Installation of Heterozygous Mutations in Human Pluripotent Stem Cells Using Prime Editing.

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Title: Efficient Installation of Heterozygous Mutations in Human Pluripotent Stem Cells Using Prime Editing.
Authors: Suter A; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Graham A; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Kuah JY; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Crisologo J; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Gunatilake C; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Sourris K; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., See M; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Rossello FJ; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.; Department of Clinical Pathology, University of Melbourne, Melbourne, Australia.; Australian Regenerative Medicine Institute, Monash University, Victoria, Australia., Ramialison M; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.; Australian Regenerative Medicine Institute, Monash University, Victoria, Australia.; Department of Paediatrics, University of Melbourne, Melbourne, Australia., Vlahos K; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia., Howden SE; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.; Department of Paediatrics, University of Melbourne, Melbourne, Australia.; Lead contact.
Source: The CRISPR journal [CRISPR J] 2025 Dec; Vol. 8 (6), pp. 401-411. Date of Electronic Publication: 2025 Sep 24.
Publication Type: Journal Article
Journal Info: Publisher: Mary Ann Liebert, Inc Country of Publication: United States NLM ID: 101738191 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2573-1602 (Electronic) Linking ISSN: 25731599 NLM ISO Abbreviation: CRISPR J Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Efficient Installation of Heterozygous Mutations in Human Pluripotent Stem Cells Using Prime Editing.
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  Data: <searchLink fieldCode="AU" term="%22Suter+A%22">Suter A</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.<br /><searchLink fieldCode="AU" term="%22Graham+A%22">Graham A</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.<br /><searchLink fieldCode="AU" term="%22Kuah+JY%22">Kuah JY</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.<br /><searchLink fieldCode="AU" term="%22Crisologo+J%22">Crisologo J</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.<br /><searchLink fieldCode="AU" term="%22Gunatilake+C%22">Gunatilake C</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.<br /><searchLink fieldCode="AU" term="%22Sourris+K%22">Sourris K</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.<br /><searchLink fieldCode="AU" term="%22See+M%22">See M</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.<br /><searchLink fieldCode="AU" term="%22Rossello+FJ%22">Rossello FJ</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.; Department of Clinical Pathology, University of Melbourne, Melbourne, Australia.; Australian Regenerative Medicine Institute, Monash University, Victoria, Australia.<br /><searchLink fieldCode="AU" term="%22Ramialison+M%22">Ramialison M</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.; Australian Regenerative Medicine Institute, Monash University, Victoria, Australia.; Department of Paediatrics, University of Melbourne, Melbourne, Australia.<br /><searchLink fieldCode="AU" term="%22Vlahos+K%22">Vlahos K</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.<br /><searchLink fieldCode="AU" term="%22Howden+SE%22">Howden SE</searchLink>; Murdoch Children's Research Institute, The Royal Children's Hospital, Melbourne, Australia.; Novo Nordisk Foundation Center for Stem Cell Medicine, Murdoch Children's Research Institute, Melbourne, Australia.; Department of Paediatrics, University of Melbourne, Melbourne, Australia.; Lead contact.
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  Data: <searchLink fieldCode="JN" term="%22101738191%22">The CRISPR journal</searchLink> [CRISPR J] 2025 Dec; Vol. 8 (6), pp. 401-411. <i>Date of Electronic Publication: </i>2025 Sep 24.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Mary+Ann+Liebert%2C+Inc%22">Mary Ann Liebert, Inc </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101738191 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2573-1602 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2225731599%22">25731599 </searchLink><i>NLM ISO Abbreviation: </i>CRISPR J <i>Subsets: </i>MEDLINE
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              Text: 2025 Dec
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