Nexiguran Ziclumeran Gene Editing in Hereditary ATTR with Polyneuropathy.

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Bibliographic Details
Title: Nexiguran Ziclumeran Gene Editing in Hereditary ATTR with Polyneuropathy.
Authors: Gillmore JD; University College London, National Amyloidosis Centre, Royal Free Hospital, London., Gane E; University of Auckland, Auckland, New Zealand., Täubel J; Richmond Pharmacology, London., Pilebro B; Umeå University, Umeå, Sweden., Echaniz-Laguna A; Bicêtre University Hospital, Assistance Publique-Hôpitaux de Paris, Université Paris-Saclay, Le Kremlin-Bicêtre, France., Kao J; Auckland City Hospital, Auckland, New Zealand., Litchy W; Mayo Clinic, Rochester, MN., Shahda S; Intellia Therapeutics, Cambridge, MA., Haagensen A; Intellia Therapeutics, Cambridge, MA., Walsh L; Intellia Therapeutics, Cambridge, MA., Smith D; Intellia Therapeutics, Cambridge, MA., Kachadourian J; Intellia Therapeutics, Cambridge, MA., Ward JH; Intellia Therapeutics, Cambridge, MA., Lebwohl D; Intellia Therapeutics, Cambridge, MA., Zhu P; Intellia Therapeutics, Cambridge, MA., Xu Y; Intellia Therapeutics, Cambridge, MA., Leung A; Intellia Therapeutics, Cambridge, MA., Sonderfan A; Intellia Therapeutics, Cambridge, MA., Gutstein DE; Regeneron Pharmaceuticals, Tarrytown, NY., Manvelian G; Regeneron Pharmaceuticals, Tarrytown, NY., Adams D; Bicêtre University Hospital, Assistance Publique-Hôpitaux de Paris, Université Paris-Saclay, Le Kremlin-Bicêtre, France.
Source: The New England journal of medicine [N Engl J Med] 2025 Oct 09; Vol. 393 (14), pp. 1375-1386. Date of Electronic Publication: 2025 Sep 25.
Publication Type: Journal Article; Clinical Trial, Phase I; Multicenter Study
Journal Info: Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1533-4406
DOI:10.1056/NEJMoa2510209