Novel single-domain antibodies targeting a unique transferrin receptor 1 epitope for cross-species delivery of drugs in the central nervous system.

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Title: Novel single-domain antibodies targeting a unique transferrin receptor 1 epitope for cross-species delivery of drugs in the central nervous system.
Authors: David M; Aix Marseille Univ, CNRS, INP, Inst Neurophysiopathol, Marseille, France; VECT-HORUS SAS, Marseille, France. Electronic address: marion.david@vect-horus.com., Cohen R; VECT-HORUS SAS, Marseille, France., Beuzelin D; VECT-HORUS SAS, Marseille, France., Ferracci G; Aix Marseille Univ, CNRS, INP, Inst Neurophysiopathol, Marseille, France; Aix Marseille Univ, PINT, Plateforme Interactions moléculaires Timone, Faculté des Sciences Médicales et Paramédicales, Marseille, France., Cresci M; Aix Marseille Univ, CNRS, INSERM, Institut Paoli-Calmettes, CRCM, Marseille, France., Faucon A; VECT-HORUS SAS, Marseille, France., Abouzid K; VECT-HORUS SAS, Marseille, France., Godefroy G; VECT-HORUS SAS, Marseille, France., Masse M; VECT-HORUS SAS, Marseille, France., Mechioukhi Y; VECT-HORUS SAS, Marseille, France., Girard SD; Aix Marseille Univ, CNRS, INP, Inst Neurophysiopathol, Marseille, France; VECT-HORUS SAS, Marseille, France., Julien-Gau I; VECT-HORUS SAS, Marseille, France., Boursery C; VECT-HORUS SAS, Marseille, France., Fraisier C; VECT-HORUS SAS, Marseille, France., Varini K; VECT-HORUS SAS, Marseille, France., Thomas M; VECT-HORUS SAS, Marseille, France., Jacquot G; VECT-HORUS SAS, Marseille, France., Lécorché P; VECT-HORUS SAS, Marseille, France., Serrano B; VECT-HORUS SAS, Marseille, France., Romette A; VECT-HORUS SAS, Marseille, France., Pélissier GD; VECT-HORUS SAS, Marseille, France., Godard M; VECT-HORUS SAS, Marseille, France., Saillant V; Deeptope, Orsay, France., Pruvost T; Deeptope, Orsay, France., Sierocki R; Deeptope, Orsay, France., Chames P; Aix Marseille Univ, CNRS, INSERM, Institut Paoli-Calmettes, CRCM, Marseille, France., Kerfelec B; Aix Marseille Univ, CNRS, INSERM, Institut Paoli-Calmettes, CRCM, Marseille, France., Temsamani J; VECT-HORUS SAS, Marseille, France., Khrestchatisky M; Aix Marseille Univ, CNRS, INP, Inst Neurophysiopathol, Marseille, France. Electronic address: michel.khrestchatisky@univ-amu.fr.
Source: Journal of controlled release : official journal of the Controlled Release Society [J Control Release] 2025 Dec 10; Vol. 388 (Pt 2), pp. 114344. Date of Electronic Publication: 2025 Oct 17.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Elsevier Science Publishers Country of Publication: Netherlands NLM ID: 8607908 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1873-4995 (Electronic) Linking ISSN: 01683659 NLM ISO Abbreviation: J Control Release Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1873-4995
DOI:10.1016/j.jconrel.2025.114344