G2B: an optimized lentiviral vector with enhanced titer and β-globin expression for improved β-thalassemia gene therapy.

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Title: G2B: an optimized lentiviral vector with enhanced titer and β-globin expression for improved β-thalassemia gene therapy.
Authors: Gao ZY; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China., Yang ZX; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China., Deng DH; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China., Zhang F; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China., Yu B; College of Computer Science and Technology, China University of Petroleum (East China), Qingdao 266000, China., Zhang YY; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China., Lv X; State Key Laboratory of Medical Molecular Biology, Institute of Basic Medical Sciences, Chinese Academy of Medical Sciences & Peking Union Medical College, Beijing, 100005, P.R. China., Nakamura Y; Cell Engineering Division, RIKEN BioResource Center, Tsukuba, Ibaraki, Japan., Gong A; College of Computer Science and Technology, China University of Petroleum (East China), Qingdao 266000, China., Cheng T; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China., Zhang JP; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China., Zhang XB; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China.
Source: Blood science (Baltimore, Md.) [Blood Sci] 2025 Oct 15; Vol. 7 (4), pp. e00253. Date of Electronic Publication: 2025 Oct 15 (Print Publication: 2025).
Publication Type: Journal Article
Journal Info: Publisher: Wolters Kluwer Health, Inc Country of Publication: United States NLM ID: 9918248414306676 Publication Model: eCollection Cited Medium: Internet ISSN: 2543-6368 (Electronic) Linking ISSN: 25436368 NLM ISO Abbreviation: Blood Sci Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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  Data: G2B: an optimized lentiviral vector with enhanced titer and β-globin expression for improved β-thalassemia gene therapy.
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  Data: <searchLink fieldCode="AU" term="%22Gao+ZY%22">Gao ZY</searchLink>; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China.<br /><searchLink fieldCode="AU" term="%22Yang+ZX%22">Yang ZX</searchLink>; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China.<br /><searchLink fieldCode="AU" term="%22Deng+DH%22">Deng DH</searchLink>; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China.<br /><searchLink fieldCode="AU" term="%22Zhang+F%22">Zhang F</searchLink>; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China.<br /><searchLink fieldCode="AU" term="%22Yu+B%22">Yu B</searchLink>; College of Computer Science and Technology, China University of Petroleum (East China), Qingdao 266000, China.<br /><searchLink fieldCode="AU" term="%22Zhang+YY%22">Zhang YY</searchLink>; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China.<br /><searchLink fieldCode="AU" term="%22Lv+X%22">Lv X</searchLink>; State Key Laboratory of Medical Molecular Biology, Institute of Basic Medical Sciences, Chinese Academy of Medical Sciences & Peking Union Medical College, Beijing, 100005, P.R. China.<br /><searchLink fieldCode="AU" term="%22Nakamura+Y%22">Nakamura Y</searchLink>; Cell Engineering Division, RIKEN BioResource Center, Tsukuba, Ibaraki, Japan.<br /><searchLink fieldCode="AU" term="%22Gong+A%22">Gong A</searchLink>; College of Computer Science and Technology, China University of Petroleum (East China), Qingdao 266000, China.<br /><searchLink fieldCode="AU" term="%22Cheng+T%22">Cheng T</searchLink>; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China.<br /><searchLink fieldCode="AU" term="%22Zhang+JP%22">Zhang JP</searchLink>; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China.<br /><searchLink fieldCode="AU" term="%22Zhang+XB%22">Zhang XB</searchLink>; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Tianjin Institutes of Health Science, Tianjin 301600, China.
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  Data: <searchLink fieldCode="JN" term="%229918248414306676%22">Blood science (Baltimore, Md.)</searchLink> [Blood Sci] 2025 Oct 15; Vol. 7 (4), pp. e00253. <i>Date of Electronic Publication: </i>2025 Oct 15 (<i>Print Publication: </i>2025).
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Wolters+Kluwer+Health%2C+Inc%22">Wolters Kluwer Health, Inc </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>9918248414306676 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Internet <i>ISSN: </i>2543-6368 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2225436368%22">25436368 </searchLink><i>NLM ISO Abbreviation: </i>Blood Sci <i>Subsets: </i>PubMed not MEDLINE
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        Value: 10.1097/BS9.0000000000000253
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        Text: English
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      – TitleFull: G2B: an optimized lentiviral vector with enhanced titer and β-globin expression for improved β-thalassemia gene therapy.
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              Text: 2025 Oct 15
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