Real-Life Efficacy and Safety of BRAF Inhibitors in Erdheim-Chester Disease.

Saved in:
Bibliographic Details
Title: Real-Life Efficacy and Safety of BRAF Inhibitors in Erdheim-Chester Disease.
Authors: Pegoraro F; Department of Experimental and Clinical Medicine, University of Florence, Florence, Italy.; Department of Hematology and Oncology, Meyer Children's Hospital IRCCS, Florence, Italy., Peyronel F; Department of Experimental and Clinical Medicine, University of Florence, Florence, Italy.; Nephrology and Dialysis Unit, Careggi University Hospital, Florence, Italy., Papo M; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France., Sutera R; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.; School of Medicine, University of Florence, Florence, Italy., Catamerò F; Department of Health Sciences, University of Florence, Florence, Italy., Poeta F; Department of Health Sciences, University of Florence, Florence, Italy., Razanamahery J; Department of Internal Medicine and Clinical Immunology, Dijon University Hospital, Dijon, France., Ledoult E; Department of Internal Medicine, Lille University Hospital, Lille, France., Le Scornet T; Department of Internal Medicine, Nantes University Hospital, Nantes, France., de Menthon M; Department of Internal Medicine and Clinical Immunology, Bicetre Hospital, Assistance Publique - Hôpitaux de Paris, Le Kremlin Bicêtre, France., Riviere E; Department of Internal Medicine, Haut-Lévèque University Hospital, Bordeaux, France., Sieni E; Department of Hematology and Oncology, Meyer Children's Hospital IRCCS, Florence, Italy., Barete S; Department of Dermatology, CEREMAST, Pitié-Salpȇtrière Hospital, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France., Idbaih A; Sorbonne Université, AP-HP, Institut du Cerveau - Paris Brain Institute - ICM, Inserm, CNRS, Hôpitaux Universitaires La Pitié Salpêtrière - Charles Foix, DMU Neurosciences, Service de Neuro-Oncologie-Institut de Neurologie, Paris, France., Cohen-Aubart F; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France., Amoura Z; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France., Emile JF; Department of Pathology, Ambroise Paré Hospital, EA4340 BECCOH, Versailles SQY University, Boulogne, France., Vaglio A; Department of Biomedical, Experimental and Clinical Sciences 'Mario Serio', University of Florence, Florence, Italy.; Nephrology and Dialysis Unit, Meyer Children's Hospital IRCCS, Florence, Italy., Haroche J; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.
Source: American journal of hematology [Am J Hematol] 2026 Jan; Vol. 101 (1), pp. 182-186. Date of Electronic Publication: 2025 Nov 08.
Publication Type: Letter
Journal Info: Publisher: Wiley-Blackwell Country of Publication: United States NLM ID: 7610369 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1096-8652 (Electronic) Linking ISSN: 03618609 NLM ISO Abbreviation: Am J Hematol Subsets: MEDLINE; In Process
Database: MEDLINE Ultimate
FullText Text:
  Availability: 0
Header DbId: mdl
DbLabel: MEDLINE Ultimate
An: 41204885
AccessLevel: 2
PubType: Editorial & Opinion
PubTypeId: editorialOpinion
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: Real-Life Efficacy and Safety of BRAF Inhibitors in Erdheim-Chester Disease.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AU" term="%22Pegoraro+F%22">Pegoraro F</searchLink>; Department of Experimental and Clinical Medicine, University of Florence, Florence, Italy.; Department of Hematology and Oncology, Meyer Children's Hospital IRCCS, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Peyronel+F%22">Peyronel F</searchLink>; Department of Experimental and Clinical Medicine, University of Florence, Florence, Italy.; Nephrology and Dialysis Unit, Careggi University Hospital, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Papo+M%22">Papo M</searchLink>; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.<br /><searchLink fieldCode="AU" term="%22Sutera+R%22">Sutera R</searchLink>; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.; School of Medicine, University of Florence, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Catamerò+F%22">Catamerò F</searchLink>; Department of Health Sciences, University of Florence, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Poeta+F%22">Poeta F</searchLink>; Department of Health Sciences, University of Florence, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Razanamahery+J%22">Razanamahery J</searchLink>; Department of Internal Medicine and Clinical Immunology, Dijon University Hospital, Dijon, France.<br /><searchLink fieldCode="AU" term="%22Ledoult+E%22">Ledoult E</searchLink>; Department of Internal Medicine, Lille University Hospital, Lille, France.<br /><searchLink fieldCode="AU" term="%22Le+Scornet+T%22">Le Scornet T</searchLink>; Department of Internal Medicine, Nantes University Hospital, Nantes, France.<br /><searchLink fieldCode="AU" term="%22de+Menthon+M%22">de Menthon M</searchLink>; Department of Internal Medicine and Clinical Immunology, Bicetre Hospital, Assistance Publique - Hôpitaux de Paris, Le Kremlin Bicêtre, France.<br /><searchLink fieldCode="AU" term="%22Riviere+E%22">Riviere E</searchLink>; Department of Internal Medicine, Haut-Lévèque University Hospital, Bordeaux, France.<br /><searchLink fieldCode="AU" term="%22Sieni+E%22">Sieni E</searchLink>; Department of Hematology and Oncology, Meyer Children's Hospital IRCCS, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Barete+S%22">Barete S</searchLink>; Department of Dermatology, CEREMAST, Pitié-Salpȇtrière Hospital, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.<br /><searchLink fieldCode="AU" term="%22Idbaih+A%22">Idbaih A</searchLink>; Sorbonne Université, AP-HP, Institut du Cerveau - Paris Brain Institute - ICM, Inserm, CNRS, Hôpitaux Universitaires La Pitié Salpêtrière - Charles Foix, DMU Neurosciences, Service de Neuro-Oncologie-Institut de Neurologie, Paris, France.<br /><searchLink fieldCode="AU" term="%22Cohen-Aubart+F%22">Cohen-Aubart F</searchLink>; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.<br /><searchLink fieldCode="AU" term="%22Amoura+Z%22">Amoura Z</searchLink>; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.<br /><searchLink fieldCode="AU" term="%22Emile+JF%22">Emile JF</searchLink>; Department of Pathology, Ambroise Paré Hospital, EA4340 BECCOH, Versailles SQY University, Boulogne, France.<br /><searchLink fieldCode="AU" term="%22Vaglio+A%22">Vaglio A</searchLink>; Department of Biomedical, Experimental and Clinical Sciences 'Mario Serio', University of Florence, Florence, Italy.; Nephrology and Dialysis Unit, Meyer Children's Hospital IRCCS, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Haroche+J%22">Haroche J</searchLink>; Departement of Internal Medicine 2, Center of reference of Histiocytosis, Hôpital Pitié-Salpêtrière, Sorbonne University, Assistance Publique-Hôpitaux de Paris, Paris, France.
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%227610369%22">American journal of hematology</searchLink> [Am J Hematol] 2026 Jan; Vol. 101 (1), pp. 182-186. <i>Date of Electronic Publication: </i>2025 Nov 08.
– Name: TypePub
  Label: Publication Type
  Group: TypPub
  Data: Letter
– Name: TitleSource
  Label: Journal Info
  Group: Src
  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Wiley-Blackwell%22">Wiley-Blackwell </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>7610369 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1096-8652 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2203618609%22">03618609 </searchLink><i>NLM ISO Abbreviation: </i>Am J Hematol <i>Subsets: </i>MEDLINE; In Process
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41204885
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1002/ajh.70137
    Languages:
      – Code: eng
        Text: English
    PhysicalDescription:
      Pagination:
        StartPage: 182
    Titles:
      – TitleFull: Real-Life Efficacy and Safety of BRAF Inhibitors in Erdheim-Chester Disease.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Pegoraro F
      – PersonEntity:
          Name:
            NameFull: Peyronel F
      – PersonEntity:
          Name:
            NameFull: Papo M
      – PersonEntity:
          Name:
            NameFull: Sutera R
      – PersonEntity:
          Name:
            NameFull: Catamerò F
      – PersonEntity:
          Name:
            NameFull: Poeta F
      – PersonEntity:
          Name:
            NameFull: Razanamahery J
      – PersonEntity:
          Name:
            NameFull: Ledoult E
      – PersonEntity:
          Name:
            NameFull: Le Scornet T
      – PersonEntity:
          Name:
            NameFull: de Menthon M
      – PersonEntity:
          Name:
            NameFull: Riviere E
      – PersonEntity:
          Name:
            NameFull: Sieni E
      – PersonEntity:
          Name:
            NameFull: Barete S
      – PersonEntity:
          Name:
            NameFull: Idbaih A
      – PersonEntity:
          Name:
            NameFull: Cohen-Aubart F
      – PersonEntity:
          Name:
            NameFull: Amoura Z
      – PersonEntity:
          Name:
            NameFull: Emile JF
      – PersonEntity:
          Name:
            NameFull: Vaglio A
      – PersonEntity:
          Name:
            NameFull: Haroche J
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 01
              M: 01
              Text: 2026 Jan
              Type: published
              Y: 2026
          Identifiers:
            – Type: issn-electronic
              Value: 1096-8652
          Numbering:
            – Type: volume
              Value: 101
            – Type: issue
              Value: 1
          Titles:
            – TitleFull: American journal of hematology
              Type: main
ResultId 1