Efficacy of Acoramidis in Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy: Results From ATTRibute-CM and Its Open-Label Extension.
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| Title: | Efficacy of Acoramidis in Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy: Results From ATTRibute-CM and Its Open-Label Extension. |
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| Authors: | Alexander KM; Stanford Amyloid Center, Division of Cardiovascular Medicine, Stanford University School of Medicine, Palo Alto, California., Davis MK; Division of Cardiology, University of British Columbia, Vancouver, British Columbia, Canada., Akinboboye O; Laurelton Heart Specialists, Queens Heart Institute, Rosedale, New York, New York., Berk J; Boston Medical Center, Boston University, Boston, Massachusetts., Bhatt K; Division of Cardiology of the Department of Medicine at Emory University, Emory Healthcare, Atlanta, Georgia., Cappelli F; Tuscan Regional Amyloidosis Centre, Careggi University Hospital, Florence, Italy., Cuddy SAM; Heart and Vascular Center, Brigham and Women's Hospital, Boston, Massachusetts., Fontana M; National Amyloidosis Centre, Division of Medicine, University College London, London, United Kingdom., Garcia-Pavia P; Hospital Universitario Puerta de Hierro Majadahonda, IDIPHISA, CIBERCV, and Centro Nacional de Investigaciones Cardiovasculares (CNIC), Madrid, Spain., Gillmore JD; Centre for Amyloidosis and Acute Phase Proteins, Division of Medicine, University College London, London, United Kingdom., Griffin JM; Division of Cardiology, Department of Medicine, Medical University of South Carolina, Charleston., Grodin JL; Department of Internal Medicine, University of Texas Southwestern Medical Center, Dallas., Judge DP; Division of Cardiology, Department of Medicine, Medical University of South Carolina, Charleston., Khouri MG; Division of Cardiology, Department of Medicine, Duke University Health System, Durham, North Carolina., Lam K; Western Australia Advanced Heart Failure and Cardiac Transplant Service, Fiona Stanley Hospital, Western Australia, Australia., Masri A; Division of Cardiology, Oregon Health & Science University, Portland., Maurer MS; Department of Medicine, Columbia University Irving Medical Center, New York, New York., Obici L; Fondazione IRCCS Policlinico San Matteo, Pavia, Italy., Ruberg FL; Boston University Chobanian & Avedisian School of Medicine, Boston Medical Center, Boston, Massachusetts., Sarswat N; Division of Cardiovascular Medicine, University of Chicago Medicine, Chicago, Illinois., Shah K; Pauley Heart Center, Virginia Commonwealth University, Richmond., Soman P; Division of Cardiology, University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania., Stern L; Department of Cardiology, Smidt Heart Institute, Cedars Sinai, Los Angeles, California., Wright R; Pacific Heart Institute and Providence, St. John's Health Center, Santa Monica, California., Xiong K; BridgeBio, San Francisco, California., Cao X; BridgeBio, San Francisco, California., Lystig T; BridgeBio, San Francisco, California., Tamby JF; BridgeBio, San Francisco, California., Castaño A; BridgeBio, San Francisco, California., Katz L; BridgeBio, San Francisco, California., Sinha U; BridgeBio, San Francisco, California., Fox JC; BridgeBio, San Francisco, California., Solomon SD; Heart and Vascular Center, Brigham and Women's Hospital, Boston, Massachusetts., Grogan M; Cardiovascular Medicine, Mayo Clinic Rochester, Minnesota. |
| Source: | JAMA cardiology [JAMA Cardiol] 2026 Jan 01; Vol. 11 (1), pp. 57-67. |
| Publication Type: | Journal Article; Multicenter Study; Randomized Controlled Trial; Clinical Trial, Phase III |
| Journal Info: | Publisher: American Medical Association Country of Publication: United States NLM ID: 101676033 Publication Model: Print Cited Medium: Internet ISSN: 2380-6591 (Electronic) NLM ISO Abbreviation: JAMA Cardiol Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 41205147 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Efficacy of Acoramidis in Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy: Results From ATTRibute-CM and Its Open-Label Extension. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Alexander+KM%22">Alexander KM</searchLink>; Stanford Amyloid Center, Division of Cardiovascular Medicine, Stanford University School of Medicine, Palo Alto, California.<br /><searchLink fieldCode="AU" term="%22Davis+MK%22">Davis MK</searchLink>; Division of Cardiology, University of British Columbia, Vancouver, British Columbia, Canada.<br /><searchLink fieldCode="AU" term="%22Akinboboye+O%22">Akinboboye O</searchLink>; Laurelton Heart Specialists, Queens Heart Institute, Rosedale, New York, New York.<br /><searchLink fieldCode="AU" term="%22Berk+J%22">Berk J</searchLink>; Boston Medical Center, Boston University, Boston, Massachusetts.<br /><searchLink fieldCode="AU" term="%22Bhatt+K%22">Bhatt K</searchLink>; Division of Cardiology of the Department of Medicine at Emory University, Emory Healthcare, Atlanta, Georgia.<br /><searchLink fieldCode="AU" term="%22Cappelli+F%22">Cappelli F</searchLink>; Tuscan Regional Amyloidosis Centre, Careggi University Hospital, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Cuddy+SAM%22">Cuddy SAM</searchLink>; Heart and Vascular Center, Brigham and Women's Hospital, Boston, Massachusetts.<br /><searchLink fieldCode="AU" term="%22Fontana+M%22">Fontana M</searchLink>; National Amyloidosis Centre, Division of Medicine, University College London, London, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Garcia-Pavia+P%22">Garcia-Pavia P</searchLink>; Hospital Universitario Puerta de Hierro Majadahonda, IDIPHISA, CIBERCV, and Centro Nacional de Investigaciones Cardiovasculares (CNIC), Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Gillmore+JD%22">Gillmore JD</searchLink>; Centre for Amyloidosis and Acute Phase Proteins, Division of Medicine, University College London, London, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Griffin+JM%22">Griffin JM</searchLink>; Division of Cardiology, Department of Medicine, Medical University of South Carolina, Charleston.<br /><searchLink fieldCode="AU" term="%22Grodin+JL%22">Grodin JL</searchLink>; Department of Internal Medicine, University of Texas Southwestern Medical Center, Dallas.<br /><searchLink fieldCode="AU" term="%22Judge+DP%22">Judge DP</searchLink>; Division of Cardiology, Department of Medicine, Medical University of South Carolina, Charleston.<br /><searchLink fieldCode="AU" term="%22Khouri+MG%22">Khouri MG</searchLink>; Division of Cardiology, Department of Medicine, Duke University Health System, Durham, North Carolina.<br /><searchLink fieldCode="AU" term="%22Lam+K%22">Lam K</searchLink>; Western Australia Advanced Heart Failure and Cardiac Transplant Service, Fiona Stanley Hospital, Western Australia, Australia.<br /><searchLink fieldCode="AU" term="%22Masri+A%22">Masri A</searchLink>; Division of Cardiology, Oregon Health & Science University, Portland.<br /><searchLink fieldCode="AU" term="%22Maurer+MS%22">Maurer MS</searchLink>; Department of Medicine, Columbia University Irving Medical Center, New York, New York.<br /><searchLink fieldCode="AU" term="%22Obici+L%22">Obici L</searchLink>; Fondazione IRCCS Policlinico San Matteo, Pavia, Italy.<br /><searchLink fieldCode="AU" term="%22Ruberg+FL%22">Ruberg FL</searchLink>; Boston University Chobanian & Avedisian School of Medicine, Boston Medical Center, Boston, Massachusetts.<br /><searchLink fieldCode="AU" term="%22Sarswat+N%22">Sarswat N</searchLink>; Division of Cardiovascular Medicine, University of Chicago Medicine, Chicago, Illinois.<br /><searchLink fieldCode="AU" term="%22Shah+K%22">Shah K</searchLink>; Pauley Heart Center, Virginia Commonwealth University, Richmond.<br /><searchLink fieldCode="AU" term="%22Soman+P%22">Soman P</searchLink>; Division of Cardiology, University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania.<br /><searchLink fieldCode="AU" term="%22Stern+L%22">Stern L</searchLink>; Department of Cardiology, Smidt Heart Institute, Cedars Sinai, Los Angeles, California.<br /><searchLink fieldCode="AU" term="%22Wright+R%22">Wright R</searchLink>; Pacific Heart Institute and Providence, St. John's Health Center, Santa Monica, California.<br /><searchLink fieldCode="AU" term="%22Xiong+K%22">Xiong K</searchLink>; BridgeBio, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Cao+X%22">Cao X</searchLink>; BridgeBio, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Lystig+T%22">Lystig T</searchLink>; BridgeBio, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Tamby+JF%22">Tamby JF</searchLink>; BridgeBio, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Castaño+A%22">Castaño A</searchLink>; BridgeBio, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Katz+L%22">Katz L</searchLink>; BridgeBio, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Sinha+U%22">Sinha U</searchLink>; BridgeBio, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Fox+JC%22">Fox JC</searchLink>; BridgeBio, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Solomon+SD%22">Solomon SD</searchLink>; Heart and Vascular Center, Brigham and Women's Hospital, Boston, Massachusetts.<br /><searchLink fieldCode="AU" term="%22Grogan+M%22">Grogan M</searchLink>; Cardiovascular Medicine, Mayo Clinic Rochester, Minnesota. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101676033%22">JAMA cardiology</searchLink> [JAMA Cardiol] 2026 Jan 01; Vol. 11 (1), pp. 57-67. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Multicenter Study; Randomized Controlled Trial; Clinical Trial, Phase III – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22American+Medical+Association%22">American Medical Association </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101676033 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>2380-6591 (Electronic) <i>NLM ISO Abbreviation: </i>JAMA Cardiol <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41205147 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1001/jamacardio.2025.4477 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 57 Titles: – TitleFull: Efficacy of Acoramidis in Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy: Results From ATTRibute-CM and Its Open-Label Extension. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Alexander KM – PersonEntity: Name: NameFull: Davis MK – PersonEntity: Name: NameFull: Akinboboye O – PersonEntity: Name: NameFull: Berk J – PersonEntity: Name: NameFull: Bhatt K – PersonEntity: Name: NameFull: Cappelli F – PersonEntity: Name: NameFull: Cuddy SAM – PersonEntity: Name: NameFull: Fontana M – PersonEntity: Name: NameFull: Garcia-Pavia P – PersonEntity: Name: NameFull: Gillmore JD – PersonEntity: Name: NameFull: Griffin JM – PersonEntity: Name: NameFull: Grodin JL – PersonEntity: Name: NameFull: Judge DP – PersonEntity: Name: NameFull: Khouri MG – PersonEntity: Name: NameFull: Lam K – PersonEntity: Name: NameFull: Masri A – PersonEntity: Name: NameFull: Maurer MS – PersonEntity: Name: NameFull: Obici L – PersonEntity: Name: NameFull: Ruberg FL – PersonEntity: Name: NameFull: Sarswat N – PersonEntity: Name: NameFull: Shah K – PersonEntity: Name: NameFull: Soman P – PersonEntity: Name: NameFull: Stern L – PersonEntity: Name: NameFull: Wright R – PersonEntity: Name: NameFull: Xiong K – PersonEntity: Name: NameFull: Cao X – PersonEntity: Name: NameFull: Lystig T – PersonEntity: Name: NameFull: Tamby JF – PersonEntity: Name: NameFull: Castaño A – PersonEntity: Name: NameFull: Katz L – PersonEntity: Name: NameFull: Sinha U – PersonEntity: Name: NameFull: Fox JC – PersonEntity: Name: NameFull: Solomon SD – PersonEntity: Name: NameFull: Grogan M IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 01 Text: 2026 Jan 01 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 2380-6591 Numbering: – Type: volume Value: 11 – Type: issue Value: 1 Titles: – TitleFull: JAMA cardiology Type: main |
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