Prime Editing for p47phox-Deficient Chronic Granulomatous Disease.
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| Title: | Prime Editing for p47phox-Deficient Chronic Granulomatous Disease. |
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| Authors: | Gori JL; Prime Medicine, Cambridge, MA., Haddad E; Department of Pediatrics, CHU Sainte-Justine Azrieli Research Center, Université de Montréal, Montreal.; Department of Microbiology, Immunology, and Infectious Diseases, CHU Sainte-Justine Azrieli Research Center, Université de Montréal, Montreal., Frangoul H; Sarah Cannon Research Institute, Children's Hospital at TriStar Centennial, Nashville., Kohn DB; Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles, Los Angeles., Morris EC; National Institute for Health and Care Research, University College London Hospitals Biomedical Research Centre, London., Martin BN; Prime Medicine, Cambridge, MA., Deary BA; Prime Medicine, Cambridge, MA., Nickerson M; Prime Medicine, Cambridge, MA., Scholz RL; Prime Medicine, Cambridge, MA., Fernandez I; Department of Pediatrics, CHU Sainte-Justine Azrieli Research Center, Université de Montréal, Montreal.; Department of Microbiology, Immunology, and Infectious Diseases, CHU Sainte-Justine Azrieli Research Center, Université de Montréal, Montreal., Leveille K; Department of Pediatrics, CHU Sainte-Justine Azrieli Research Center, Université de Montréal, Montreal.; Department of Microbiology, Immunology, and Infectious Diseases, CHU Sainte-Justine Azrieli Research Center, Université de Montréal, Montreal., De Ravin SS; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD., Kang EM; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD., Pierzynski M; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD., Estwick T; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD., Littel P; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD., Kuhns DB; Leidos Biomedical Research, Frederick National Laboratory for Cancer Research, Frederick, MD., Long Priel DA; Leidos Biomedical Research, Frederick National Laboratory for Cancer Research, Frederick, MD., Teira P; Department of Pediatrics, CHU Sainte-Justine Azrieli Research Center, Université de Montréal, Montreal., Turvey S; Department of Pediatrics, British Columbia Children's Hospital, University of British Columbia, Vancouver, Canada., Arnold J; Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles, Los Angeles., Evans MD; Sarah Cannon Research Institute, Children's Hospital at TriStar Centennial, Nashville., McManus M; Sarah Cannon Research Institute, Children's Hospital at TriStar Centennial, Nashville., Carpenter B; Department of Hematology, University College London Hospitals NHS Foundation Trust, London., Waterman DP; Prime Medicine, Cambridge, MA., Anzalone AV; Prime Medicine, Cambridge, MA., Petrusich A; Prime Medicine, Cambridge, MA., Osuna CE; Prime Medicine, Cambridge, MA., O'Malley TT; Prime Medicine, Cambridge, MA., Stewart-Ornstein J; Prime Medicine, Cambridge, MA., Heath JM; Prime Medicine, Cambridge, MA., Nehilla BJ; Prime Medicine, Cambridge, MA., Asmal M; Prime Medicine, Cambridge, MA., Malech HL; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD. |
| Source: | The New England journal of medicine [N Engl J Med] 2026 Mar 26; Vol. 394 (12), pp. 1195-1203. Date of Electronic Publication: 2025 Dec 07. |
| Publication Type: | Clinical Trial, Phase I; Clinical Trial, Phase II; Journal Article; Multicenter Study |
| Journal Info: | Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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