Gene-corrected regulatory T cell therapy for IL2RA deficiency.
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| Title: | Gene-corrected regulatory T cell therapy for IL2RA deficiency. |
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| Authors: | Ha AS; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA., Kalter N; The Institute for Advanced Materials and Nanotechnology, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat Gan 5290002, Israel., Rosenberg M; The Institute for Advanced Materials and Nanotechnology, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat Gan 5290002, Israel., Acevedo LA; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA., Liang B; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA., Liu W; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA., Paruthiyil S; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA., Sinha M; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA., Vu A; Diabetes Center, University of California, San Francisco, San Francisco, CA 94143, USA; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA., Nguyen V; Diabetes Center, University of California, San Francisco, San Francisco, CA 94143, USA., Qi Z; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA., Krishnappa N; The Innovative Genomics Institute, University of California, Berkeley, Berkeley, CA 94720, USA., Shu J; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA., Yu J; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA., Catanzaro J; Department of Immunobiology and Internal Medicine, Yale University, New Haven, CT 06520, USA., Bluestone JA; Sonoma Biotherapeutics, South San Francisco, CA 94080, USA., Tang Q; Diabetes Center, University of California, San Francisco, San Francisco, CA 94143, USA; Department of Surgery, University of California, San Francisco, San Francisco, CA 94143, USA; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA., Urnov FD; Department of Molecular and Cell Biology, University of California, Berkeley, Berkeley, CA 94720, USA; The Innovative Genomics Institute, University of California, Berkeley, Berkeley, CA 94720, USA., Marson A; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA., Hendel A; The Institute for Advanced Materials and Nanotechnology, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat Gan 5290002, Israel., Herold KC; Department of Immunobiology and Internal Medicine, Yale University, New Haven, CT 06520, USA., Shy BR; Department of Laboratory Medicine, University of California, San Francisco, San Francisco, CA 94143, USA; Gladstone-UCSF Institute of Genomic Immunology, San Francisco, CA 94158, USA. Electronic address: brian.shy@ucsf.edu., Esensten JH; Advanced Biotherapy Center, Sheba Medical Center, Ramat Gan 5266202, Israel. Electronic address: jonathan.esensten@sheba.health.gov.il. |
| Source: | Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2026 Mar 04; Vol. 34 (3), pp. 1367-1381. Date of Electronic Publication: 2025 Dec 09. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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