HLA-haploidentical hematopoietic stem cell transplantation in patients with sickle cell disease: results from the phase II DREP-HAPLO trial.

Saved in:
Bibliographic Details
Title: HLA-haploidentical hematopoietic stem cell transplantation in patients with sickle cell disease: results from the phase II DREP-HAPLO trial.
Authors: Dhedin N; Adolescent and Young Adult Hematology Unit, Saint Louis University Hospital, Assistance Publique-Hopitaux de Paris (AP-HP), Paris, France; Epidemiology and Clinical Statistics for Trials and Real-world evidence Research (ECSTRRA), Saint Louis Research Institute, UMR1342, INSERM, Universite de Paris. nathalie.dhedin@aphp.fr., Bruno B; Paediatric Hematology, F-59000 Lille., Paillard C; Department of Paediatric Haematology and Oncology, Strasbourg University Hospital, Strasbourg, France; Strasbourg University, INSERM, IRM UMR-S 1109, F-67000 Strasbourg., Gounfle E; Department of Health Research and Innovation, Intercommunal Hospital Center of Creteil, Creteil., Buchbinder N; Department of Paediatric Haematology and Oncology, Charles Nicolle University Hospital, Rouen., Chardin MO; Institute of Pediatric Oncology and Hematology, Lyon., Gaba M; Department of Health Research and Innovation, Intercommunal Hospital Center of Creteil, Creteil., Arlet JB; French Sickle Cell Referral Center, Internal Medicine Department, Georges Pompidou European Hospital, and Paris University, Paris., Arnaud C; Pediatric department Sickle Cell Referral Center, Centre Hospitalier Intercommunal de Creteil., Jung C; Department of Health Research and Innovation, Intercommunal Hospital Center of Creteil, Creteil, France; Pediatric department Intercommunal Hospital Center of Creteil and University Paris-Est Creteil, Creteil., Pondarre C; Intercommunal Hospital Center of Creteil, INSERM U955, IMRB, Paris XII University, Creteil.
Source: Haematologica [Haematologica] 2026 Jul 01; Vol. 111 (7), pp. 2377-2384. Date of Electronic Publication: 2025 Dec 11.
Publication Type: Journal Article; Clinical Trial, Phase II; Multicenter Study
Journal Info: Publisher: Ferrata Storti Foundation Country of Publication: Italy NLM ID: 0417435 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1592-8721 (Electronic) Linking ISSN: 03906078 NLM ISO Abbreviation: Haematologica Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1592-8721
DOI:10.3324/haematol.2025.300013