Assessment of Immune Responses Against AAV Encoded Transgene Products.

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Title: Assessment of Immune Responses Against AAV Encoded Transgene Products.
Authors: Gorovits B; Regeneron Pharmaceuticals, Inc, Tarrytown, USA. boris.gorovits@regeneron.com., Azadeh M; Progeria Research Foundation, Inc., Cambridge, Massachusetts, USA., Fiscella M; REGENXBIO Inc, Rockville, USA., Harrison T; Precision for Medicine Inc., Frederick, Maryland, USA., Hofer M; Jefferson Institute for Bioprocessing, Lower Gwynedd, USA., Janetzki S; ZellNet Consulting, Inc, Fort Lee, New Jersey, USA., Jawa V; EpiVax, Inc, Providence, Rhode Island, USA., Long B; 4D Molecular Therapeutics, Emeryville, USA., Lu Y; Sangamo Therapeutics, Inc, Richmond, USA., Mahnke YD; FlowKnowHow LLC, New York, USA., Maia M; South San Francisco, CA, USA., Majumdar R; LabCorp Holdings, Inc, Burlington, USA., Miller M; Miller Bioanalytical Consulting LLC, Carlsbad, USA., Milton M; Lake Boon Pharmaceutical Consulting, LLC, Hudson, USA., Nelson R; BioAgilytix Labs, LLC, Durham, USA., Partridge MA; Regeneron Pharmaceuticals, Inc, Tarrytown, USA., Shaik S; Takeda Pharmaceutical Company Limited, Cambridge, USA., Snoeck V; UCB, B-1420, Braine-l'Alleud, Belgium., Vettermann C; 4D Molecular Therapeutics, Emeryville, USA., Wu B; Johnson & Johnson Innovative Medicine, Titusville, USA., Zhao A; Regeneron Pharmaceuticals, Inc, Tarrytown, USA.
Source: The AAPS journal [AAPS J] 2026 Jan 05; Vol. 28 (1), pp. 43. Date of Electronic Publication: 2026 Jan 05.
Publication Type: Journal Article; Review
Journal Info: Publisher: American Association of Pharmaceutical Scientists Country of Publication: United States NLM ID: 101223209 Publication Model: Electronic Cited Medium: Internet ISSN: 1550-7416 (Electronic) Linking ISSN: 15507416 NLM ISO Abbreviation: AAPS J Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Assessment of Immune Responses Against AAV Encoded Transgene Products.
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  Data: <searchLink fieldCode="AU" term="%22Gorovits+B%22">Gorovits B</searchLink>; Regeneron Pharmaceuticals, Inc, Tarrytown, USA. boris.gorovits@regeneron.com.<br /><searchLink fieldCode="AU" term="%22Azadeh+M%22">Azadeh M</searchLink>; Progeria Research Foundation, Inc., Cambridge, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Fiscella+M%22">Fiscella M</searchLink>; REGENXBIO Inc, Rockville, USA.<br /><searchLink fieldCode="AU" term="%22Harrison+T%22">Harrison T</searchLink>; Precision for Medicine Inc., Frederick, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Hofer+M%22">Hofer M</searchLink>; Jefferson Institute for Bioprocessing, Lower Gwynedd, USA.<br /><searchLink fieldCode="AU" term="%22Janetzki+S%22">Janetzki S</searchLink>; ZellNet Consulting, Inc, Fort Lee, New Jersey, USA.<br /><searchLink fieldCode="AU" term="%22Jawa+V%22">Jawa V</searchLink>; EpiVax, Inc, Providence, Rhode Island, USA.<br /><searchLink fieldCode="AU" term="%22Long+B%22">Long B</searchLink>; 4D Molecular Therapeutics, Emeryville, USA.<br /><searchLink fieldCode="AU" term="%22Lu+Y%22">Lu Y</searchLink>; Sangamo Therapeutics, Inc, Richmond, USA.<br /><searchLink fieldCode="AU" term="%22Mahnke+YD%22">Mahnke YD</searchLink>; FlowKnowHow LLC, New York, USA.<br /><searchLink fieldCode="AU" term="%22Maia+M%22">Maia M</searchLink>; South San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Majumdar+R%22">Majumdar R</searchLink>; LabCorp Holdings, Inc, Burlington, USA.<br /><searchLink fieldCode="AU" term="%22Miller+M%22">Miller M</searchLink>; Miller Bioanalytical Consulting LLC, Carlsbad, USA.<br /><searchLink fieldCode="AU" term="%22Milton+M%22">Milton M</searchLink>; Lake Boon Pharmaceutical Consulting, LLC, Hudson, USA.<br /><searchLink fieldCode="AU" term="%22Nelson+R%22">Nelson R</searchLink>; BioAgilytix Labs, LLC, Durham, USA.<br /><searchLink fieldCode="AU" term="%22Partridge+MA%22">Partridge MA</searchLink>; Regeneron Pharmaceuticals, Inc, Tarrytown, USA.<br /><searchLink fieldCode="AU" term="%22Shaik+S%22">Shaik S</searchLink>; Takeda Pharmaceutical Company Limited, Cambridge, USA.<br /><searchLink fieldCode="AU" term="%22Snoeck+V%22">Snoeck V</searchLink>; UCB, B-1420, Braine-l'Alleud, Belgium.<br /><searchLink fieldCode="AU" term="%22Vettermann+C%22">Vettermann C</searchLink>; 4D Molecular Therapeutics, Emeryville, USA.<br /><searchLink fieldCode="AU" term="%22Wu+B%22">Wu B</searchLink>; Johnson & Johnson Innovative Medicine, Titusville, USA.<br /><searchLink fieldCode="AU" term="%22Zhao+A%22">Zhao A</searchLink>; Regeneron Pharmaceuticals, Inc, Tarrytown, USA.
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  Data: <searchLink fieldCode="JN" term="%22101223209%22">The AAPS journal</searchLink> [AAPS J] 2026 Jan 05; Vol. 28 (1), pp. 43. <i>Date of Electronic Publication: </i>2026 Jan 05.
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