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Safety profile of idursulfase administered at home in patients with mucopolysaccharidosis II enrolled in the Hunter Outcome Survey.

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Title: Safety profile of idursulfase administered at home in patients with mucopolysaccharidosis II enrolled in the Hunter Outcome Survey.
Authors: Burton BK; Ann & Robert H. Lurie Children's Hospital of Chicago, Northwestern University, Chicago, IL, USA., Guffon N; Reference Center for Inherited Metabolic Diseases, Hospices Civils de Lyon, Lyon, France., Roberts J; Saint Mary's Hospital, Manchester, UK., van der Ploeg AT; Center for Lysosomal and Metabolic Diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands., Jones SA; Saint Mary's Hospital, Manchester, UK., Audi J; Takeda Pharmaceuticals International AG, Zürich, Switzerland., Botha J; Takeda Pharmaceuticals International AG, Zürich, Switzerland. Electronic address: jaco.botha@takeda.com., Whiteman DAH; Takeda Pharmaceutical Company Limited, Lexington, MA, USA., Giugliani R; Postgraduate Program in Genetics and Molecular Biology UFRGS, Medical Genetics Service HCPA, INAGEMP, DASA and Casa dos Raros, Porto Alegre, Brazil., Muenzer J; University of North Carolina at Chapel Hill, Chapel Hill, NC, USA.
Source: Molecular genetics and metabolism [Mol Genet Metab] 2026 Mar; Vol. 147 (3), pp. 109734. Date of Electronic Publication: 2026 Jan 12.
Publication Type: Journal Article
Journal Info: Publisher: Academic Press Country of Publication: United States NLM ID: 9805456 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1096-7206 (Electronic) Linking ISSN: 10967192 NLM ISO Abbreviation: Mol Genet Metab Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Safety profile of idursulfase administered at home in patients with mucopolysaccharidosis II enrolled in the Hunter Outcome Survey.
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  Data: <searchLink fieldCode="AU" term="%22Burton+BK%22">Burton BK</searchLink>; Ann & Robert H. Lurie Children's Hospital of Chicago, Northwestern University, Chicago, IL, USA.<br /><searchLink fieldCode="AU" term="%22Guffon+N%22">Guffon N</searchLink>; Reference Center for Inherited Metabolic Diseases, Hospices Civils de Lyon, Lyon, France.<br /><searchLink fieldCode="AU" term="%22Roberts+J%22">Roberts J</searchLink>; Saint Mary's Hospital, Manchester, UK.<br /><searchLink fieldCode="AU" term="%22van+der+Ploeg+AT%22">van der Ploeg AT</searchLink>; Center for Lysosomal and Metabolic Diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.<br /><searchLink fieldCode="AU" term="%22Jones+SA%22">Jones SA</searchLink>; Saint Mary's Hospital, Manchester, UK.<br /><searchLink fieldCode="AU" term="%22Audi+J%22">Audi J</searchLink>; Takeda Pharmaceuticals International AG, Zürich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Botha+J%22">Botha J</searchLink>; Takeda Pharmaceuticals International AG, Zürich, Switzerland. Electronic address: jaco.botha@takeda.com.<br /><searchLink fieldCode="AU" term="%22Whiteman+DAH%22">Whiteman DAH</searchLink>; Takeda Pharmaceutical Company Limited, Lexington, MA, USA.<br /><searchLink fieldCode="AU" term="%22Giugliani+R%22">Giugliani R</searchLink>; Postgraduate Program in Genetics and Molecular Biology UFRGS, Medical Genetics Service HCPA, INAGEMP, DASA and Casa dos Raros, Porto Alegre, Brazil.<br /><searchLink fieldCode="AU" term="%22Muenzer+J%22">Muenzer J</searchLink>; University of North Carolina at Chapel Hill, Chapel Hill, NC, USA.
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              Text: 2026 Mar
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