Enzyme replacement therapy for CLN1 batten disease that crosses the blood-brain-barrier.

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Title: Enzyme replacement therapy for CLN1 batten disease that crosses the blood-brain-barrier.
Authors: Raman R; Collaborations Pharmaceuticals Inc., Raleigh, NC 27606, USA. Electronic address: renuka@collaborationspharma.com., Horst B; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA., Shahrokh Z; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA., Hatambeygi N; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA., Zare M; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA., Leszczyniecka M; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA., Harris JS; Collaborations Pharmaceuticals Inc., Raleigh, NC 27606, USA., Banks WA; Geriatric Research Education and Clinical Center, Veterans Affairs Puget Sound Health Care System, Seattle, WA 98108, USA., Hansen KM; Geriatric Research Education and Clinical Center, Veterans Affairs Puget Sound Health Care System, Seattle, WA 98108, USA; Division of Gerontology and Geriatric Medicine, Department of Medicine, University of Washington School of Medicine, Seattle, WA 98104, USA., Erickson MA; Geriatric Research Education and Clinical Center, Veterans Affairs Puget Sound Health Care System, Seattle, WA 98108, USA; Division of Gerontology and Geriatric Medicine, Department of Medicine, University of Washington School of Medicine, Seattle, WA 98104, USA., Ekins S; Collaborations Pharmaceuticals Inc., Raleigh, NC 27606, USA.
Source: Molecular genetics and metabolism [Mol Genet Metab] 2026 Mar; Vol. 147 (3), pp. 109733. Date of Electronic Publication: 2026 Jan 16.
Publication Type: Journal Article
Journal Info: Publisher: Academic Press Country of Publication: United States NLM ID: 9805456 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1096-7206 (Electronic) Linking ISSN: 10967192 NLM ISO Abbreviation: Mol Genet Metab Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Enzyme replacement therapy for CLN1 batten disease that crosses the blood-brain-barrier.
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  Data: <searchLink fieldCode="AU" term="%22Raman+R%22">Raman R</searchLink>; Collaborations Pharmaceuticals Inc., Raleigh, NC 27606, USA. Electronic address: renuka@collaborationspharma.com.<br /><searchLink fieldCode="AU" term="%22Horst+B%22">Horst B</searchLink>; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA.<br /><searchLink fieldCode="AU" term="%22Shahrokh+Z%22">Shahrokh Z</searchLink>; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA.<br /><searchLink fieldCode="AU" term="%22Hatambeygi+N%22">Hatambeygi N</searchLink>; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA.<br /><searchLink fieldCode="AU" term="%22Zare+M%22">Zare M</searchLink>; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA.<br /><searchLink fieldCode="AU" term="%22Leszczyniecka+M%22">Leszczyniecka M</searchLink>; STC Biologics, Inc., 330 Nevada Street, Newton, MA 02460, USA.<br /><searchLink fieldCode="AU" term="%22Harris+JS%22">Harris JS</searchLink>; Collaborations Pharmaceuticals Inc., Raleigh, NC 27606, USA.<br /><searchLink fieldCode="AU" term="%22Banks+WA%22">Banks WA</searchLink>; Geriatric Research Education and Clinical Center, Veterans Affairs Puget Sound Health Care System, Seattle, WA 98108, USA.<br /><searchLink fieldCode="AU" term="%22Hansen+KM%22">Hansen KM</searchLink>; Geriatric Research Education and Clinical Center, Veterans Affairs Puget Sound Health Care System, Seattle, WA 98108, USA; Division of Gerontology and Geriatric Medicine, Department of Medicine, University of Washington School of Medicine, Seattle, WA 98104, USA.<br /><searchLink fieldCode="AU" term="%22Erickson+MA%22">Erickson MA</searchLink>; Geriatric Research Education and Clinical Center, Veterans Affairs Puget Sound Health Care System, Seattle, WA 98108, USA; Division of Gerontology and Geriatric Medicine, Department of Medicine, University of Washington School of Medicine, Seattle, WA 98104, USA.<br /><searchLink fieldCode="AU" term="%22Ekins+S%22">Ekins S</searchLink>; Collaborations Pharmaceuticals Inc., Raleigh, NC 27606, USA.
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        Value: 10.1016/j.ymgme.2026.109733
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              Text: 2026 Mar
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