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Clinical expert opinion on the role of elosulfase alfa in non-ambulatory individuals with Morquio A syndrome.

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Title: Clinical expert opinion on the role of elosulfase alfa in non-ambulatory individuals with Morquio A syndrome.
Authors: de Souza CFM; Hospital de Clinicas de Porto Alegre (HCPA), Casa dos Raros, Post Graduate Program in Child and Adolescent Health Federal University of Rio Grande do Sul (UFRGS), Porto Alegre, Brazil., Burton BK; Ann & Robert H. Lurie Children's Hospital of Chicago and Northwestern University Feinberg School of Medicine, Chicago, IL, USA., Campeau PM; CHU Sainte-Justine Research Center, Montreal, QC, Canada., Giugliani R; Federal University of Rio Grande do Sul (UFRGS), Hospital de Clinicas de Porto Alegre (HCPA), Dasa Genomics, and Casa dos Raros, Porto Alegre, Brazil., Guffon N; Reference Center for Inherited Metabolic Diseases, Hospices Civils de Lyon, France., Lampe C; University hospital of Gießen, Gießen, Lysosomal Unit, Center for Rare Diseases, Germany., Muschol N; International Center for Lysosomal Disorders (ICLD), University Medical Center Hamburg-Eppendorf, Hamburg, Germany., Sivri S; Hacettepe University Children's Hospital, Ankara, Turkey., Solano M; Fundación Cardioinfantil, Bogotá, Colombia., Stepien KM; Salford Royal Hospital, Northern Care Alliance NHS Foundation Trust, Salford, UK.
Source: Molecular genetics and metabolism reports [Mol Genet Metab Rep] 2026 Jan 21; Vol. 46, pp. 101290. Date of Electronic Publication: 2026 Jan 21 (Print Publication: 2026).
Publication Type: Journal Article
Journal Info: Publisher: Elsevier Inc Country of Publication: United States NLM ID: 101624422 Publication Model: eCollection Cited Medium: Print ISSN: 2214-4269 (Print) Linking ISSN: 22144269 NLM ISO Abbreviation: Mol Genet Metab Rep Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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  Data: Clinical expert opinion on the role of elosulfase alfa in non-ambulatory individuals with Morquio A syndrome.
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  Data: <searchLink fieldCode="AU" term="%22de+Souza+CFM%22">de Souza CFM</searchLink>; Hospital de Clinicas de Porto Alegre (HCPA), Casa dos Raros, Post Graduate Program in Child and Adolescent Health Federal University of Rio Grande do Sul (UFRGS), Porto Alegre, Brazil.<br /><searchLink fieldCode="AU" term="%22Burton+BK%22">Burton BK</searchLink>; Ann & Robert H. Lurie Children's Hospital of Chicago and Northwestern University Feinberg School of Medicine, Chicago, IL, USA.<br /><searchLink fieldCode="AU" term="%22Campeau+PM%22">Campeau PM</searchLink>; CHU Sainte-Justine Research Center, Montreal, QC, Canada.<br /><searchLink fieldCode="AU" term="%22Giugliani+R%22">Giugliani R</searchLink>; Federal University of Rio Grande do Sul (UFRGS), Hospital de Clinicas de Porto Alegre (HCPA), Dasa Genomics, and Casa dos Raros, Porto Alegre, Brazil.<br /><searchLink fieldCode="AU" term="%22Guffon+N%22">Guffon N</searchLink>; Reference Center for Inherited Metabolic Diseases, Hospices Civils de Lyon, France.<br /><searchLink fieldCode="AU" term="%22Lampe+C%22">Lampe C</searchLink>; University hospital of Gießen, Gießen, Lysosomal Unit, Center for Rare Diseases, Germany.<br /><searchLink fieldCode="AU" term="%22Muschol+N%22">Muschol N</searchLink>; International Center for Lysosomal Disorders (ICLD), University Medical Center Hamburg-Eppendorf, Hamburg, Germany.<br /><searchLink fieldCode="AU" term="%22Sivri+S%22">Sivri S</searchLink>; Hacettepe University Children's Hospital, Ankara, Turkey.<br /><searchLink fieldCode="AU" term="%22Solano+M%22">Solano M</searchLink>; Fundación Cardioinfantil, Bogotá, Colombia.<br /><searchLink fieldCode="AU" term="%22Stepien+KM%22">Stepien KM</searchLink>; Salford Royal Hospital, Northern Care Alliance NHS Foundation Trust, Salford, UK.
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  Data: <searchLink fieldCode="JN" term="%22101624422%22">Molecular genetics and metabolism reports</searchLink> [Mol Genet Metab Rep] 2026 Jan 21; Vol. 46, pp. 101290. <i>Date of Electronic Publication: </i>2026 Jan 21 (<i>Print Publication: </i>2026).
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Elsevier+Inc%22">Elsevier Inc </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101624422 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Print <i>ISSN: </i>2214-4269 (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2222144269%22">22144269 </searchLink><i>NLM ISO Abbreviation: </i>Mol Genet Metab Rep <i>Subsets: </i>PubMed not MEDLINE
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              Text: 2026 Jan 21
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