Gene therapy outcomes in young patients with RPE65-retinal degeneration.

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Bibliographic Details
Title: Gene therapy outcomes in young patients with RPE65-retinal degeneration.
Authors: Stephenson KAJ; Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada., Alsalamah AK; Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada; Vitreoretinal Division, Ocular Genetics Service, King Khaled Eye Specialist Hospital, Riyadh, Saudi Arabia., Tumber A; Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada., Mercer GD; Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada; Unity Health St. Michael's Hospital, Toronto, ON, Canada; Department of Ophthalmology and Vision Sciences, University of Toronto, Toronto, ON, Canada., Ballios BG; Department of Ophthalmology and Vision Sciences, University of Toronto, Toronto, ON, Canada; University Health Network, Toronto, ON, Canada; Kensington Vision and Research Centre, Toronto, ON, Canada; Sunnybrook Health Sciences Centre, Toronto, ON, Canada., Muni RH; Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada; Unity Health St. Michael's Hospital, Toronto, ON, Canada; Department of Ophthalmology and Vision Sciences, University of Toronto, Toronto, ON, Canada., Tavares E; Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada; The Hospital for Sick Children, Programme of Genetics and Genome Biology, Toronto, ON, Canada., Kertes PJ; Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada; Department of Ophthalmology and Vision Sciences, University of Toronto, Toronto, ON, Canada; University Health Network, Toronto, ON, Canada; Kensington Vision and Research Centre, Toronto, ON, Canada; Sunnybrook Health Sciences Centre, Toronto, ON, Canada., Vincent A; Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada; Department of Ophthalmology and Vision Sciences, University of Toronto, Toronto, ON, Canada; The Hospital for Sick Children, Programme of Genetics and Genome Biology, Toronto, ON, Canada., Héon E; Department of Ophthalmology and Vision Sciences, The Hospital for Sick Children, Toronto, ON, Canada; Department of Ophthalmology and Vision Sciences, University of Toronto, Toronto, ON, Canada; The Hospital for Sick Children, Programme of Genetics and Genome Biology, Toronto, ON, Canada. Electronic address: elise.heon@sickkids.ca.
Source: Canadian journal of ophthalmology. Journal canadien d'ophtalmologie [Can J Ophthalmol] 2026 Jun; Vol. 61 (3), pp. 685-692. Date of Electronic Publication: 2026 Feb 27.
Publication Type: Journal Article
Journal Info: Publisher: Elsevier Country of Publication: England NLM ID: 0045312 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1715-3360 (Electronic) Linking ISSN: 00084182 NLM ISO Abbreviation: Can J Ophthalmol Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1715-3360
DOI:10.1016/j.jcjo.2026.01.016